- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Machado-Joseph Disease Type 3
Total 54014 results
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Astellas Pharma Global Development, Inc.Approved for marketingAcute Myeloid Leukemia (AML) | FMS-like Tyrosine Kinase-3 (FLT3) MutationsUnited States, Canada, Japan
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Northwestern UniversityNational Cancer Institute (NCI); BrainUp IncNot yet recruitingRecurrent WHO Grade 2 Glioma | Recurrent Glioblastoma, IDH-Wildtype | Recurrent WHO Grade 3 Glioma | Recurrent WHO Grade 4 GliomaUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingRecurrent Neuroblastoma | Stage 4S Neuroblastoma | Stage 2A Neuroblastoma | Stage 2B Neuroblastoma | Stage 3 Neuroblastoma | Stage 4 NeuroblastomaUnited States, Canada, Australia, New Zealand
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Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingStage 4S Neuroblastoma | Ganglioneuroblastoma | Stage 2A Neuroblastoma | Stage 2B Neuroblastoma | Stage 3 Neuroblastoma | Stage 4 Neuroblastoma | Stage 1 Neuroblastoma | Stage 2 NeuroblastomaUnited States, Canada, Australia, New Zealand
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Cooperative International Neuromuscular Research...Carolinas Medical Center lead study siteCompletedBecker Muscular Dystrophy | Limb-Girdle Muscular Dystrophy, Type 2A (Calpain-3 Deficiency) | Limb-Girdle Muscular Dystrophy, Type 2B (Miyoshi Myopathy, Dysferlin Deficiency) | Limb-Girdle Muscular Dystrophy, Type 2I (FKRP-deficiency)United States
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MeiraGTx, LLCRecruitingGrade 2 and 3 Late Xerostomia Caused by Radiotherapy for Cancers of the Upper Aerodigestive Tract, Excluding the Parotid GlandsUnited States, Canada
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Ruijin HospitalUnknownDiffuse Large B-cell Lymphoma | Follicular Lymphoma Grade 3BChina
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Stanford UniversityTerminatedBreast Cancer | Breast Cancer Early Stage Breast Cancer (Stage 1-3) | Breast Cancer Metastatic Breast CancerUnited States
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Merck Sharp & Dohme LLCCompletedPrevention of HPV Types 16- and 18-related Cervical Cancer, Cervical Intraepithelial Neoplasia (CIN) 1/2/3, and Cervical Adenocarcinoma in SituChina
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Medical College of WisconsinNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsTerminatedFollicular Lymphoma | Recurrent Grade 1 Follicular Lymphoma | Recurrent Grade 2 Follicular Lymphoma | Recurrent Grade 3 Follicular LymphomaUnited States
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Western University of Health SciencesGuardion Health Sciences, Inc.Active, not recruitingAge-Related Macular Degeneration | Dry Eye Syndromes | Omega 3 IndexUnited States
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Shanghai Jiao Tong University School of MedicineCompletedFebrile Neutropenia | Grade 3/4 NeutropeniaChina
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Fundación de Ayuda a la Investigación sobre la...UnknownChronic Kidney Disease Stage 3 | Chronic Kidney Disease Stage 4Spain
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Scholar Rock, Inc.Active, not recruitingNeuromuscular Diseases | Neuromuscular Manifestations | Atrophy | Muscular Atrophy | Spinal Muscular Atrophy | Muscular Atrophy, Spinal | Spinal Muscular Atrophy Type 3 | SMA | Anti-myostatin | Spinal Muscular Atrophy Type IIUnited States, Spain, Belgium, Germany, Netherlands, Poland, Italy, France, United Kingdom
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Liaocheng People's HospitalRecruitingPressure Injuries - Stage 3 | Pressure Injuries - Stage 4China
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Mayo ClinicNational Institutes of Health (NIH)CompletedOmega-3 Fatty Acids | Pediatric Bipolar Disorder | Adolescent Bipolar Disorder | Magnetic Resonance Spectroscopy ImagingUnited States
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Marco CapogrossoRoche-GenentechNot yet recruitingSpinal Muscular Atrophy | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy 4United States
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Scholar Rock, Inc.Active, not recruitingNeuromuscular Diseases | Neuromuscular Manifestations | Atrophy | Muscular Atrophy | Spinal Muscular Atrophy | Muscular Atrophy, Spinal | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type 2 | Anti-myostatinUnited States, Germany, Belgium, Spain, United Kingdom, Netherlands, France, Italy, Poland
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National Cancer Institute (NCI)Active, not recruitingRecurrent Grade 1 Follicular Lymphoma | Recurrent Grade 2 Follicular Lymphoma | Recurrent Grade 3 Follicular Lymphoma | Refractory Follicular Lymphoma | Grade 3a Follicular LymphomaUnited States, Canada, Singapore
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Enrollme.ru, LLCDanone NutriciaCompletedPressure Ulcer ( Stage 2-3)Russian Federation
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University Medical Center GroningenDutch Cancer Society; ViciniVax B.VCompleted
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Medical University of South CarolinaEntera Health, IncCompletedAdvanced COPD (GOLD Stage 3 or 4) With CachexiaUnited States
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Stanford UniversityNational Institutes of Health (NIH); University of California; Breast Cancer... and other collaboratorsActive, not recruitingBreast Cancer | Breast Cancer Non-invasive Breast Cancer | Breast Cancer Early Stage Breast Cancer (Stage 1-3)United States
