- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Lipid Metabolism, Inborn Errors
Total 7146 results
-
ISU Abxis Co., Ltd.CompletedGaucher DiseaseAustralia
-
ProtalixCompleted
-
ISU Abxis Co., Ltd.Withdrawn
-
Genzyme, a Sanofi CompanyCompleted
-
ProtalixCompleted
-
University Hospital, Clermont-FerrandUnknown
-
Brigham and Women's HospitalGenzyme, a Sanofi CompanyUnknown
-
ProtalixCompleted
-
TakedaActive, not recruiting
-
CENTOGENE GmbH RostockActive, not recruiting
-
Lysosomal and Rare Disorders Research and Treatment...UnknownGaucher DiseaseUnited States
-
PfizerCompletedGaucher DiseaseIsrael, South Africa, Paraguay
-
PfizerCompletedGaucher DiseaseUnited States, Chile, United Kingdom, Israel, Canada, Spain, South Africa, Italy
-
Hospital St. Joseph, Marseille, FranceCompleted
-
Assistance Publique - Hôpitaux de ParisCompletedGaucher DiseaseFrance
-
Amicus TherapeuticsCompleted
-
Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Lipid Metabolism, Inborn Errors | Hypobetalipoproteinemias | Hypolipoproteinemias | Hypolipopro... and other conditionsNetherlands
-
Visirna Therapeutics HK LimitedNot yet recruitingFamilial Chylomicronemia Syndrome
-
Emily de los ReyesRecruitingBatten Disease | CLN6United States
-
Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeSpain, United Kingdom, France, Canada, United States, Italy, Netherlands, Norway, Portugal, Slovakia, Sweden
-
Ionis Pharmaceuticals, Inc.AvailableFamilial Chylomicronemia Syndrome
-
Jiangsu HengRui Medicine Co., Ltd.CompletedMixed Hyperlipidemia | Non-familial HypercholesterolemiaChina
-
UniQure Biopharma B.V.CompletedLipoprotein Lipase Deficiency | Familial Hyperlipoproteinemia Type 1 | Familial HyperchylomicronemiaGermany
-
Karolinska InstitutetEnrolling by invitationHypercholesterolemia | Familial HypercholesterolemiaSweden
-
University of AlicanteCompletedHypertension | Obesity | Body Weight | Diet, Healthy | Machine Learning | Cholesterol; LipidosisSpain
-
Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedFamilial Chylomicronemia SyndromeUnited States, Brazil, Canada, France, Germany, Hungary, Israel, Italy, Netherlands, South Africa, Spain, United Kingdom
-
Organon and CoCompletedPrimary Hypercholesterolemia and Homozygous Familial Hypercholesterolemia (HoFH)
-
REGENXBIO Inc.CompletedHomozygous Familial Hypercholesterolemia (HoFH)United States
-
National Taiwan University HospitalUnknownFamilial HypercholesterolemiaTaiwan
-
StemCells, Inc.WithdrawnNeuronal Ceroid LipofuscinosisUnited States
-
ShireTerminated
-
TakedaCompleted
-
Genzyme, a Sanofi CompanyCompletedGaucher DiseaseCanada, Russian Federation, Tunisia
-
ShireCompleted
-
PfizerCompletedGaucher DiseaseUnited Kingdom, Canada, Israel, United States, Australia, Spain
-
PfizerCompletedGaucher DiseaseChile, United Kingdom, Canada, Spain, Israel, United States, Australia, South Africa
-
PfizerCompletedGaucher DiseaseIsrael, Paraguay, South Africa
-
Yasmeen Abd Elbaset HamzaaUnknownGaucher Disease
-
Genzyme, a Sanofi CompanyCompletedGaucher DiseaseUnited States
-
Genzyme, a Sanofi CompanyCompletedGaucher DiseaseUnited States, Sweden, India, Netherlands, Austria, Japan, China, Serbia, France, Croatia, Australia, Portugal, Canada, Brazil, Greece, Romania, Russian Federation
-
ISU Abxis Co., Ltd.Completed
-
Odense University HospitalRecruitingAtherosclerosis | Familial HypercholesterolemiaDenmark
-
Assistance Publique - Hôpitaux de ParisRecruitingAtherosclerosis | Familial HypercholesterolemiaFrance
-
Edison Pharmaceuticals IncTerminated
-
AlexionCompletedWolman Disease | Lysosomal Acid Lipase DeficiencyUnited States, Canada, United Kingdom, Italy, France
-
University of LeipzigCompletedCoronary Disease | HypolipoproteinemiaGermany
-
Fondazione SISA (Societa Italiana per lo Studio...Recruiting