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Clinical Trials on Inherited Neuromuscular Conditions
Total 437627 results
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National Cancer Institute (NCI)CompletedMetastatic Lung Non-Squamous Non-Small Cell Carcinoma | Recurrent Lung Non-Squamous Non-Small Cell Carcinoma | Stage IV Lung Non-Small Cell Cancer AJCC v7United States
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Brigham and Women's HospitalNational Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingMyocardial Infarction | Heart Diseases | Cardiovascular Diseases | Coronary Disease | Diabetes Mellitus | Angina Pectoris | Menopause | Cerebrovascular Accident | Pulmonary Embolism | Postmenopause
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ProtalixChiesi Farmaceutici S.p.A.CompletedFabry DiseaseUnited States, Serbia, Spain, United Kingdom, Australia, Paraguay
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AVROBIOTerminatedFabry DiseaseAustralia, Brazil
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Aaron FensterCompletedDetermine the Number of Anatomical Sites at Which Successful Thermoacoustic Fat Measurements Can be Made From Five Acquisitions Using the FLIP ITA Device | Determine the Correlation of Fat Measures Obtained by the FLIP Device and Those Obtained From Quantitative MRI | Provide Insight...Canada
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University of Southern CaliforniaNational Cancer Institute (NCI); Society of Thoracic RadiologyActive, not recruitingStage IIA Non-Small Cell Lung Carcinoma | Stage IIB Non-Small Cell Lung Carcinoma | Stage IA Non-Small Cell Lung Carcinoma | Stage IB Non-Small Cell Lung CarcinomaUnited States
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University of California, San FranciscoNational Human Genome Research Institute (NHGRI)CompletedEpilepsy | Cerebral Palsy | Intellectual Disability | Developmental Delay | Metabolic Disease | Neuro-Degenerative Disease | Encephalopathy | Birth Defect | Multiple Congenital Anomaly | Developmental DefectUnited States
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University Medicine GreifswaldCompletedObstructive Sleep Apnea Syndrome | Temporomandibular DisordersGermany
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Novo Nordisk A/SEli Lilly and Company; AstraZeneca; United BioSource, LLCEnrolling by invitationDiabetes Mellitus, Type 2 | Diabetes | Weight Management | Medullary Thyroid CarcinomaUnited States
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Oslo University HospitalEnrolling by invitation
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National Cancer Institute (NCI)CompletedHead and Neck Squamous Cell Carcinoma | Stage IVA Oropharyngeal Carcinoma AJCC v7 | Stage IVB Oropharyngeal Carcinoma AJCC v7United States
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Codiak BioSciencesTerminatedAdvanced Hepatocellular Carcinoma (HCC) | Gastric Cancer Metastatic to Liver | Colorectal Cancer Metastatic to LiverUnited States
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Campus docent Sant Joan de Déu-Universitat de BarcelonaCompletedCOVID-19 Acute Respiratory Distress SyndromeSpain
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ShireTerminatedFabry DiseaseSpain, Greece, Germany, Portugal, Canada, Finland, Poland, Sweden
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Seoul National University Bundang HospitalEnrolling by invitationAcute Myocardial Infarction | Chronic Liver Disease | Benign Breast Disease | Thyroid Disease | Malignant Breast NeoplasmKorea, Republic of
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Chiesi Farmaceutici S.p.A.Chiesi USA, Inc.AvailableFabry DiseaseUnited States
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Massachusetts General HospitalCompleted
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Spark TherapeuticsCompletedLysosomal Storage Diseases | Glycogen Storage Disease Type 2 | Pompe Disease (Late-onset) | Pompe Disease | LOPD | Acid Maltase DeficiencyUnited States, Italy, United Kingdom, Netherlands, France, Germany
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Lundquist Institute for Biomedical Innovation at...Active, not recruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIUnited States
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Indiana UniversityChildren's Therapy of WoodinvilleEnrolling by invitationAnxiety | Autism Spectrum Disorder | Sensory Processing Disorder | Eating Disorders | Swallowing Disorder | Gastro-Intestinal Disorder | Sensory DisordersUnited States
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Fox Chase Cancer CenterNational Cancer Institute (NCI)CompletedStage IA Non-small Cell Lung Cancer | Stage IB Non-small Cell Lung Cancer | Stage IIA Non-small Cell Lung Cancer | Stage IIB Non-small Cell Lung CancerUnited States
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Dayton Children's HospitalActive, not recruitingTraumatic Brain Injury | Intracranial Hemorrhages | Head Trauma | Hematoma of Head | Head Injuries | Craniocerebral Injuries | Head Injury, Minor | Traumatic Brain HemorrhageUnited States
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AmMax Bio, Inc.Merck Sharp & Dohme LLCCompletedColorectal Cancer | Pancreatic Cancer | Non-Small Cell Lung CancerCanada, United States, Australia, Belgium, Spain, Germany
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Universidad Industrial de SantanderUniversity of North Carolina, Chapel HillCompletedMicrocephaly | Mental RetardationColombia
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Sun Yat-sen UniversityJiangsu HengRui Medicine Co., Ltd.Active, not recruitingBrain Metastases | Non-squamous Non-small-cell Lung CancerChina
