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Clinical Trials on Infantile-onset Spinal Muscular Atrophy
Total 2865 results
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Assiut UniversityRecruitingEarly-Onset Scoliosis Deformity of SpineEgypt
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Texas Christian UniversityRecruiting
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Logan College of ChiropracticUnknown
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McMaster UniversityRecruitingHealthy | Muscle Disuse AtrophyCanada
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Pediatric Spine FoundationColumbia UniversityRecruitingEarly-Onset Scoliosis Deformity of SpineUnited States, Canada, Finland, Hong Kong
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UMC UtrechtApifixWithdrawnIdiopathic Scoliosis | Early-Onset Scoliosis Deformity of Spine (Disorder)Netherlands
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BiogenRecruitingHealthy Volunteer | Muscular Atrophy, SpinalKorea, Republic of, Germany, Belgium, Netherlands, France, Italy, Poland, Canada, United Kingdom, Israel
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AO Innovation Translation CenterActive, not recruitingEarly Onset ScoliosisUnited Kingdom, Switzerland
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Duke UniversityCenters for Disease Control and Prevention; National ALS Registry; Agency for...CompletedMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Progressive Muscular AtrophyUnited States
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EVEREST PESQUISA E DESENVOLVIMENTO LTDANot yet recruiting
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McMaster UniversityMyos CorporationCompletedNutrition, Healthy | Muscle Disuse AtrophyCanada
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Milton S. Hershey Medical CenterBioSensicsNot yet recruitingAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Progressive Muscular Atrophy
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Asan Medical CenterActive, not recruitingSarcopenia | Lumbar Spinal Stenosis | Neurogenic ClaudicationKorea, Republic of
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University of Sao PauloCompleted
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University of Sao Paulo General HospitalAgência Brasileira de Desenvolvimento Industrial (Brazilian Agency For Industrial...Not yet recruitingBrain Injuries | Spinal Cord Injuries | Muscle AtrophyBrazil
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Duke UniversityCReATe Consortium (funded by NIH/NCATS/NINDS)CompletedAmyotrophic Lateral Sclerosis | Progressive Muscular AtrophyUnited States
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Centre Hospitalier Universitaire, AmiensRecruitingSpinal Muscular Atrophy | Non Invasive Ventilation | Respiratory Bacterial InfectionFrance
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Massachusetts General HospitalNorthwestern University; University of Florida; University of Minnesota; Henry... and other collaboratorsRecruitingALS | Kennedy Disease | MND (Motor Neurone DIsease) | PLS | PMA - Progressive Muscular Atrophy | PBP - Progressive Bulbar PalsyUnited States, Italy
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University of OklahomaCompletedCerebral Palsy | Spinal Muscular Atrophy | Arthrogryposis | Other Central Nervous System or Musculoskeletal DisordersUnited States
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University of MiamiFloridaRecruitingInsulin Resistance | Spinal Cord Injuries | Tetraplegia | Muscle Loss | Paraplegia | Atrophy, MuscularUnited States
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University of BirminghamUniversity of Nottingham; Biotechnology and Biological Sciences Research CouncilCompletedSarcopenia | Muscle Loss | Prehabilitation | Disuse Atrophy | Protein MetabolismUnited Kingdom
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University of AlbertaMcGill University; University of Toronto; Laval University; Simon Fraser UniversityRecruitingAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Frontotemporal Degeneration | Progressive Muscular AtrophyCanada
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Shriners Hospitals for ChildrenChest Wall and Spine Deformity Research FoundationUnknownInfantile | Congenital Progressive ScoliosisUnited States
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Duke UniversityUCB PharmaCompletedMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Progressive Muscular AtrophyUnited States
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McMaster UniversityActive, not recruitingHypertrophy | Exercise | Proteomics | Atrophy, DisuseCanada
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Bin LiUnknownAcute LHON | Onset Within Three Months | Onset Between 3 to 6 Months | Onset Between 6 to 12 Months | Onset Between 12 to 24 Months | Onset Between 24 to 60 Months | Onset Over 60 MonthsChina
