Clinical Trials on Methylmalonic Acidemia in Germany

Total 3 results

Recordati Rare Diseases

Recruiting

Understanding the Long-Term Management of Organic Acidemia Patients With CARBAGLU®: A Mixed Methods Approach (PROTECT)

Propionic Acidemia | Methylmalonic Acidemia

France, Spain, Italy, United Kingdom, Norway, Germany, Sweden
PTC Therapeutics
Genzyme, a Sanofi Company

Terminated

Ataluren for Nonsense Mutation Methylmalonic Acidemia

Amino Acid Metabolism, Inborn Errors

France, United Kingdom, Italy, Belgium, Germany, Switzerland
German Diabetes Center
University Children's Hospital, Düsseldorf

Completed

Energy Metabolism in Branched-chain Organic Acidemias

Metabolic Syndrome | Insulin Resistance | Energy Metabolism

Germany

3

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