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Blue Note TherapeuticsTerminatedAnatomic Stage I Breast Cancer AJCC v8 | Anatomic Stage II Breast Cancer AJCC v8 | Anatomic Stage III Breast Cancer AJCC v8 | Stage III Lung Cancer AJCC v8 | Stage II Lung Cancer AJCC v8 | Stage I Lung Cancer AJCC v8United States
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University Hospital Center of MartiniqueCompletedDiabetes Mellitus | Diabetes | Diabetes Complications | Foot Ulcer, DiabeticFrance
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Thomas Jefferson UniversityCompletedStage IVA Lung Cancer AJCC v8 | Stage IVB Lung Cancer AJCC v8 | Lung Non-Small Cell Carcinoma | Stage IV Lung Cancer AJCC v8 | Health Care Provider | Activating ALK Gene Mutation Negative | Activating EGFR Gene Mutation Negative | Activating ROS1 Gene Mutation NegativeUnited States
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Idorsia Pharmaceuticals Ltd.CompletedFabry DiseaseUnited States, Spain, Belgium, Australia, Austria, Canada, Germany, Ireland, Italy, Netherlands, Norway, Poland, Switzerland, United Kingdom
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AudibleHealth AI, Inc.Sunrise Research Institute; Analytical Solutions Group, Inc.; Kelley Medical... and other collaboratorsCompletedCoronavirus Disease 2019 | SARS-CoV-2 Infection | COVID-19 Pandemic | COVID-19 Virus Infection | Coronavirus Disease-19 | COVID-19 Virus Disease | 2019 Novel Coronavirus Disease | 2019 Novel Coronavirus Infection | 2019-nCoV DiseaseUnited States
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Centre de Recherche de l'Institut Universitaire...Canadian Institutes of Health Research (CIHR)CompletedTourette Syndrome | Tourette Syndrome in Children | Tic Disorder, Chronic Motor or VocalCanada
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SanofiTerminatedRetinitis Pigmentosa | Usher SyndromeUnited States, France
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Philogen S.p.A.CompletedBreast Cancer | Solid Tumor | Metastatic Melanoma | Non-small Cell Lung Cancer (NSCLC)Italy
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Novartis PharmaceuticalsCompletedColorectal Cancer, Triple Negative Breast Cancer, NSCLC - AdenocarcinomaUnited States, France, Taiwan, Canada, Italy, Singapore, Belgium, Spain, Israel
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Vanderbilt University Medical CenterCompletedObsessive-Compulsive Disorder | Tourette Syndrome | Sensory DisordersUnited States
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Niguarda HospitalCompletedAcute Coronary Syndrome With ST Elevation on Electrocardiogram | Acute Coronary Syndrome Without ST Elevation on Electrocardiogram | Noncritical Coronary Artery Disease Coronary Stenosis Less Than 50 Per Cent | Aortic AneurysmsItaly
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G.V. (Sonny) Montgomery VA Medical CenterMerck Sharp & Dohme LLCCompletedPatient Adherence, Chronic Hepatitis C, Alcohol-related DisordersUnited States
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Massachusetts General HospitalNational Cancer Institute (NCI)CompletedBrain and Central Nervous System Tumors | Long-term Effects Secondary to Cancer Therapy in ChildrenUnited States
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University of South FloridaUniversity of California, Los Angeles; Temple UniversityCompletedGeneralized Anxiety Disorder | Social Phobia | Separation Anxiety Disorder | Specific Phobia | Autism | Autism Spectrum Disorders | Obsessive-compulsive Disorder | Asperger's Syndrome | Pervasive Developmental Disability - Not Otherwise SpecifiedUnited States
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PharmaMarCompletedEwing's Sarcoma | Primitive Neuroectodermal Tumor (PNET) | Askin's Tumor of the Chest Wall | Extraosseous Ewing's Sarcoma (EOE)France, United States, Italy
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University Hospital, MontpellierCompletedSjogren's Syndrome | ANCA Associated VasculitisFrance
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University Hospital, BordeauxCompletedStroke | Coronavirus Disease 2019 | Acute Myocardial InfarctionFrance
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Charite University, Berlin, GermanyGerman Cancer AidCompletedMalignant Neoplasm of Stomach | Secondary Malignant Neoplasm of Peritoneum | Secondary Malignant Neoplasm of Other and Unspecified SitesGermany
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ShireCompleted
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University of Colorado, DenverColumbia University; Brigham and Women's Hospital; University of Washington; Tulane... and other collaboratorsCompletedDepression | SARS-CoV 2 | Respiratory Failure | Anxiety | Post Traumatic Stress Disorder | Corona Virus Infection | Family Members | Post Intensive Care Unit SyndromeUnited States
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ShireCompleted
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ShireCompletedFabry DiseaseUnited States, Slovenia, Australia, Finland, Poland, Czechia, United Kingdom
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Hospital Universitario Reina Sofia de CordobaCompletedMyocardial Infarction | Diabetes Mellitus | Metabolic Syndrome | Cognitive Decline | Unstable Angina | MalignancySpain
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Zimmer BiometTerminatedJoint Diseases | Osteoarthritis, Hip | Avascular Necrosis of Hip | Congenital Dysplasia of the Hip | Degenerative Joint Disease of Hip | Rheumatoid Arthritis of Hip | Post-Traumatic Osteoarthritis of HipCanada
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University Hospital, MontpellierCompletedIschemic Stroke | Sleep Apnea | Cerebral Infarct | Periodic Limb Movement DisorderFrance