Clinical Trials on Inherited Metabolic Storage Diseases
Total 61996 results
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Assistance Publique - Hôpitaux de ParisEuropean Leukodystrophy AssociationCompletedLate Infantile Metachromatic LeukodystrophyFrance
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SanofiRecruitingFabry's DiseaseUnited States
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Hospital Clinico Universitario de SantiagoAlvaro Hermida (Co-IP); Susana Belen Bravo; Maria Teresa Cardoso; Cristobal Colon... and other collaboratorsRecruiting
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Amicus Therapeutics France SASCompletedFabry Disease | Anderson Fabry DiseaseFrance
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National Institute of Neurological Disorders and...Completed
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National Human Genome Research Institute (NHGRI)RecruitingDiabetes | Undiagnosed Diseases | Inherited Metabolic Disorders | Batten's Disease | Tay SachsUnited States
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University of PittsburghWithdrawnMetachromatic LeukodystrophyUnited States
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ShireTakeda Development Center Americas, Inc.Active, not recruitingMetachromatic Leukodystrophy (MLD)Denmark, Germany, Japan, Australia, France, Brazil, Czechia
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National Organization for Rare DisordersFood and Drug Administration (FDA)Active, not recruitingMetachromatic LeukodystrophyUnited States
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Institut National de la Santé Et de la Recherche...Assistance Publique - Hôpitaux de Paris; European Leukodystrophy AssociationActive, not recruitingMetachromatic LeukodystrophyFrance
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Shenzhen Geno-Immune Medical InstituteUnknown
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Magenta Therapeutics, Inc.TerminatedInherited Metabolic Disorders (IMD)United States
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Chiesi Farmaceutici S.p.A.ICON plcNot yet recruiting
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UniQure Biopharma B.V.RecruitingFabry DiseaseUnited States
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Brunel UniversityRoyal Free Hospital NHS Foundation TrustRecruiting
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Institut National de la Santé Et de la Recherche...Not yet recruitingFabry Disease
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ShireActive, not recruiting
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SanofiCompletedFabry DiseaseUnited Arab Emirates
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Amicus TherapeuticsActive, not recruitingFabry DiseaseUnited States, United Kingdom
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Idorsia Pharmaceuticals Ltd.Active, not recruitingFabry DiseaseUnited States, United Kingdom, Norway, Germany, Australia, Canada, Spain, Switzerland, Austria, Belgium, France, Netherlands, Poland
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Chiesi ItaliaCompleted
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ProtalixChiesi Farmaceutici S.p.A.CompletedFabry DiseaseAustralia, Netherlands, United Kingdom, Canada, Czechia, Norway, Slovenia
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Freeline TherapeuticsTerminatedLysosomal Storage Diseases | Fabry DiseaseUnited States, Norway, Germany, Austria, United Kingdom, Italy, Canada
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Manchester University NHS Foundation TrustNorthern Care Alliance NHS Foundation TrustActive, not recruiting
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Amicus TherapeuticsCompletedFabry DiseaseJapan, Taiwan, Turkey, United States, Brazil
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ShireNo longer available
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CENTOGENE GmbH RostockShire Human Genetic Therapies, Inc.CompletedCerebrovascular AccidentAustria, Belgium, Croatia, Finland, France, Georgia, Germany, Ireland, Italy, Malta, Poland, Portugal, Spain, United Kingdom
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseFrance, Poland, United States, Russian Federation, United Kingdom
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Lysosomal and Rare Disorders Research and Treatment...SanofiUnknown
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Amicus TherapeuticsCompletedOpen-Label Extension Study of the Long-Term Effects of Migalastat HCL in Patients With Fabry DiseaseFabry DiseaseUnited States, Austria, United Kingdom, Argentina, Australia, Belgium, Brazil, Canada, Denmark, Egypt, France, Italy, Japan, Spain, Turkey
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Genzyme, a Sanofi CompanyTerminatedFabry DiseaseAustria, Brazil, France, United States, Argentina, Belgium, Canada, Finland, Hungary, Norway, Poland, Spain, Taiwan, United Kingdom
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Boston Children's HospitalWithdrawn
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University Hospital, BordeauxCompleted
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Amicus TherapeuticsCompletedFabry DiseaseFrance, Austria, United States, Belgium, Japan, United Kingdom, Denmark, Brazil, Australia, Italy
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Amicus TherapeuticsCompletedFabry DiseaseUnited States, Italy, Spain, Turkey, Brazil, Canada, United Kingdom, France, Poland, Australia, Egypt, Argentina, Denmark
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Amicus TherapeuticsCompletedFabry DiseaseUnited States, Australia, France, United Kingdom, Brazil, Canada
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Amicus TherapeuticsTerminatedFabry DiseaseAustralia, United States, Italy, Spain, Belgium, Turkey, Brazil, Argentina, United Kingdom, Denmark, France, Canada, Egypt
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University Hospital, CaenUnknown
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National Institute of Neurological Disorders and...National Institute of Neurological Disorders and Stroke@@@Shire Human Genetic...Completed
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Genzyme, a Sanofi CompanyCompleted
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Rigshospitalet, DenmarkCompletedFabry DiseaseDenmark
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National Institute of Neurological Disorders and...Completed
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Assistance Publique - Hôpitaux de ParisUnknown
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AceLink Therapeutics, Inc.Tigermed Consulting Co., LtdRecruiting
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Albina Nowak, MDNot yet recruiting
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Chiesi Farmaceutici S.p.A.ICON plcRecruiting
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Children's Hospital Medical Center, CincinnatiSanofiRecruitingFabry DiseaseUnited States
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University of Sao Paulo General HospitalPfizerRecruiting