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Clinical Trials on MPS - Mucopolysaccharidosis
Total 803 results
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CelgeneCompletedMyelodysplastic Syndromes (MDS) | Chronic Myelomonocytic Leukemia (CMML) | Acute Myelogenous Leukemia (AML)United States
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National Institute of Allergy and Infectious Diseases...Autoimmunity Centers of Excellence; Clinical Trials in Organ Transplantation...CompletedSevere Acute Respiratory Syndrome Coronavirus 2 (SARS-CoV-2) | Coronavirus Disease 2019 (COVID-19) | Multisystem Inflammatory Syndrome in Children (MIS-C)United States
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University Health Network, TorontoNovartis PharmaceuticalsCompletedMyelofibrosis (MF) | Myeloproliferative Neoplasms (MPN) | Polycythemia Vera (PV) | Essential Thrombocythemia (ET)Canada
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Targazyme, Inc.UnknownLymphoma | Leukemia | Hodgkin's Lymphoma | Transplantation Infection | Myelodysplastic Syndrome (MDS) | Non-Hodgkin's Lymphoma (NHL) | Blood And Marrow TransplantationUnited States
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedMicroscopic Polyangiitis (MPA) | Granulomatosis With Polyangiitis (Wegener's) (GPA)United States, Belgium, France, United Kingdom, Denmark, Canada, Japan, Australia, New Zealand, Sweden, Czechia, Italy, Greece, Mexico, Norway
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University of California, San FranciscoUnited States Department of DefenseRecruitingDepression | Multiple Sclerosis | MSUnited States
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US Department of Veterans AffairsCompletedMS (Multiple Sclerosis)United States
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National Heart, Lung, and Blood Institute (NHLBI)Children's National Research InstituteCompletedLymphoma, Non-Hodgkin | MDS (Myelodysplastic Syndrome) | Myeloproliferative Disorder | ALL (Acute B-Lymphoblastic Leukemia) | AML (Acute Myelogenous LeukemiaUnited States
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CelgeneCompletedMultiple Myeloma | Non-Hodgkin's Lymphoma | AML | Solid Tumors | MDS | Hodgkin's DiseaseUnited States
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Joanne Kurtzberg, MDAldagenCompletedAnemia, Aplastic | MDS | Inborn Errors of Metabolism | Congenital Marrow Failure | Congenital Immunodeficiency SyndromeUnited States
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Novartis PharmaceuticalsCompletedThalassemia, Non-transfusional-dependent Thalassemia (NTDT), Myeloplastic Dysplasia (MDS), Other AnemiaAustralia
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Jazz PharmaceuticalsTerminatedMultiple Sclerosis (MS)United States, Poland, Czechia, United Kingdom, Romania
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St. Jude Children's Research HospitalKaryopharm Therapeutics IncCompletedAcute Myeloid Leukemia (AML) | Acute Lymphoblastic Leukemia (ALL) | Myelodysplastic Syndrome (MDS) | Mixed Phenotype Acute Leukemia (MPAL)United States
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National Cancer Institute (NCI)Enrolling by invitationAcute Lymphoblastic Leukemia | Acute Myelogenous Leukemia | Non-Hodgkins Lymphoma | Myelodysplastic Syndrome (MDS) | Hodgkins LymphomaUnited States
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Constellation PharmaceuticalsThe Leukemia and Lymphoma SocietyActive, not recruitingNeoplasms | Neoplasms by Histologic Type | Leukemia | Preleukemia | Primary Myelofibrosis | Myeloproliferative Disorders | Myelofibrosis | Precancerous Conditions | Myelodysplastic/Myeloproliferative Neoplasm | Myelodysplastic Syndrome (MDS) | Leukemia, Myelocytic, Acute | Bone Marrow Disease | Hematological Disease and other conditionsCanada, United States, United Kingdom, Germany, Italy, Belgium, France, Netherlands, Poland
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Gamida Cell ltdCompletedNon-Hodgkin's Lymphoma | Acute Lymphoblastic Leukemia (ALL) | Myelodysplastic Syndrome (MDS) | Hodgkin's Disease | Acute Myelogenous Leukemia (AML)United States
