- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Liver Fat in Australia
Total 1775 results
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Catabasis PharmaceuticalsCompletedMuscular Dystrophy, DuchenneUnited States, Canada, Australia, United Kingdom, Germany, Ireland, Israel, Sweden
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ApcinteX LtdCentessa Pharmaceuticals plcRecruitingHemophilia A | Hemophilia BSpain, Taiwan, United Kingdom, Italy, Germany, United States, South Africa, Australia, Poland, Armenia, France, India, Canada, Brazil, Turkey, Egypt
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AlbireoRecruitingBiliary AtresiaNetherlands, United States, Spain, Italy, Taiwan, Korea, Republic of, France, Germany, United Kingdom, Canada, Belgium, China, Australia, Poland, Turkey, Malaysia, New Zealand, Hungary, Israel
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Belgium, Netherlands, Australia, Germany, Ireland, United Kingdom
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Spain, Australia, United Kingdom, Germany, Ireland
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AEterna ZentarisCompletedGrowth Hormone Deficiency With Pituitary AnomaliesUnited Kingdom, United States, France, Poland, Spain, Austria, Germany, Italy, Serbia
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KalVista Pharmaceuticals, Ltd.RecruitingHereditary AngioedemaUnited States, Bulgaria, France, Greece, Hungary, Israel, Italy, Netherlands, New Zealand, North Macedonia, Poland, Spain, United Kingdom, Australia, Germany, South Africa, Austria, Portugal, Slovakia, Romania, Canada, Saudi Arabia, Japa...
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II;Pompe's DiseaseCzechia, Taiwan, Belgium, Germany, Korea, Republic of, United States, Argentina, Australia, Austria, Brazil, Canada, Denmark, France, Hungary, Italy, Japan, Mexico, Netherlands, Poland, Portugal, Russian Federation, Spain, Switzerland, Turk... and more
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PfizerCompletedHemophilia AUnited States, Argentina, Austria, Colombia, Croatia, Jordan, Mexico, New Zealand, Oman, Peru, Poland, Romania, Turkey
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Novo Nordisk A/SActive, not recruitingHaemophilia A With Inhibitors | Haemophilia ASpain, Korea, Republic of, Canada, United Kingdom, United States, Germany, South Africa, Italy, Austria, Belgium, France, Japan
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Regeneron PharmaceuticalsSanofiCompletedAtopic DermatitisGermany, Poland, Belgium, Netherlands, Russian Federation, Ireland, United Kingdom, Slovakia, Austria, Spain
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Belgium, Netherlands, United Kingdom, Canada, Australia, France, Germany, Italy, Czechia, Austria, Sweden, Greece
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Clementia Pharmaceuticals Inc.TerminatedExostoses, Multiple HereditaryUnited States, Spain, Canada, Japan, Italy, Portugal, United Kingdom, Turkey, Australia, Belgium, France, Netherlands
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Spruce BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, Australia, Brazil, Canada, Denmark, Estonia, Germany, Ireland, Italy, Korea, Republic of, Latvia, Lithuania, Netherlands, Poland, Romania, Spain, Sweden, Switzerland, Turkey, United Kingdom
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Mukoviszidose Institut gGmbHCompletedCystic FibrosisGermany, Italy, Ireland, Austria, Belgium, Hungary, Poland, Spain, Sweden
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AstraZenecaMerck Sharp & Dohme LLCActive, not recruitingNeurofibromatosis 1 | Plexiform Neurofibroma (PN)United States, Canada, France, Italy, Germany, China, United Kingdom, Spain, Japan, Russian Federation, Australia, Poland, Brazil
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BUnited States, Australia, Canada, China, France, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Germany, India, Italy, Japan, South Africa, Spain, Taiwan
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Amicus TherapeuticsCompletedFabry DiseaseUnited States, Italy, Spain, Turkey, Brazil, Canada, United Kingdom, France, Poland, Australia, Egypt, Argentina, Denmark
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, Belgium, Australia, Canada, France, Germany, Israel, Italy, Spain, Sweden, United Kingdom
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Vertex Pharmaceuticals IncorporatedCompletedCystic Fibrosis, Homozygous for the F508del CFTR MutationUnited States, Germany, Canada, Netherlands, Czech Republic, Italy, Ireland, Sweden, United Kingdom, Australia, France
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Belgium, Netherlands, United Kingdom, Canada, Germany, Australia, France, Italy, Czechia, Austria, Greece, Sweden
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AbbottCompletedSevere Respiratory Syncytial Virus InfectionAustria, Belgium, France, Germany, Italy, Norway, Poland, Slovenia, Spain, United Kingdom
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TakedaOvid Therapeutics Inc.CompletedEpilepsy | Dravet Syndrome | Lennox-Gastaut SyndromeUnited States, Canada, Israel, Poland, Spain, Australia, China, Portugal
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Hoffmann-La RocheCompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, Australia, Japan, France, Netherlands, Spain, Argentina, Germany, Italy, United Kingdom, Sweden
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Baxalta now part of ShireBaxalta Innovations GmbH, now part of ShireCompletedHemophilia AUnited States, Belgium, France, Norway, Netherlands, Austria, Hungary, Italy, Poland, Portugal, Romania, Russian Federation, Spain, Sweden