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RinuaGene Biotechnology Co., Ltd.Not yet recruitingCervical Intraepithelial Neoplasia Grade 2/3 | Human Papillomavirus Associated Intraepithelial Neoplasia | Human Papillomavirus Type 16 Infection | Human Papillomavirus Type 18 Infection
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Gulhane School of MedicineCompletedWe Investigated the Relationship Between Plasma FGF23 Levels and Endothelial Dysfunction in a Sizable Series of Incident Stage 3-4 CKD Patients.Turkey
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Tianjin Medical University Cancer Institute and...RecruitingPancreatic Carcinoma | Neuroendocrine Carcinoma | Neuroendocrine Tumor Grade 3China
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National Cancer Institute (NCI)Active, not recruitingGlioblastoma | WHO Grade 3 Glioma | Advanced Malignant Solid Neoplasm | Recurrent Malignant Solid Neoplasm | Recurrent Glioma | Recurrent Cholangiocarcinoma | WHO Grade 2 GliomaUnited States
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Universidad de AntioquiaBarts and the London School of Medicine and Dentistry; Instituto Colombiano... and other collaboratorsCompletedCervical Cancer | Cervical Abnormalities | Cervical Intraepithelial Neoplasia Grade 2/3Colombia
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Shanghai Mental Health CenterHarbin Medical University; Qingdao Mental Health CenterRecruitingBipolar Disorder | Major Depressive Disorder | Omega-3 Fatty AcidsChina
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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National Cancer Institute (NCI)CompletedRecurrent Grade 1 Follicular Lymphoma | Recurrent Grade 2 Follicular Lymphoma | Recurrent Grade 3 Follicular Lymphoma | Recurrent Mantle Cell LymphomaUnited States
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Neurotech PharmaceuticalsUniversity of California, San FranciscoCompletedRetinitis Pigmentosa | Usher Syndrome Type 2 | Usher Syndrome Type 3United States
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Northern Care Alliance NHS Foundation TrustBrighter ABCompletedDiabetes type1 | Diabetes type2United Kingdom
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Ultragenyx Pharmaceutical IncCompletedLong-chain Fatty Acid Oxidation Disorders (LC-FAOD) | Very Long Chain Acyl-CoA Dehydrogenase (VLCAD) Deficiency | Trifunctional Protein (TFP) Deficiency | Carnitine Palmitoyltransferase (CPT II) Deficiency | Longchain 3-hydroxy-acyl-CoA Dehydrogenase (LCHAD) DeficiencyUnited States, United Kingdom
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Sanliurfa Mehmet Akif Inan Education and Research...CompletedPre-Eclampsia | Cathepsin B Level | Pentraxin 3 LevelTurkey
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MedImmune LLCCompletedRespiratory Syncytial Virus Infections | Respiratory Viral Infections | Parainfluenza Virus 3, HumanUnited States
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University Hospital, MontpellierUniversité MontpellierTerminatedDiabetic Patients Type 1 and 2 | Podologic Grade From 0 to 3France
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University of PennsylvaniaNational Institutes of Health (NIH)CompletedControl | 1 Night Recovery Sleep | 3 Nights Recovery Sleep | 5 Nights Recovery SleepUnited States
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George Washington UniversityNational Cancer Institute (NCI)RecruitingCervical Cancer | Human Papilloma Virus | CIN 2/3United States
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Cairo UniversityMohamed, Ahmed A., M.D.; Mohamed Yousry Mohamed; Tamer Fayez Safan; Tamer Mohamed... and other collaboratorsCompleted
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyActive, not recruitingPrimary Hyperoxaluria Type 3United States, Germany, United Kingdom, Canada, Poland
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University of California, San FranciscoDuke UniversityRecruitingWolman Disease | MPS IVA | Pompe Disease Infantile-Onset | Gaucher Disease, Type 2 | MPS VI | MPS I | Gaucher Disease, Type 3 | MPS II | Mps VIIUnited States
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Mayo ClinicNational Cancer Institute (NCI)TerminatedMalignant Glioma | WHO Grade 3 Glioma | Intractable Epilepsy | Seizure Disorder | WHO Grade 2 GliomaUnited States
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Centre Hospitalier Régional de la CitadelleCompletedSafety and Efficacy Study of Pyridostigmine on Patients With Spinal Muscular Atrophy Type 3 (EMOTAS)Spinal Muscular Atrophy Type 3Belgium
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Shanghai Eye Disease Prevention and Treatment CenterXinhua Hospital, Shanghai Jiao Tong University School of Medicine; Shanghai... and other collaboratorsCompletedAge 3 to 16 Years (Inclusive), Male or Female | Clinical Diagnosis Confirming That Myopia Has Occurred in at Least One Eye | The Guardian Voluntarily Signed the Subject's Informed Consent FormChina
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Chulalongkorn UniversityRecruitingEmpagliflozin in Post AKI Stage 2-3Thailand
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Charles University, Czech RepublicNot yet recruitingRecurrence | Cervical Intraepithelial Neoplasia Grade 2/3Czechia
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DiaMedica Therapeutics IncCompletedDiabetes | Chronic Kidney Disease | Chronic Kidney Disease, Stage 4 (Severe) | Chronic Kidney Disease, Stage 3 (Moderate)United States
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OHSU Knight Cancer InstituteWithdrawnPrimary Peritoneal Carcinoma | Epithelial Ovarian Carcinoma | Ovarian Carcinoma, Stage 3 or 4United States
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Celularity IncorporatedTerminatedStage 2 Pulmonary Sarcoidosis | Stage 3 Pulmonary SarcoidosisUnited States