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Clinical Trials on Leukocyte Adhesion Deficiency 1 (LAD)
Total 538 results
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Rocket Pharmaceuticals Inc.California Institute for Regenerative Medicine (CIRM)CompletedLeukocyte Adhesion Defect - Type ISpain, United States, United Kingdom
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Rocket Pharmaceuticals Inc.WithdrawnLeukocyte Adhesion Defect - Type ISpain
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National Institute of Allergy and Infectious Diseases...Recruiting
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Orpha LabsCompletedLeukocyte Adhesion Deficiency, Type II
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National Cancer Institute (NCI)CompletedLeukocyte Adhesion Deficiency SyndromeUnited States
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National Institute of Allergy and Infectious Diseases...CompletedLeukocyte Adhesion Deficiency SyndromeUnited States
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National Institute of Allergy and Infectious Diseases...CompletedLeukocyte-Adhesion Deficiency SyndromeUnited States
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AUG TherapeuticsRecruitingLeukocyte Adhesion DeficiencyUnited States
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AUG TherapeuticsRecruitingLeukocyte Adhesion DeficiencyUnited States
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Rocket Pharmaceuticals Inc.Enrolling by invitationLeukocyte Adhesion DeficiencySpain, United States, United Kingdom
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National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous Disease (CGD) | X-Linked Severe Combined Immune Deficiency (XSCID) | Leukocyte Adhesion Deficiency 1 (LAD) | Graft Versus Host Disease (cGvHD)United States
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Medical College of WisconsinNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsCompletedChronic Granulomatous Disease | Hemophagocytic Lymphohistiocytosis | Leukocyte Adhesion Deficiency | Chronic Active Epstein-Barr Virus Infection | HIGM-1 | IPEXUnited States, Canada
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Eunice Kennedy Shriver National Institute of Child...University of WashingtonUnknownWiskott-Aldrich Syndrome | Leukocyte Adhesion Deficiency Syndrome | X-Linked Agammaglobulinemia | X-Linked Hyper IgM SyndromeUnited States
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National Cancer Institute (NCI)Recruiting
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Fairview University Medical CenterTerminatedImmunologic Deficiency Syndromes | Common Variable Immunodeficiency | Severe Combined Immunodeficiency | Chronic Granulomatous Disease | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | Graft Versus Host Disease | X-linked Agammaglobulinemia | Chediak-Higashi Syndrome | Virus-Associated... and other conditionsUnited States
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Instituto Nacional de Ciencias Medicas y Nutricion...SuspendedHIV-1-infection | Immune Deficiency | CD4+ T Lymphocytopenia | Immuno-senescenceMexico
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IpsenRecruitingIGF1 DeficiencySpain, United States, Italy, France, United Kingdom, Germany, Austria, French Guiana, Poland, Sweden, Martinique
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IpsenTerminatedIGF-1 DeficiencySpain
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University of Texas Southwestern Medical CenterRecruitingGlucose Transporter Type 1 Deficiency Syndrome | GLUT1 Deficiency Syndrome | Glucose Transporter type1 (GLUT-1) Deficiency | GLUT-1 Deficiency SyndromeUnited States
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University of Texas Southwestern Medical CenterRecruitingGlucose Metabolism Disorders | Epilepsy | Glucose Transporter Type 1 Deficiency Syndrome | Glut1 Deficiency Syndrome 1 | Glut1 Deficiency Syndrome 1, Autosomal Recessive | Glucose Transporter Protein Type 1 Deficiency Syndrome | Glucose Transport DefectUnited States
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Hospices Civils de LyonCompleted
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Assiut UniversityUnknown
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Juan PascualNational Institute of Neurological Disorders and Stroke (NINDS)CompletedGlucose Metabolism Disorders | Epilepsy | Glucose Transporter Type 1 Deficiency Syndrome | Glut1 Deficiency Syndrome 1, Autosomal Recessive | Glucose Transporter Protein Type 1 Deficiency Syndrome | Glucose Transport Defect | GLUT1DS1United States