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Galderma R&DCompletedAtopic DermatitisUnited States, France, Poland, Germany, Australia, Canada
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Lundbeck LLCCompletedEpilepsy | Epilepsy, Generalized | SeizuresUnited States, Belarus, India, Australia, Lithuania
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Galderma R&DActive, not recruitingModerate-to-Severe Atopic DermatitisUnited States, Australia, Austria, Belgium, Bulgaria, Canada, Czechia, Estonia, France, Georgia, Germany, Hungary, Italy, Korea, Republic of, Latvia, Lithuania, Netherlands, New Zealand, Poland, Singapore, Spain, United Kingdom
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Novo Nordisk A/SRecruitingGrowth Hormone Disorder | Growth Hormone Deficiency in ChildrenUnited States, Japan, Israel, India, Austria, Slovenia, Belgium, Brazil, France, Germany, Sweden, Turkey, Ukraine
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Ascendis Pharma A/SCompletedEndocrine System Diseases | Pituitary Diseases | Hormone Deficiency | Growth Hormone Deficiency, PediatricUnited States, Armenia, Belarus, Bulgaria, Georgia, Greece, Russian Federation, Ukraine, Australia, New Zealand, Poland
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Teva Branded Pharmaceutical Products R&D, Inc.Nuvelution TS Pharma, Inc.CompletedTourette SyndromeUnited States, Argentina, Australia, Colombia, Hungary, Italy, Korea, Republic of, Mexico, Poland, Ukraine
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Baxalta now part of ShireTakeda Development Center Americas, Inc.RecruitingVon Willebrand Disease (VWD)United States, Italy, Spain, Netherlands, Turkey, France, Austria, Germany, Russian Federation
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsSaudi Arabia, Algeria, Turkey, Germany, Poland, Netherlands, Italy, Belgium, South Africa, United Kingdom, Sweden, Austria, Portugal, France, Czech Republic, Venezuela
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SanofiRecruitingDermatitis AtopicIsrael, Chile, Australia, United States, Canada, Korea, Republic of, Taiwan, China
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Eli Lilly and CompanyDermira, Inc.Active, not recruitingAtopic DermatitisUnited States, Spain, Canada, France, Korea, Republic of, Taiwan, Australia, Germany, Bulgaria, Estonia, Latvia, Lithuania, Mexico, Poland, Singapore, Ukraine
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Palladio BiosciencesCentessa Pharmaceuticals plcTerminatedAutosomal Dominant Polycystic Kidney | ADPKDUnited States, Spain, Hungary, United Kingdom, Australia, Bulgaria, Poland, Turkey
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BioMarin PharmaceuticalRecruitingHypochondroplasiaUnited States, Spain, Canada, France, Japan, Australia, Italy, Argentina, Brazil, Germany, United Kingdom
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Medivation, Inc.PfizerCompletedHuntington DiseaseGermany, Canada, United States, Denmark, United Kingdom, Australia, Sweden
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Novartis Gene TherapiesActive, not recruitingSMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type I | Spinal Muscular Atrophy Type IIIUnited States, Belgium, France, Japan, United Kingdom, Italy, Taiwan, Australia, Canada
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Gilead SciencesTerminatedHypertrophic CardiomyopathyAustralia, United States, Netherlands, Israel, Italy, France, Germany, United Kingdom
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Translational Research Center for Medical Innovation...RecruitingNeutral Lipid Storage DiseaseChina, United States, France, Austria, Germany, Italy, Japan, Netherlands, United Kingdom
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease (Late-Onset) | Glycogenesis Type II | Acid Maltase Deficiency (AMD)United States, France, Canada, Netherlands, Australia
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Alexion Pharmaceuticals, Inc.Enrolling by invitationHypophosphatasia (HPP)United States, Italy, Russian Federation, Spain, United Kingdom, Germany, Canada, France, Saudi Arabia, Poland, Australia
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Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Belgium, Australia, Israel, Switzerland, Germany, France, Canada, Denmark, Indonesia, Italy, Netherlands, Spain, Sweden, Turkey, United Kingdom
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ApcinteX LtdCentessa Pharmaceuticals plcRecruitingHemophilia A | Hemophilia BUnited States, Italy, Spain, Taiwan, Australia, Belgium, United Kingdom, France, Germany, India, South Africa, Canada, Poland, Armenia, Turkey
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BUnited States, Australia, China, Denmark, France, Israel, Japan, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Germany, India, South Africa, Spain, Taiwan, Hungary, Italy
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Viridian Therapeutics, Inc.Active, not recruitingThyroid Eye DiseaseUnited States, Spain, United Kingdom, Canada, Germany, Italy, Netherlands, Australia, France, Turkey
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Chile, France, Germany, Italy, Japan, Netherlands, Portugal, Spain, Tunisia, Turkey, United Kingdom
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Yale UniversityNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health...CompletedHypertrophic Cardiomyopathy | Long QT SyndromeUnited States, United Kingdom, Canada, Australia, New Zealand
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AnaptysBio, Inc.RecruitingAtopic Dermatitis EczemaGeorgia, United States, Australia, Canada, Czechia, New Zealand, Poland