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Tragara Pharmaceuticals, Inc.CompletedMultiple Myeloma | AML | Blast Crisis | MDS | ALLUnited States
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AmgenTerminatedAcute Myeloid Leukemia | Multiple Myeloma | AML | Myelodysplastic Syndrome | MDS | Non-Hodgkins Lymphoma | NHLUnited States, Australia, Italy, France, Greece, Japan
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAcute Myeloid Leukemia (AML) | Myelodysplastic Syndrome (MDS) | Chronic Myeloid Leukemia (CML)United States
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Regeneron PharmaceuticalsCompletedGenetic Diseases, Inborn | Familial Cold Autoinflammatory Syndrome (FCAS) | Familial Cold Urticaria | Muckle-Wells Syndrome (MWS)United States
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Sheikh Shakhbout Medical CityRecruitingSpasticity, Muscle | Sclerosis, Multiple | Spastic | MS (Multiple Sclerosis)United Arab Emirates
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Assistance Publique Hopitaux De MarseilleCompletedThalassemia Major (TM) | Thalassemia Intermedia (TI) | Microparticles (MP)Originating From Platelets, Endothelial Cells and MonocytesFrance
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Stony Brook UniversityNovartisCompletedMultiple Sclerosis | Cognitive Deficits | Gilenya Modifying Therapy for MSUnited States
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National Institute of Allergy and Infectious Diseases...CompletedDoxycycline to Treat Mansonella Perstans Infection in Patients With and Without Lymphatic FilariasisMansonella Perstans Infection | Mp MicrofilaremiaUnited States
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Franziska WachterHarvard Clinical and Translational Science Center (Harvard Catalyst)RecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | MDS | Aml | Myeloid Neoplasm | Myeloid Malignancies | Inherited Bone Marrow Failure SyndromeUnited States
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Adlai Nortye Biopharma Co., Ltd.Merck Sharp & Dohme LLCActive, not recruitingCervical Cancer | Triple-negative Breast Cancer | NSCLC, Squamous or Non-Squamous | Urothelial Carcinoma of the Bladder | Microsatellite Stable (MSS) Colorectal Cancer (CRC)United States, France
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National Heart, Lung, and Blood Institute (NHLBI)CompletedMDS | Chronic Lymphocytic Leukemia (CLL) | Acute Lymphoblastic Leukemia (ALL) | Acute Myelogenous Leukemia (AML) | Chronic Myelogenous Leukemia (CML)United States
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Qilu Hospital of Shandong UniversityUnknownMS (Multiple Sclerosis) | NMO Spectrum Disorder
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAcute Lymphoblastic Leukemia | Chronic Myelogenous Leukemia | Myelodysplastic Syndrome (MDS) | CLL (Chronic Lymphocytic Leukemia) | CML (Chronic Myelogenous LeukemiaUnited States
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Alaunos TherapeuticsCompletedLymphoma | Multiple Myeloma | Acute Leukemia | Chronic Myeloproliferative Disease | Chronic Lymphoproliferative Disease | Poor-risk Myelodysplasia (MDS)United States
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Sheikh Shakhbout Medical CityRecruitingSpasticity, Muscle | Oxygen Consumption | Sclerosis, Multiple | Spastic | MS (Multiple Sclerosis)United Arab Emirates
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Brown, Theodore R., M.D., MPHEvergreen HealthcareCompletedErythema | MS (Multiple Sclerosis)United States
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IGC Pharma LLCRecruitingAggression | Depression | Anxiety | Alzheimer Disease | Memory Impairment | Agitated; State, Acute Reaction to Stress | Agitation,Psychomotor | Care Giving Burden | NPS | Aggressive OutburstUnited States, Canada, Puerto Rico
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Istituto Scientifico Romagnolo per lo Studio e...RecruitingProstate Cancer | Diagnosis | 68Ga-PSMA PET/CT Guided Prostate Biopsy | Mp-3TMRI Guided Prostate Biopsy | TNM StagingItaly
