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Clinical Trials on Hypoadrenocorticism, Familial
Total 1149 results
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.CompletedFamilial Chylomicronemia Syndrome | Lipoprotein Lipase Deficiency | Hyperlipoproteinemia Type 1Canada
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University of MichiganCompletedNAFLD | Nonalcoholic Steatohepatitis | Familial Partial LipodystrophyUnited States
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University of Southern CaliforniaEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedObesity | Obesity, Childhood | Obesity; FamilialUnited States
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University of MinnesotaRecruitingRacially/Ethnically Diverse Families From Urban SettingsUnited States
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University of MichiganNot yet recruitingPregnancy Related | Infant Behavior | Obesity; FamilialUnited States
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University of Alabama at BirminghamNational Institute on Minority Health and Health Disparities (NIMHD)Active, not recruitingObesity | Obesity, Childhood | Obesity; FamilialUnited States
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University of California, San FranciscoDestination: Home SV; Sí Se Puede Collective; Sacred Heart Community Service; County...RecruitingFamilies Experiencing Homelessness and/or Housing InstabilityUnited States
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University of California, Los AngelesVA Greater Los Angeles Healthcare SystemWithdrawnVeteran Families | Family Communications | Civilian Life ReintegrationUnited States
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Rambam Health Care CampusWithdrawnFamilial Mediterranean Fever (FMF )
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Verve Therapeutics, Inc.Not yet recruitingHypercholesterolemia | Atherosclerotic Cardiovascular Disease | Heterozygous Familial HypercholesterolemiaNew Zealand, United Kingdom
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Akcea TherapeuticsRecruitingHereditary Transthyretin Amyloidosis With PolyneuropthyUnited States, Canada
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Verve Therapeutics, Inc.Active, not recruitingHypercholesterolemia | Atherosclerotic Cardiovascular Disease | Heterozygous Familial HypercholesterolemiaNew Zealand, United Kingdom
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University of MessinaUniversità degli Studi di Ferrara; University of Pavia; Careggi Hospital; Fondazione...UnknownPatient-Reported Outcome Measures in Wild-Type and Variant Cardiac Transthyretin Amyloidosis (ITALY)Transthyretin AmyloidosisItaly
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AlbireoActive, not recruitingProgressive Familial Intrahepatic CholestasisUnited States, Spain, Netherlands, United Kingdom, Turkey, Canada, Italy, Germany, France, Israel, Australia, Belgium, Poland, Saudi Arabia, Sweden
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Yale UniversityCompletedFamilial Alcoholism VulnerabilityUnited States
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Institute of Liver and Biliary Sciences, IndiaKEM Hospital Research Centre; Apollo Hospital, New Delhi, India; Jaslok Hospital... and other collaboratorsRecruitingProgressive Familial Intrahepatic CholestasisIndia
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University Medical Center GroningenEnrolling by invitationProgressive Familial Intrahepatic CholestasisNetherlands
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Yale UniversityNational Institute on Alcohol Abuse and Alcoholism (NIAAA)RecruitingFamilial Alcoholism VulnerabilityUnited States
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AlbireoApproved for marketingProgressive Familial Intrahepatic CholestasisUnited States
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Novartis PharmaceuticalsCompletedNon Familial Chylocmicronemia Syndrome (Non-FCS)United States, Canada, Russian Federation
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National Liver Institute, EgyptUnknownProgressive Familial Intrahepatic CholestasisEgypt
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Alnylam PharmaceuticalsCompletedFamilial Amyloidotic Cardiomyopathy (FAC)United States, France, Spain, United Kingdom, Belgium, Brazil
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Novartis PharmaceuticalsCompletedColchicine Resistant/Intolerant Familial Mediterranean FeverIsrael
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Immunovia, Inc.CompletedPancreatic Ductal Adenocarcinoma | Familial Pancreatic Cancer | FAMMM - Familial Atypical Mole Malignant Melanoma SyndromeUnited States, Sweden, Canada, Spain, United Kingdom
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Massachusetts General HospitalPfizer; Akcea Therapeutics; Alnylam Pharmaceuticals; Eidos Therapeutics, a BridgeBio...RecruitingHeart Failure | Amyloidosis | Heart Failure, Diastolic | Transthyretin AmyloidosisUnited States
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Elif OralCompletedFatty Liver | Hypertriglyceridemia | NASH - Nonalcoholic Steatohepatitis | Familial Partial LipodystrophyUnited States
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NYU Langone HealthWithdrawnNausea | Vomiting | Familial DysautonomiaUnited States
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NYU Langone HealthCompletedFamilial Dysautonomia
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Daiichi Sankyo, Inc.TerminatedAtherosclerosis | Heterozygous Familial HypercholesterolemiaUnited States, United Kingdom, Spain, South Africa, Israel, Canada, Netherlands, Norway, Sweden
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M.D. Anderson Cancer CenterCompletedAttenuated Familial Adenomatous Polyposis | Deleterious Familial Adenomatous PolyposisUnited States
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Arizona State UniversityArizona Health Care Cost Containment SystemEnrolling by invitation
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Memorial Sloan Kettering Cancer CenterUniversity of Southern California; Weill Medical College of Cornell University and other collaboratorsActive, not recruiting
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University of ChicagoTerminatedOsteoporosis | Osteopenia | Hypercalciuria | Hypercalciuria, Familial IdiopathicUnited States
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Intellia TherapeuticsRegeneron PharmaceuticalsRecruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Australia, United Kingdom, New Zealand
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Duke UniversityCompletedFamilies Experiencing Homelessness With Children Under 48 Months of AgeUnited States
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Lev-Hasharon Mental Healtlh CenterUnknown
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Centre Medico-Chirurgicale et Obstetrique Cote...UnknownLumbar Stenosis, FamilialFrance
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Assistance Publique - Hôpitaux de ParisCompletedThoracic Aortic AneurysmFrance
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National Human Genome Research Institute (NHGRI)Completed
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Massachusetts General HospitalBroad InstituteRecruitingPrion Diseases | Familial Fatal Insomnia | CJD (Creutzfeldt Jakob Disease) | GSS | FFIUnited States
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Australia, Brazil, Bulgaria, France, Italy, Japan, Mexico, Netherlands, Taiwan, United Kingdom, Belgium, Czechia, Denmark, New Zealand, Sweden, Korea, Republic of, Argentina, Chile, Hong Kong, Portugal
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Poland, Argentina, Australia, Belgium, France, Germany, Japan, Netherlands, Portugal, Spain, Sweden, United Kingdom, Canada, Czechia, Denmark, Hungary, Ireland, Norway, Korea, Republic of, Austria, Croatia, Israel, Latvia, Lithuan... and more
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedCoronary Artery Disease | Heterozygous Familial HypercholesterolemiaUnited States, Canada
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHomozygous Familial HypercholesterolemicUnited States
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NYU Langone HealthCompletedDysautonomia, Familial | Baroreflex Failure SyndromeUnited States
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Virginia Commonwealth UniversityNot yet recruitingAmyloidosis, HereditaryUnited States
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University Hospital, MontpellierCompletedOppositional Defiant Disorder With Familial SettingFrance
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AstraZenecaRecruitingTransthyretin Amyloidosis Cardiomyopathy, Heart Failure With Preserved Ejection FractionRussian Federation
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Eidos Therapeutics, a BridgeBio companyCompletedFamilial ATTR-CM (ATTRm-CM, or FAC) | Wild-type ATTR-CM (ATTRwt-CM)United States
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University Hospital, MontpellierSoroptimist association of MonacoRecruitingSolid Tumor, Childhood | Pediatric Tumor | Familial Cancer | Hematological TumorFrance