- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Inborn Amino Acid Metabolism Disorder
Total 43860 results
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Baylor College of MedicineSeattle Children's Hospital; University of California, San FranciscoCompleted
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HLB Cell Co., Ltd.WithdrawnUrea Cycle DisorderKorea, Republic of
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Horizon Therapeutics, LLCCompletedUrea Cycle DisorderUnited States, Canada
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University of Novi Sad, Faculty of Sport and Physical...Completed
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Horizon Pharma Ireland, Ltd., Dublin IrelandCompletedUrea Cycle DisordersUnited States
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Horizon Pharma Ireland, Ltd., Dublin IrelandCompletedUrea Cycle DisordersUnited States, Canada
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Children's National Research InstitutePatient-Centered Outcomes Research Institute; Eunice Kennedy Shriver National... and other collaboratorsCompleted
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Promethera TherapeuticsCompletedUrea Cycle DisordersBelgium, Spain, France, Poland
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Kaleido BiosciencesCompletedUrea Cycle DisordersSwitzerland
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PTC TherapeuticsNot yet recruitingPhenylketonuriaUnited States
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First Affiliated Hospital Bengbu Medical CollegeRecruiting
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Vitaflo International, LtdBirmingham Women's and Children's NHS Foundation TrustRecruiting
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Jnana TherapeuticsRecruitingPhenylketonuriaUnited States, Australia
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University Medical Centre LjubljanaNot yet recruitingPhenylketonurias | Nutritional and Metabolic Diseases
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SynlogicTerminatedPhenylketonuriaUnited States, Canada, Georgia, Turkey
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University of Southern CaliforniaNational PKU AllianceActive, not recruitingPhenylketonuriasUnited States
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Boston Children's HospitalBioMarin PharmaceuticalCompletedPhenylketonuriasUnited States
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University of NebraskaCompleted
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Homology Medicines, IncTerminated
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University of Missouri-ColumbiaBioMarin PharmaceuticalEnrolling by invitationPhenylketonuriasUnited States
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APR Applied Pharma Research s.a.Terminated
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University Hospital Inselspital, BerneUniversity of ZurichCompleted
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University Hospitals Cleveland Medical CenterBioMarin PharmaceuticalCompleted
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The University of Texas Medical Branch, GalvestonTerminated
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Boston Children's HospitalBioMarin PharmaceuticalCompleted
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NestléWithdrawn
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Universidade do PortoBioMarin Pharmaceutical; Centro Hospitalar do PortoCompleted
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University of British ColumbiaVitaflo International, LtdUnknown
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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Nutricia UK LtdWithdrawn
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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University of Wisconsin, MadisonBoston Children's HospitalCompletedPhenylketonuriaUnited States
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BioMarin PharmaceuticalTerminatedPhenylketonuriaItaly, Switzerland
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Emory UniversityBioMarin Pharmaceutical; Atlanta Clinical and Translational Science InstituteCompletedPhenylketonuriaUnited States
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Children's National Research InstituteGeorgetown UniversityWithdrawn
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Oregon Health and Science UniversityTerminated
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Merck KGaA, Darmstadt, GermanySmerud Medical Research International AS; Merck Serono NorwayCompleted
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BioMarin PharmaceuticalCompletedStudy of Phenoptin in Subjects With Phenylketonuria Who Participated in Protocols PKU-004 or PKU-006PhenylketonuriaUnited States
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The Kennedy Institute-National Eye ClinicSygekassernes HelsefondCompleted
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University Hospital, Clermont-FerrandUnknown
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Dr. Schär AG / SPACompletedPhenylketonurias | Inborn Errors of Metabolism | Metabolic Disease | PKUUnited Kingdom
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Children's Hospital of PhiladelphiaEunice Kennedy Shriver National Institute of Child Health and Human Development...WithdrawnUrea Cycle Disorders, Inborn | Inborn Errors of Metabolism | Propionic Acidemia | Methylmalonic Acidemia | Carbamyl Phosphate Synthetase Deficiency
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Vitaflo International, LtdBirmingham Women's and Children's NHS Foundation TrustCompletedPhenylketonuria | Inborn Errors of MetabolismUnited Kingdom
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Canada, United Kingdom, Portugal
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Canada, United Kingdom, Portugal
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Baylor College of MedicineRare Diseases Clinical Research Network; Neogenis LaboratoriesCompletedUrea Cycle Disorders, Inborn | Urea Cycle Disorder | Argininosuccinic Aciduria | Argininosuccinate Lyase DeficiencyUnited States
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Horizon Pharma Ireland, Ltd., Dublin IrelandCompletedUrea Cycle DisordersUnited States, Canada