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Clinical Trials on Long-chain Fatty Acid Oxidation Disorders \(LC-FAOD\)
Total 25 results
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Academisch Medisch Centrum - Universiteit van Amsterdam...Stichting StofwisselkrachtNot yet recruitingLong-chain Fatty Acid Oxidation Disorders \(LC-FAOD\)Netherlands
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Ultragenyx Pharmaceutical IncRecruitingLong-chain Fatty Acid Oxidation Disorders (LC-FAOD)Turkey, United Kingdom, Spain, Saudi Arabia, Poland, Czechia, Germany
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Ultragenyx Pharmaceutical IncCompletedLong-chain Fatty Acid Oxidation Disorders (LC-FAOD)United States
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Ultragenyx Pharmaceutical IncTerminatedLong-chain Fatty Acid Oxidation Disorders (LC-FAOD)United States
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Ultragenyx Pharmaceutical IncRecruitingLong-chain Fatty Acid Oxidation Disorders (LC-FAOD)United States, Canada
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Ultragenyx Pharmaceutical IncCompletedLong-chain Fatty Acid Oxidation Disorders (LC-FAOD) | Very Long Chain Acyl-CoA Dehydrogenase (VLCAD) Deficiency | Trifunctional Protein (TFP) Deficiency | Carnitine Palmitoyltransferase (CPT II) Deficiency | Longchain 3-hydroxy-acyl-CoA Dehydrogenase (LCHAD) DeficiencyUnited States, United Kingdom
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Maria Luz Couce PicoFundación Ramón DomínguezWithdrawnLong-chain Fatty Acid Transport DeficiencySpain
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Reneo Pharma LtdCompletedFatty Acid Oxidation DisordersUnited States, France, Spain
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Reneo Pharma LtdCompletedFatty Acid Oxidation DisorderUnited States, Spain, France, Austria, Poland, Belgium, Czechia, Denmark, Hungary, Italy, United Kingdom
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Dr. Schär AG / SPACompletedFatty Acid Oxidation DisorderRussian Federation
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Dr. Schär AG / SPACompletedEpilepsy | Ketosis | Malabsorption | Fatty Acid Oxidation Disorder | Ketogenic Diet | Medium Chain TriglyceridesUnited Kingdom
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University...RecruitingEnd Stage Liver Disease | Mitochondrial Diseases | Acute Liver Failure | Respiratory Chain Deficiencies, Mitochondrial | Disorder of Fatty Acid OxidationUnited States, Canada
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Southeast University, ChinaZhongda Hospital; Chinese Nutrition SocietyActive, not recruitingMetabolic Diseases | Dyslipidemias | Oxidative Stress | Immune System Disorder | Fatty Acid Metabolism DisorderChina
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Dr. Schär AG / SPACompletedEpilepsy | Ketosis | Malabsorption | Fatty Acid Oxidation Disorder | Ketogenic DietUnited Kingdom
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Temple UniversityCompletedDiabetes Mellitus | Insulin Resistance | Other Fatty Acid Oxidation DisordersUnited States
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University of LeicesterCompletedDiabetes Mellitus, Type 2 | Metabolic Disturbance | Fatty Acid Oxidation Disorder | Metabolic CardiomyopathyUnited Kingdom
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University of NottinghamCompletedOxidative Stress | Hepatic Fatty Acid Metabolism | Systemic Insulin Resistance | Cardiovascular StatusUnited Kingdom
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University Medical Center GroningenUMC Utrecht; University of Oxford; Academisch Medisch Centrum - Universiteit... and other collaboratorsCompletedVLCAD Deficiency | Fatty Acid Oxidation DefectsNetherlands
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West Kazakhstan Medical UniversityRecruitingOrnithine Transcarbamylase Deficiency | Biotinidase Deficiency | Citrullinemia | Glutaric Acidemia Type II | Argininosuccinic Aciduria | Maple Syrup Urine Disease | Primary Carnitine Deficiency | Homocystinuria | Carnitine Palmitoyltransferase II Deficiency | Arginase Deficiency | Very Long-chain Acyl-CoA... and other conditionsKazakhstan
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Children's National Research InstituteNational Center for Advancing Translational Sciences (NCATS)RecruitingHypoxic-Ischemic Encephalopathy | Urea Cycle Disorder | Organic Acidemia | Fatty Acid Oxidation Disorder | Maple Syrup Urine Disease | Glutaric Acidemia IUnited States
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Faculty Hospital Kralovske VinohradyCompletedObstructive Sleep Apnea | Continuous Positive Airway Pressure | Fatty Acid MetabolismCzechia
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Rigshospitalet, DenmarkUnknownCarbohydrate Metabolism, Inborn Errors | Metabolism, Inborn Errors | Lipid Metabolism, Inborn Errors | Glycogen Storage Disease Type II | Glycogen Storage Disease Type V | VLCAD Deficiency | Glycogen Storage Disease Type III | Phosphoglycerate Kinase Deficiency | Neutral Lipid Storage Disease | Carnitine... and other conditionsDenmark
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University of PittsburghSuspendedMultiple Sclerosis | Diabetes Mellitus | Chronic Kidney Diseases | Gastritis | Rheumatoid Arthritis | Chronic Pain | Irritable Bowel Syndrome | Hepatitis | Inflammatory Bowel Diseases | Dyslipidemias | Chronic Disease | Celiac Disease | Cholecystitis | Crohn Disease | Cystic Fibrosis | Chronic Pancreatitis | NASH - Nonalcoholic... and other conditionsUnited States
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States