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Stem Cells ArabiaUnknownMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Progressive Muscular Atrophy | Progressive Bulbar Palsies
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Ohio State UniversityCompletedSpinal Cord Injuries | Metabolic Disease | Skeletal Muscle AtrophyUnited States
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Maastricht University Medical CenterTerminatedImmobilization | Muscle Disuse AtrophyNetherlands
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Thomas Jefferson UniversityRecruitingStroke | Cerebral Palsy | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Hemiparesis | Spinal Muscular Atrophy | Quadriplegia | Arthrogryposis | Neurologic Diseases | Charcot-Marie-Tooth | Weakness of Extremities as Sequela of Stroke | Weakness Due to Upper Motor Neuron Dysfunction | Arm ParalysisUnited States
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Maastricht University Medical CenterCompleted
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Johns Hopkins UniversityMassachusetts General Hospital; Washington University School of Medicine; Emory... and other collaboratorsCompletedMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Progressive Muscular Atrophy | Healthy Controls | Flail Arm ALS | Monomelic Amyotrophy | Asymptomatic ALS Gene CarriersUnited States
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Shimaa KamalActive, not recruitingGene Mutation in Infantile Onset Diabetes MellitusEgypt
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Bispebjerg HospitalRecruitingMuscle Function | Neuromuscular Electrical Stimulation | Disuse Atrophy (Muscle) of Lower Extremities | Myofibrillar Protein SynthesisDenmark
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National Institutes of Health Clinical Center (CC)RecruitingCerebral Palsy | Muscular Dystrophy | Spina Bifida | Incomplete Spinal Cord InjuryUnited States
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National Institutes of Health Clinical Center (CC)RecruitingCerebral Palsy | Muscular Dystrophy | Spina Bifida | Incomplete Spinal Cord InjuryUnited States
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The Hong Kong Polytechnic UniversityCompletedEndocrine System Diseases | Muscular Atrophy, Spinal | Child With Cancer | Child With Cerebral PalsyChina
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Maastricht University Medical CenterCompletedImmobilization | Neuromuscular Electrical Stimulation | Disuse AtrophyNetherlands
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Radius Pharmaceuticals, Inc.TerminatedInfantile SpasmUnited States
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University of Colorado, DenverMallinckrodtRecruitingInfantile Spasms, Non-IntractableUnited States
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University of Dublin, Trinity CollegeMotor Neurone Disease Association, UK; Irish Research Council, IE; Thierry Latran... and other collaboratorsRecruitingMultiple Sclerosis | Primary Lateral Sclerosis | Postpoliomyelitis Syndrome | Motor Neuron Disease, Amyotrophic Lateral Sclerosis | Motor Neuron Disease Progressive Spinal Muscle AtrophyIreland
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Clinic for Special ChildrenRecruitingMyopathy | Myopathy; Hereditary | Myopathies, Nemaline | TNNT1-associated Myopathy | Infantile-onset Nemaline Rod Myopathy | Myopathy, Rod | Amish Nemaline Myopathy | Nemaline Myopathy 5 | NEM5 | Genetic Muscle Disease | Recessive Hereditary Disorder (Autosomal) | ANMUnited States
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Kullasate SakpichaisakulRecruitingWest Syndrome | Infantile SpasmThailand
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Bio-Pharm Solutions Co., Ltd.TerminatedRefractory Infantile SpasmsUnited States, Korea, Republic of
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UCB Biopharma S.P.R.L.TerminatedInfantile Spasms (IS)France
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CENTOGENE GmbH RostockCompletedScoliosis | Muscular Atrophy | Duchenne Muscular Dystrophy | Lordosis | Muscular Weakness | Increased Lordosis/Scoliosis | Hyporeflexia | Red-Green Color BlindnessEgypt, India, Albania, Pakistan, Georgia, Lebanon, Romania, Sri Lanka
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Bio-Medical Research, Ltd.Liverpool University Hospitals NHS Foundation TrustCompletedKnee Osteoarthritis | Disuse AtrophyUnited Kingdom
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Rigshospitalet, DenmarkCompleted
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University of Erlangen-Nürnberg Medical SchoolRecruitingPompe Disease (Late-onset) | Pompe Disease | Pompe's Disease Juvenile Onset | Pompe Disease Infantile-OnsetGermany
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Novartis PharmaceuticalsTerminatedAge-related Macular Degeneration | Choroidal Neo-Vascular Age-onset Macular DegenerationUnited Kingdom, United States