Clinical Trials on Inborn Errors of Metabolism
Total 6430 results
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Alexion Pharmaceuticals, Inc.RecruitingHypophosphatasiaUnited States, Japan, Germany, Turkey, Italy, India, Australia, France, United Kingdom, Argentina, Canada
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Alexion Pharmaceuticals, Inc.Not yet recruiting
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AlexionRecruiting
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Children's Mercy Hospital Kansas CityRecruiting
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Sheffield Teaching Hospitals NHS Foundation TrustNational Institute for Health Research, United Kingdom; Alexion Pharmaceuticals...Completed
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Sheffield Teaching Hospitals NHS Foundation TrustUniversity of SheffieldActive, not recruiting
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Duke UniversityRecruitingHypophosphatasiaUnited States
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Ultragenyx Pharmaceutical IncNovartis; Mereo BioPharmaCompleted
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Dr. Lothar SeefriedAlexion PharmaceuticalsCompleted
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CENTOGENE GmbH RostockAlexion PharmaceuticalsCompleted
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Alexion PharmaceuticalsCompletedHypophosphatasiaUnited States, Germany
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Translational Research Center for Medical Innovation...Osaka University Graduate School of MedicineCompleted
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Alexion Pharmaceuticals, Inc.Not yet recruitingHypophosphatasiaUnited States, Taiwan, Thailand, Vietnam, United Kingdom, Korea, Republic of, Israel, Italy, Australia, Turkey, France, Poland, Germany, Spain, Belgium, China, Canada, Brazil, Argentina, Mexico
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Alexion Pharmaceuticals, Inc.RecruitingHypophosphatasiaItaly, Spain, Israel, Korea, Republic of, Belgium, Germany, United States, China, France, Taiwan, Austria, Japan, India, Australia, Argentina, Poland, Turkey, Brazil, Thailand, United Kingdom, Canada, Slovakia, Czechia
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Vitaflo International, LtdUniversity College London Hospitals; University Medical Center Groningen; University... and other collaboratorsCompletedGlycogen Storage DiseaseUnited States, United Kingdom, France, Netherlands
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Alexion Pharmaceuticals, Inc.Completed
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AM-PharmaCompleted
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Sheffield Teaching Hospitals NHS Foundation TrustCompleted
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Wuerzburg University HospitalCompleted
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Children's Hospital of PhiladelphiaActive, not recruitingMaple Syrup Urine DiseaseUnited States
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Children's Hospital of PhiladelphiaEunice Kennedy Shriver National Institute of Child Health and Human Development...WithdrawnUrea Cycle Disorders, Inborn | Inborn Errors of Metabolism | Propionic Acidemia | Methylmalonic Acidemia | Carbamyl Phosphate Synthetase Deficiency
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Monash University MalaysiaRecruiting
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Alexion Pharmaceuticals, Inc.Enrolling by invitationHypophosphatasia (HPP)United States, Italy, Russian Federation, Spain, United Kingdom, Germany, Canada, France, Saudi Arabia, Poland, Australia
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Alexion PharmaceuticalsApproved for marketingHypophosphatasiaUnited States, France
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Origin BiosciencesCompletedMolybdenum Cofactor DeficiencyUnited States, Australia, United Kingdom, Germany, Netherlands, Turkey
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Alexion PharmaceuticalsCompletedHypophosphatasiaUnited States, Spain, Australia, United Kingdom, Italy, France, Canada, Germany, Japan, Russian Federation, Saudi Arabia, Turkey
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University of PittsburghCompleted
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LogicBio Therapeutics, IncAlexion Pharmaceuticals, Inc.Active, not recruitingMethylmalonic AcidemiaUnited States
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Hvidovre University HospitalOdense University HospitalActive, not recruitingHypophosphatasia (HPP)Denmark
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedAmino Acid Metabolism, Inborn ErrorsFrance, United Kingdom, Italy, Belgium, Germany, Switzerland
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University of FloridaCompleted
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Eunice Kennedy Shriver National Institute of Child...Completed
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Sohag UniversityNot yet recruitingInborn Errors of ImmunityEgypt
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VA Office of Research and DevelopmentCompletedGout | Health Related Quality of Life | Low Medication AdherenceUnited States
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ModernaTX, Inc.RecruitingPropionic AcidemiaUnited States, Spain, Netherlands, France, United Kingdom, Australia, Canada, Italy
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ModernaTX, Inc.RecruitingPropionic AcidemiaUnited States, Canada, United Kingdom
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AlexionWithdrawn
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CENTOGENE GmbH RostockWithdrawnDefective MineralizationGermany, Sri Lanka, India
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Alexion PharmaceuticalsCompletedHypophosphatasiaUnited States, Canada
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Alexion PharmaceuticalsCompletedHypophosphatasiaUnited States, United Arab Emirates, United Kingdom
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Alexion PharmaceuticalsCompleted
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University of FloridaDiabetes SentryTerminatedClinical Evaluation of a Non-Invasive Hypoglycemia Detector in a Glycogen Storage Disease PopulationGlycogen Storage DiseaseUnited States
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Eunice Kennedy Shriver National Institute of Child...Completed
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Krzysztof BankiewiczNational Institute of Neurological Disorders and Stroke (NINDS); University...Recruiting
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University of British ColumbiaCanadian Institutes of Health Research (CIHR); Saudi Arabian Cultural Bureau...Unknown
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Italian Society for RheumatologyCompleted
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Istanbul UniversityBiruni UniversityNot yet recruitingLipid Storage DiseaseTurkey
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National Institutes of Health Clinical Center (CC)Active, not recruiting
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Nantes University HospitalActive, not recruitingHYPOCHOL : A Genetically-based Strategy to Identify New Targets in Cholesterol Metabolism (HYPOCHOL)HypobetalipoproteinemiaFrance