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University at BuffaloUniversity of PaviaCompletedMultiple Sclerosis (MS) | Clinically Isolated Syndrome (CIS) | Other Neurological Disorders (OND) | Healthy (HC)
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Benovus Bio, Inc.UnknownMyelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML) | Multiple Myeloma (MM) | Smoldering Multiple Myeloma (sMM)United States
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National Heart, Lung, and Blood Institute (NHLBI)TerminatedAcute Lymphoblastic Leukemia | Chronic Lymphocytic Leukemia | MDS (Myelodysplastic Syndrome) | CML (Chronic Myelogenous Leukemia) | AML (Acute Myelogenous Leukemia)United States
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Tel-Aviv Sourasky Medical CenterUnknownTo Evaluate the Effect of Therapy With IT MTX on the Disease Course of Patients With Progressive MS
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Center for International Blood and Marrow Transplant...National Marrow Donor ProgramCompletedChronic Lymphocytic Leukemia (CLL) | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML) | Chemotherapy-sensitive Lymphoma | Acute Lymphoblastic Leukemia (ALL)/T Lymphoblastic Lymphoma | Acute Biphenotypic Leukemia (ABL) | Acute Undifferentiated Leukemia (AUL)United States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAcute Lymphocytic Leukemia | MDS (Myelodysplastic Syndrome) | CLL (Chronic Lymphocytic Leukemia) | CML (Chronic Myelogenous Leukemia) | AML (Acute Myelogenous Leukemia)United States
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University of UtahNational Cancer Institute (NCI)TerminatedObstructive Sleep Apnea Syndrome | Polycythemia Vera | Essential Thrombocythemia | CALR Gene Mutation | JAK2 Gene Mutation | MPL Gene MutationUnited States
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Gamida Cell ltdActive, not recruitingLymphoma | Acute Leukemia | Hematological Malignancies | Acute Lymphoblastic Leukemia (ALL) | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML) | Chronic Myelogenous Leukemia (CML)Spain, United States, United Kingdom, Israel, Singapore, Brazil, Italy, France, Netherlands, Portugal
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Memorial Sloan Kettering Cancer CenterPediatric Brain Tumor ConsortiumTerminatedFanconi Anemia | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML)United States
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NovartisCompletedMyelodysplastic Syndromes | Hemoglobinopathies | Diamond-Blackfan Anemia | Transfusional Iron Overload | Other Inherited or Acquired Anaemia | MPD Syndrome | Other Rare AnaemiasAustralia
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Michael Morse, MDTerminatedAcute Lymphoblastic Leukemia (ALL) | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML) | B Cell Malignancies | Chronic Myelogenous Leukemia (CML)United States
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Ikena OncologyRecruitingSolid Tumor | Solid Tumors, Adult | Malignant Pleural Mesothelioma (MPM) | Epithelioid Hemangioendothelioma (EHE) | NF2 Deficient Mesothelioma | Other NF2 Deficient Solid Tumors and Solid Tumors With YAP1/TAZ Fusion Genes | NF2 Deficiency | YAP1 or TAZ Gene FusionsUnited States, United Kingdom
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National Human Genome Research Institute (NHGRI)RecruitingHermansky-Pudlak Syndrome (HPS)United States
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Masonic Cancer Center, University of MinnesotaTerminatedMultiple Myeloma | AML | MDS | Non-hodgkin's Lymphoma | Leukemia, Lymphocytic, Acute | Hodgkin's Disease | Leukemia, Myeloid, Chronic | Leukemia, Lymphocytic, Chronic | JMMLUnited States
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Columbia UniversityCompletedCOVID-19 | MS (Multiple Sclerosis) | Support GroupsUnited States
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Compugen LtdRecruitingMultiple Myeloma | Ovarian Cancer | Lung Cancer | Advanced Cancer | Colon Cancer | Plasma Cell Neoplasm | HNSCC | Microsatellite Stable Colorectal Carcinoma | MSS-CRCUnited States