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University of Texas Southwestern Medical CenterNational Institute of Neurological Disorders and Stroke (NINDS)Active, not recruitingGlucose Metabolism Disorders | Epilepsy | Glucose Transporter Type 1 Deficiency Syndrome | Glut1 Deficiency Syndrome 1, Autosomal Recessive | Glucose Transporter Protein Type 1 Deficiency Syndrome | Glucose Transport Defect | GLUT1DS1United States
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University of FloridaAlpha-1 FoundationEnrolling by invitation
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Thomayer University HospitalMasaryk UniversityRecruiting
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Imagine InstituteRecruiting
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TRPHARMEnrolling by invitationAdenosine Deaminase DeficiencyTurkey
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University of Sao PauloCompleted
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National Institute of Allergy and Infectious Diseases...CompletedHIV-1 Infection | HIV Antibodies | Neutralizing Antibody | Viral Load | Monoclonal AntibodyUnited States
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Prothya BiosolutionsLandsteiner Foundation for Blood TransfusionCompletedNeutropenia | MBL-DeficientNetherlands
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Michael Campos, MDCSL BehringCompletedAlpha 1 Antitrypsin DeficiencyUnited States
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University of PittsburghNational Heart, Lung, and Blood Institute (NHLBI)CompletedAlpha 1 Antitrypsin Deficiency | AATDUnited States
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FDA Office of Orphan Products DevelopmentBezoloven, Inc.WithdrawnVitamin D Deficiency | Lead PoisoningUnited States
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Washington University School of MedicineNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); N... and other collaboratorsTerminatedLiver Cirrhosis | Alpha-1-antitrypsin DeficiencyUnited States
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Alnylam PharmaceuticalsTerminatedZZ Type Alpha-1 Antitrypsin Deficiency Liver DiseaseUnited Kingdom
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Juan PascualNo longer availableGlucose Transporter Type 1 Deficiency Syndrome | Glut1 Deficiency SyndromeUnited States
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Juan PascualCompletedGlucose Transporter Type 1 Deficiency Syndrome | GLUT1 Deficiency SyndromeUnited States
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Juan PascualWithdrawnGlucose Transporter Type 1 Deficiency Syndrome | Glut1 Deficiency SyndromeUnited States
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Children's Hospital Los AngelesCompletedType 1 Diabetes | Vitamin D Deficiency/InsufficiencyUnited States
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Heidelberg UniversityTerminatedHereditary Emphysema (Alpha 1-antitrypsin Deficiency)Germany
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Grifols Therapeutics LLCCompletedEmphysema | Alpha 1-antitrypsin Deficiency (AATD)United States
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University Hospital, Strasbourg, FranceCompletedPrimary Immune-Deficiency (PID) Common Variable Immune Deficiency (CVID)France
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Mayo ClinicTerminatedCardiopulmonary BypassUnited States
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Grifols Therapeutics LLCActive, not recruitingPulmonary Emphysema in Alpha-1 PI DeficiencyUnited States, Australia, Denmark, New Zealand, Estonia, Poland, Russian Federation, Sweden, Brazil, Canada, France, Finland
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Schön Klinik Berchtesgadener LandGrifols Therapeutics LLC; Alpha-1 FoundationCompletedChronic Obstructive Pulmonary Disease | Alpha-1-antitrypsin-deficiencyGermany
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Baxalta now part of ShireArriva Pharmaceuticals, Inc.CompletedAlpha1-antitrypsin DeficiencyUnited States
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Grifols Therapeutics LLCCompletedAlpha₁-Antitrypsin DeficiencyUnited States
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IpsenTerminatedrhGH and rhIGF-1 Combination Therapy in Children With Short Stature Associated With IGF-1 DeficiencyInsulin-like Growth Factor-1 DeficiencyUnited States
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Grifols Therapeutics LLCGrifols Japan K.K.CompletedAlpha1-Antitrypsin DeficiencyJapan