- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Lipidoser
Total 568 results
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Polaryx Therapeutics, Inc.Not yet recruitingJuvenile Neuronal Ceroid Lipofuscinosis
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REGENXBIO Inc.Active, not recruitingNeuronal Ceroid Lipofuscinosis Type 2United Kingdom
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CENTOGENE GmbH RostockWithdrawnCholesterol Ester Storage Disease | Acid Lipase Deficiency | Acid Cholesteryl Ester Hydrolase Deficiency, Wolman TypeGermany, India, Sri Lanka
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University of RochesterBatten Disease Support and Research Assocation (BDSRA)CompletedJuvenile Neuronal Ceroid LipofuscinosisUnited States
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StemCells, Inc.CompletedNeuronal Ceroid LipofuscinosisUnited States
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Assiut UniversityNot yet recruitingPsychiatric Problem | Wolman Disease
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | Cholesterol Ester Storage Disease(CESD) | LAL-DeficiencyFrance, United States, United Kingdom, Czechia
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Hospices Civils de LyonUnknownLiver Post-transplant PatientsFrance
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | LAL-Deficiency | Cholesterol Ester Storage Disease (CESD)France, United Kingdom, United States, Canada, Czechia
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Eunice Kennedy Shriver National Institute of Child...RecruitingBatten Disease | Juvenile Neuronal Ceroid Lipofuscinosis (CLN3)United States
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TakedaActive, not recruiting
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CENTOGENE GmbH RostockActive, not recruiting
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Amicus TherapeuticsTerminatedBatten Disease | Neuronal Ceroid Lipofuscinosis CLN6 | Neuronal Ceroid Lipofuscinosis CLN3United States
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Amicus TherapeuticsCompletedVariant Late-Infantile Neuronal Ceroid LipofuscinosisUnited States
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Lysosomal and Rare Disorders Research and Treatment...UnknownGaucher DiseaseUnited States
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PfizerCompletedGaucher DiseaseIsrael, South Africa, Paraguay
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PfizerCompletedGaucher DiseaseUnited States, Chile, United Kingdom, Israel, Canada, Spain, South Africa, Italy
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Hospices Civils de LyonUnknownPatients Waiting for a Liver Transplant.France
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Nationwide Children's HospitalMassachusetts General HospitalCompletedNeuronal Ceroid Lipofuscinosis | Batten's DiseaseUnited States
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Hospital St. Joseph, Marseille, FranceCompleted
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Assistance Publique - Hôpitaux de ParisCompletedGaucher DiseaseFrance
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Amicus TherapeuticsCompleted
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University of MinnesotaRecruitingGaucher DiseaseUnited States
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TakedaNot yet recruiting
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Duke UniversityRecruiting
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TakedaCompletedGaucher DiseaseUnited States
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ShireCompletedGaucher DiseaseIndia
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PfizerCompleted
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ShireQuintiles, Inc.Completed
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ISU Abxis Co., Ltd.CompletedGaucher DiseaseAustralia
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ProtalixCompleted
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ISU Abxis Co., Ltd.Withdrawn
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | Cholesterol Ester Storage Disease(CESD)United States, United Kingdom, France, Canada, Czech Republic, Italy, Poland, Switzerland
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Genzyme, a Sanofi CompanyCompleted
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ProtalixCompleted
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University Hospital, Clermont-FerrandUnknown
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Brigham and Women's HospitalGenzyme, a Sanofi CompanyUnknown
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ProtalixCompleted
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ShireTerminated
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BioMarin PharmaceuticalActive, not recruitingLate-Infantile Neuronal Ceroid Lipofuscinosis Type 2United States
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TakedaCompleted
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Genzyme, a Sanofi CompanyCompletedGaucher DiseaseCanada, Russian Federation, Tunisia
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REGENXBIO Inc.WithdrawnNeuronal Ceroid Lipofuscinosis Type 2 (CLN2)
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ShireCompleted
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Weill Medical College of Cornell UniversityNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes... and other collaboratorsCompletedBatten Disease | Late Infantile Neuronal Ceroid LipofuscinosisUnited States
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PfizerCompletedGaucher DiseaseUnited Kingdom, Canada, Israel, United States, Australia, Spain