- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Ichthyosis, X-Linked
Total 2437 results
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University of FloridaRecruiting
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PfizerActive, not recruitingDuchenne Muscular DystrophyUnited States, Spain, Belgium, Korea, Republic of, Taiwan, Canada, Australia, Germany, Japan, France, Italy, United Kingdom, Russian Federation, Israel, Switzerland
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BBulgaria, United States, United Kingdom, Russian Federation, Switzerland
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Edgewise Therapeutics, Inc.Medpace, Inc.Enrolling by invitationBecker Muscular DystrophyUnited States, Netherlands, United Kingdom
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St. Jude Children's Research HospitalChildren's Hospital of Philadelphia; National Heart, Lung, and Blood Institute... and other collaboratorsActive, not recruitingHemophilia BUnited States, United Kingdom
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Santhera PharmaceuticalsSanthera PharmaceuticalsActive, not recruitingDuchenne Muscular DystrophyCanada
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Sarepta Therapeutics, Inc.Active, not recruitingMuscular Dystrophy, DuchenneUnited States, Korea, Republic of, India, Slovenia, Turkey, United Kingdom, Germany, Switzerland, Spain, Czechia, France, Serbia, Taiwan, Netherlands, Mexico, Colombia, Denmark, New Zealand, Norway, Greece, Hungary, Ireland, Italy, Jo... and more
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Sheffield Children's NHS Foundation TrustSheffield Hallam University; National Institute for Health Research, United... and other collaboratorsActive, not recruiting
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Active, not recruitingDuchenne Muscular DystrophyKorea, Republic of, Chile, Japan, China, United Kingdom, Netherlands, Spain, Norway, Russian Federation, Australia, Greece, Italy, New Zealand, Turkey, Mexico, Czechia, Canada
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University College, LondonRadboud University Medical Center; Groupe Hospitalier Pitie-Salpetriere; Leiden... and other collaboratorsCompletedDuchenne Muscular DystrophyNetherlands, France, United Kingdom
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Swedish Orphan BiovitrumIQVIA Pvt. LtdTerminatedHemophilia A | Hemophilia BBulgaria, Croatia, Czechia, France, Hungary, Ireland, Italy, Romania, Slovenia, Spain, United Kingdom
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Santhera PharmaceuticalsAvailableDuchenne Muscular DystrophyUnited States, Canada, Israel
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophyKorea, Republic of, Chile, Taiwan, China, United States, United Kingdom, Netherlands, Spain, Australia, Norway, Russian Federation, Greece, Italy, Turkey, Mexico, Canada, Hong Kong, New Zealand, Ukraine
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Hacettepe UniversityCompletedDuchenne Muscular DystrophyTurkey
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.TerminatedMuscular Dystrophy, DuchenneUnited States, Canada
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Freeline TherapeuticsTerminatedHemophilia BUnited States, United Kingdom
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ReveraGen BioPharma, Inc.University of Pittsburgh; Newcastle University; European Union; Cooperative International...CompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, United Kingdom, Spain, Netherlands, Sweden, Czechia, Australia, Greece, Israel
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Haukeland University HospitalExtrastiftelsenCompleted
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Phrixus Pharmaceuticals, Inc.Charley's FundTerminated
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University College, LondonTerminatedHemophilia BIreland, United Kingdom, Italy, United States
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Acceleron Pharma Inc. (a wholly owned subsidiary...Terminated
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Catabasis PharmaceuticalsCompletedMuscular Dystrophy, DuchenneUnited States
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Newcastle... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Germany, Italy
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CSL BehringCompletedHemophilia BGermany, Denmark, Netherlands
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ItalfarmacoSyneos HealthCompletedDuchenne Muscular DystrophyUnited States, Italy, Spain, Canada, Belgium, France, Germany, Israel, Netherlands, Serbia, United Kingdom
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BUnited States, Australia, Canada, China, France, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Germany, India, Italy, Japan, South Africa, Spain, Taiwan
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BUnited States, Australia, China, Denmark, France, Israel, Japan, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Germany, India, South Africa, Spain, Taiwan, Hungary, Italy
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Sangamo TherapeuticsTerminated
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Haukeland University HospitalOslo University Hospital; Norwegian School of Sport SciencesCompletedDuchenne Muscular DystrophyNorway
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NS Pharma, Inc.Cooperative International Neuromuscular Research Group; Nippon Shinyaku Co.... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada
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Santhera PharmaceuticalsTerminatedDuchenne Muscular DystrophyUnited States, Belgium, United Kingdom, Austria, France, Germany, Italy, Spain, Switzerland
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Catalyst BiosciencesCompletedHemophilia BSouth Africa
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Charite University, Berlin, GermanyCompletedDuchenne Muscular DystrophyGermany
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Taiho Pharmaceutical Co., Ltd.Completed
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ReveraGen BioPharma, Inc.University of Pittsburgh; Cooperative International Neuromuscular Research...CompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Sweden, Australia, Israel
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Rare Disease Research, LLCSarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyUnited States
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Baxalta now part of ShireCompletedHemophilia BKorea, Republic of
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Baxalta now part of ShireCompleted
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Medexus Pharma, Inc.CompletedHemophilia BUnited States, France, United Kingdom, India, Israel, Italy, Poland
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Baxalta now part of ShireCompletedHemophilia A | Hemophilia BUnited States
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Marmara UniversityUnknownDuchenne Muscular Dystrophy
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Children's Hospital Medical Center, CincinnatiIpsen; Charley's FundCompletedDuchenne Muscular DystrophyUnited States
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PfizerTerminatedDuchenne Muscular DystrophyUnited States, Australia, Canada, United Kingdom, Japan, Bulgaria, Italy, Poland
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Catabasis PharmaceuticalsTerminatedDuchenne Muscular DystrophyUnited States, Canada, Australia, United Kingdom, Germany, Sweden
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ISU Abxis Co., Ltd.Catalyst BiosciencesCompletedHemophilia BKorea, Republic of
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Processa PharmaceuticalsTerminatedDuchenne Muscular DystrophyUnited States
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Stem Cells ArabiaUnknownDuchenne Muscular DystrophyJordan