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Clinical Trials on Intrauterine Retardation in United Kingdom
Total 310 results
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Healx LimitedWithdrawnFragile X SyndromeUnited States, Australia
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Elizabeth Berry-KravisNational Institute of Neurological Disorders and Stroke (NINDS); Novartis PharmaceuticalsCompleted
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedRett Syndrome | CDKL5 Disorder | MECP2 Duplication dIsorder | FOXG1 SyndromeUnited States
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JCR Pharmaceuticals Co., Ltd.Enrolling by invitationMucopolysaccharidosis IIUnited States
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REGENXBIO Inc.Enrolling by invitation
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National Human Genome Research Institute (NHGRI)CompletedAutism | Asperger's Syndrome | Rett's DisorderUnited States
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University of Mississippi Medical CenterCompletedAutistic Disorder | Rett Syndrome | Asperger Syndrome | Pervasive Developmental Disorder | Childhood Disintegrative DisorderUnited States
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Rare Thyroid Therapeutics International ABEgetis Therapeutics; AnovoRxAvailableMonocarboxylate Transporter 8 Deficiency | Allan-Herndon-Dudley SyndromeUnited States
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Hoffmann-La RocheCompleted
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Eunice Kennedy Shriver National Institute of Child...University of MinnesotaCompleted
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Nova Mentis Life Science CorpFourthWall TestingRecruitingAutism Spectrum Disorder | Fra(X) SyndromeUnited States
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ShionogiCompletedCerebral Palsy | Sialorrhea | Mental Retardation | Neurological ConditionsUnited States
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RespireRxFRAXA Research FoundationCompletedFragile X Syndrome | AutismUnited States
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Tetra Discovery PartnersRecruitingFragile X SyndromeUnited States
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Tetra Discovery PartnersEnrolling by invitationFragile X SyndromeUnited States
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University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute of... and other collaboratorsCompletedRett Syndrome, Preserved Speech Variant | Mecp2 Duplication Syndrome | Rett-related DisordersUnited States
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Zynerba Pharmaceuticals, Inc.CompletedFragile X SyndromeUnited States, New Zealand, Australia
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Neuren Pharmaceuticals LimitedCompleted
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingAutism Spectrum Disorder | Autistic Disorder | Fragile X Syndrome | Asperger SyndromeUnited States
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National Institute of Mental Health (NIMH)CompletedSchizophrenia | Bipolar Disorder | Attention Deficit Disorder With Hyperactivity | Mental Retardation | Mental Disorder Diagnosed in ChildhoodUnited States
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Eunice Kennedy Shriver National Institute of Child...RecruitingAutism Spectrum Disorder | Fragile X Syndrome | Developmental Delay | Genetic Disorder | Asperger DisorderUnited States
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Lundquist Institute for Biomedical Innovation at...Active, not recruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIUnited States
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Rocket Pharmaceuticals Inc.Recruiting
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Seaside Therapeutics, Inc.Completed
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Rocket Pharmaceuticals Inc.Active, not recruitingDanon DiseaseUnited States
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.TerminatedFragile X SyndromeUnited States
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REGENXBIO Inc.Withdrawn
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ArmaGen, IncCompletedMucopolysaccharidosis IIUnited States, Germany, Philippines
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Rocket Pharmaceuticals Inc.RecruitingDanon DiseaseUnited States
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Stanford UniversityTerminatedFragile X Syndrome (FXS) | Idiopathic Intellectual Developmental Disorder (IDD)United States
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National Human Genome Research Institute (NHGRI)CompletedMental Retardation | Sleep Disorders, Circadian Rhythm | Developmental Delay Disorders | Chromosome Deletion | Self Injurious BehaviorUnited States
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Duke UniversityRecruiting
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International Rett Syndrome FoundationBaylor College of Medicine; Children's Hospital of Philadelphia; University of... and other collaboratorsRecruitingNervous System Diseases | Neurologic Manifestations | Neurobehavioral Manifestations | Genetic Diseases, X-Linked | Intellectual Disability | Neurodevelopmental Disorders | Neurologic Disorder | Rett Syndrome | Genetic Disease | Rett Syndrome, AtypicalUnited States
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Sangamo TherapeuticsTerminatedMucopolysaccharidosis II | MPS IIUnited States
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Lundquist Institute for Biomedical Innovation at...CompletedMucopolysaccharidosis Type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VIUnited States
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Lundquist Institute for Biomedical Innovation at...TerminatedMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIUnited States
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Denali Therapeutics Inc.Enrolling by invitationMucopolysaccharidosis IIUnited States, Canada, Belgium, Czechia, Netherlands
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Jirair Krikor BedoyanUltragenyx Pharmaceutical IncRecruitingPyruvate Dehydrogenase Complex DeficiencyUnited States
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Cyprium Therapeutics, Inc.Enrolling by invitation
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Eunice Kennedy Shriver National Institute of Child...Completed
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Psyadon PharmaCompletedLesch-Nyhan DiseaseUnited States
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University of California, San DiegoBioMarin PharmaceuticalWithdrawnBehavioral Manifestations of Lesch-Nyhan DiseaseUnited States
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Washington University School of MedicineUniversity of Rochester; ResMed Foundation; The Hebrew University Hadassah Medical...TerminatedObstructive Sleep Apnea | Pregnancy Related | Fetal Growth RestrictionUnited States, Israel
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Masonic Cancer Center, University of MinnesotaRecruiting
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University of PittsburghNational Institute of Neurological Disorders and Stroke (NINDS); Rare Diseases...RecruitingPyruvate Dehydrogenase Complex Deficiency DiseaseUnited States
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TakedaTakeda Development Center Americas, Inc.Active, not recruitingHunter SyndromeUnited States, Germany, Malaysia, Philippines, Thailand, Dominican Republic, Serbia, Vietnam
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REGENXBIO Inc.Active, not recruitingMucopolysaccharidosis Type II (MPS II)United States, Canada