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Clinical Trials on Leber Congenital Amaurosis in United States
Total 3906 results
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Boston Children's HospitalMuscular Dystrophy AssociationRecruitingCentronuclear Myopathy | Myotubular Myopathy | Nemaline Myopathy | Central Core Disease | Congenital Fiber Type Disproportion | Multiminicore Disease | Rigid Spine Muscular Dystrophy | Undefined Congenital MyopathyUnited States
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Louisiana State University Health Sciences Center...UnknownBreast Reconstruction | Implant Failure | Congenital Malformations | Micromastia | Breast PtosisUnited States
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National Human Genome Research Institute (NHGRI)RecruitingCongenital Anomaly | Rare Disorders | Intellectual DisabilitiesUnited States
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Mayo ClinicCompletedPregnancy Complications | Congenital Heart DiseaseUnited States
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Emory UniversityChildren's Healthcare of AtlantaCompletedBicuspid Aortic Valve | Congenital Heart DiseaseUnited States
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Children's Healthcare of AtlantaTerminated
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Children's Healthcare of AtlantaCompletedCongenital Defects | Cardiopulmonary Bypass | HemostasisUnited States
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Great Ormond Street Hospital for Children NHS Foundation...CompletedCongenital Talipes Equino VarusUnited Kingdom
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Johns Hopkins UniversityCompletedEpidermolysis Bullosa Simplex | Pachyonychia CongenitaUnited States
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Duke UniversityCompletedHernia, DiaphragmaticUnited States
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Ochsner Health SystemCompletedPain, Acute | Congenital Heart DiseaseUnited States
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University of UtahNational Heart, Lung, and Blood Institute (NHLBI); Primary Children's HospitalRecruitingHypoxia | Neurodevelopmental Disorders | Congenital Heart Disease in Children | Complex Congenital Heart DiseaseUnited States
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Timothy J Nelson, MD, PhDThe Hospital for Sick Children; Mayo Clinic; Children's Hospital of Philadelphia and other collaboratorsActive, not recruitingCongenital Heart Disease, SRV DependentUnited States
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Lori EricksonEnrolling by invitation
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Emory UniversityChildren's healthcare of Atlanta: Cardiac Research Donor FundsCompletedAortic CoarctationUnited States
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Timothy J. NelsonCompletedStudy of Autologous Bone Marrow Derived Mononuclear Cells for Treatment of Ebstein Anomaly (Ebstein)Ebstein AnomalyUnited States
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University of Wisconsin, MadisonCompletedTetralogy of FallotUnited States
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Boston Children's HospitalNational Heart, Lung, and Blood Institute (NHLBI)CompletedHyperglycemia | Heart Defects, CongenitalUnited States
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Palvella Therapeutics, Inc.Active, not recruitingPachyonychia CongenitaUnited States
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Stanford UniversityEnrolling by invitationPulmonary Hypertension | Congenital Heart DiseaseUnited States
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University of MichiganChiesi Farmaceutici S.p.A.TerminatedCongenital Heart Disease | Hypoplastic Left Heart SyndromeUnited States
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University of California, San FranciscoWithdrawnHeart Septal Defects, Ventricular | Atrioventricular Septal DefectUnited States
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Medtronic CardiovascularCompletedCongenital Heart Defects | Dysfunctional Right Ventricular Outflow Tract ConduitsUnited States
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Nemours Children's ClinicThomas Jefferson UniversityRecruitingTetralogy of Fallot | Pulmonary InsufficiencyUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedPulmonary Hypertension | Congenital Heart Disease | Caridovascular DiseaseUnited States
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Golden Jubilee National HospitalCompletedHeart Diseases | Congenital DisorderUnited Kingdom
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Boston Children's HospitalThe Hospital for Sick Children; Baylor College of Medicine; Children's Hospital... and other collaboratorsRecruitingCongenital Heart Disease in ChildrenUnited States, Canada
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Indiana UniversityRecruitingCongenital Heart Defects | Heterotaxy SyndromeUnited States
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Medtronic Heart ValvesCompletedDysfunctional RVOT Conduits in Patients With Congenital Heart DefectsSpain, United States, Austria, Canada
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National Eye Institute (NEI)Completed
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Krystal Biotech, Inc.Not yet recruitingAutosomal Recessive IchthyosisUnited States
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University of UtahCompletedSepsis | Congenital Diaphragmatic Hernia | Neonatal Cardiopulmonary FailureUnited States
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The Cleveland ClinicTerminatedPulmonary InsufficiencyUnited States
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University of California, DavisEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedCongenital Heart DiseaseUnited States
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ActelionHenry Ford Health System; Covance; Medidata Solutions; Almac Clinical Technologies and other collaboratorsTerminatedCongenital Heart Disease With Fontan CirculationUnited Kingdom, Taiwan, France, Poland, China, Australia, Czechia, Canada, United States, Denmark, New Zealand
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Le Bonheur Children's HospitalAbbottNot yet recruiting
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Children's Hospital Medical Center, CincinnatiThrasher Research FundCompletedAcute Kidney Injury | Congenital Heart DiseaseUnited States
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Northwestern UniversityIcahn School of Medicine at Mount SinaiCompletedNetherton Syndrome | Ichthyosis | Lamellar Ichthyosis | Autosomal Recessive Congenital Ichthyosis | Congenital Ichthyosiform Erythroderma | Epidermolytic IchthyosisUnited States
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MD Stem CellsRecruitingGlaucoma | Age-Related Macular Degeneration | Macular Degeneration | Retinitis Pigmentosa | Leber Hereditary Optic Neuropathy | Optic Atrophy | Blindness | Optic Neuropathy | Vision, Low | Retinal Disease | Stargardt Disease | Maculopathy | Retinopathy | Optic Nerve Disease | Nonarteritic Ischemic Optic Neuropathy | Vision... and other conditionsUnited States, United Arab Emirates
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University of Texas Southwestern Medical CenterAmerican Heart AssociationCompletedSingle Ventricle | FontanUnited States
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National Heart, Lung, and Blood Institute (NHLBI)TerminatedMyocardial Infarction | Myocardial Ischemia | Acquired Heart Disease | Atherosclerosis | Congenital Heart DiseaseUnited States
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Baylor College of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedCongenital Heart Disease | Hypoplastic Left Heart Syndrome | Transposition of the Great Arteries | Aortic Arch Hypoplasia or InterruptionUnited States
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingCongenital Heart Disease | Structural Heart Disease | Pulmonary Artery HypertensionUnited States
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Maggie's Pearl, LLCActive, not recruitingPmm2-CDG | Phosphomannomutase 2 Deficiency | Phosphomannomutase 2 Congenital Disorder of Glycosylation | Phosphomannomutase II Congenital Disorder of Glycosylation | Phosphomannomutase II DeficiencyUnited States
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Boston Children's HospitalThe Gerber FoundationCompletedCongenital Heart Disease | Infection | Upper Gastrointestinal Bleeding | Stress UlcerUnited States
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Children's National Research InstituteCompletedAtrial Septal Defect | Cardiac Transplant | Patent Ductus Arterious | Bidirectional Cavopulmonary AnastomosisUnited States
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University of AberdeenCompleted
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University of Wisconsin, MadisonMeriter FoundationRecruiting
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Baylor College of MedicineWithdrawnDevelopmental Dysplasia of the HipUnited States