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Clinical Trials on Medication Errors and Other Product Use Errors and Issues in New Zealand
Total 569 results
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AlexionTerminatedWilson DiseaseUnited States, France, Germany, Spain, Canada, Singapore, Poland, Denmark, Hungary, Australia, Austria, Czechia, Hong Kong, Israel, Japan, Korea, Republic of, New Zealand, Russian Federation, Serbia, Taiwan, Turkey, United Kingdom
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AmgenCompletedFamilial HypercholesterolemiaCanada, Italy, Norway, Belgium, United States, Turkey, Australia, Austria, South Africa, Poland, Switzerland, Spain, Portugal, Slovenia, Brazil, Russian Federation, Hungary, United Kingdom, Colombia, Czechia, Netherlands, Greece, Ma...
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BioMarin PharmaceuticalCompleted
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Weill Medical College of Cornell UniversityNathan's Battle FoundationCompletedBatten Disease | Late Infantile Neuronal Ceroid LipofuscinosisUnited States
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Kyowa Hakko Kirin Pharma, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Canada
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BioMarin PharmaceuticalApproved for marketing
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Horizon Pharma Rheumatology LLCCompletedRefractory Chronic GoutUnited States
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Novo Nordisk A/SCompletedKidney Diseases | Urologic Diseases | Genetic Disease | Primary Hyperoxaluria Type 1 (PH1) | Primary Hyperoxaluria Type 2 (PH2)Poland, United States, United Kingdom, New Zealand, Australia, Canada, France, Germany, Israel, Italy, Japan, Lebanon, Netherlands, Romania, Spain
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PfizerCompletedHypertriglyceridemia | Hyperlipoproteinemia Type IVUnited States, Canada
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Macfarlane Burnet Institute for Medical Research...PATH; UNITAID; University of Melbourne; Menzies School of Health Research; Medicines... and other collaboratorsRecruitingVivax Malaria | G6PD DeficiencyPapua New Guinea
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Amryt PharmaRecruitingHomozygous Familial HypercholesterolemiaItaly, United States, Argentina, Canada, France, Greece, Netherlands, United Kingdom
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Swedish Orphan BiovitrumCompletedAcute Gouty ArthritisUnited States
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Weill Medical College of Cornell UniversityNational Institutes of Health (NIH)CompletedBatten Disease | Late-Infantile Neuronal Ceroid LipofuscinosisUnited States
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Weill Medical College of Cornell UniversityCompletedBatten Disease | Late Infantile Neuronal Ceroid LipofuscinosisUnited States
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LG ChemRecruitingHyperuricemia | Gout | Gout Flare | TophiUnited States
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University of New MexicoCompletedPain, Postoperative | Physical Activity | Opioid Use | Abuses Over-The-Counter/Prescription Medications | Patient Dependence onUnited States
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OrphalanActive, not recruiting
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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Kyowa Hakko Kirin Pharma, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Canada
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PfizerCompletedHyperlipidemia | Hypercholesterolemia, FamilialUnited States, Canada, South Africa, Czech Republic, Italy, Finland, Netherlands, France
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Sangamo TherapeuticsTerminatedMucopolysaccharidosis II | MPS IIUnited States
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Arthrosi TherapeuticsCompletedHyperuricemia | Gout | Arthritis, Gouty | Gout ChronicUnited States, Australia, Taiwan
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Exsar CorporationSuspendedType I Gaucher DiseaseUnited States
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Regeneron PharmaceuticalsSanofiCompletedHomozygous Familial HypercholesterolemiaUnited States, South Africa, Canada, Greece, Japan, Ukraine, Austria, Czechia, France, Germany, Italy, Taiwan, Turkey
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Nacuity Pharmaceuticals, Inc.Recruiting
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LG ChemRecruitingHyperuricemia | Gout | Gout Flare | TophiUnited States
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Glycogenosis 2United States
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Novartis PharmaceuticalsActive, not recruitingFamilial Hypercholesterolemia - HeterozygousUnited States, Germany, South Africa, Greece, Italy, Czechia, Taiwan, Slovakia, Turkey, France, Russian Federation, Canada, Spain, Jordan, Switzerland, Hungary, Poland, Netherlands, Norway, United Kingdom, Lebanon, Argentina, Brazil, ... and more
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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Merck Sharp & Dohme LLCActive, not recruitingHypercholesterolemia | Familial HypercholesterolemiaColombia, Israel, Taiwan, United States, Argentina, China, Germany, Italy, Japan, Korea, Republic of, Mexico, South Africa, Spain, Turkey
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SynlogicCompletedPhenylketonuriaUnited States
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Kyowa Kirin, Inc.CompletedX-Linked HypophosphatemiaUnited States
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Scheie Syndrome | Hurler's Syndrome | Hurler-Scheie SyndromeUnited States, Canada, United Kingdom, Brazil, Germany, Italy, Netherlands
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NYU Langone HealthGenzyme, a Sanofi CompanyCompleted
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Pompe Disease Infantile-OnsetUnited States, France, South Africa
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BioMarin PharmaceuticalCompletedPhenylketonuria | HyperphenylalaninaemiaUnited States
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeUnited States, Canada, Sweden
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Genzyme, a Sanofi CompanyWithdrawnGaucher Disease, Type 1United States, India
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PfizerCompletedHeterozygous Familial HypercholesterolemiaCanada, Netherlands, United Kingdom, United States, Spain, Poland, Finland, Norway, South Africa, Italy, Bulgaria
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PfizerCompletedHyperlipidemia | Hypercholesterolemia, FamilialAustralia, Canada, United States, France, South Africa, Sweden, Norway, Denmark, Iceland
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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Boston Children's HospitalAgios Pharmaceuticals, Inc.CompletedPyruvate Kinase Deficiency | Congenital Non-Spherocytic Hemolytic AnemiaUnited States, Germany, Canada, Czechia, Italy, Netherlands
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BioMarin PharmaceuticalCompleted
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Allena PharmaceuticalsCompletedEnteric Hyperoxaluria | Primary Hyperoxaluria | HyperoxalemiaUnited States, United Kingdom, Germany
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Ari ZimranPfizerActive, not recruitingGaucher Disease, Type 3Israel, Turkey, India
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase DeficiencyFrance, Poland, United Kingdom, Spain, Mexico, Turkey, Japan, Australia, Russian Federation, United States, Germany, Italy, Czechia, Argentina, Croatia
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Cytonet GmbH & Co. KGTerminatedUrea Cycle DisordersUnited States, Canada
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | Cholesterol Ester Storage Disease(CESD) | LAL-DeficiencyFrance, United States, United Kingdom, Czechia