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Clinical Trials on Mevalonate Kinase Deficiency in Australia
Total 305 results
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American Regent, Inc.Duke Clinical Research InstituteCompletedHeart Failure | Iron-deficiencyUnited States, Canada, Australia, Bulgaria, Georgia, New Zealand, Latvia, Hungary, Poland, Czechia, Lithuania, Russian Federation, Ukraine
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Ascendis Pharma A/SCompletedEndocrine System Diseases | Pituitary Diseases | Hormone Deficiency | Growth Hormone Deficiency, PediatricUnited States, Armenia, Belarus, Bulgaria, Georgia, Greece, Russian Federation, Ukraine, Australia, New Zealand, Poland
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Moritz OberndorferMerck Gesellschaft mbH, AustriaCompletedHIV Infections | Diabetes Mellitus | Dyslipidemias | Cardiovascular Risk FactorAustria
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Novo Nordisk A/SRecruitingGrowth Hormone Disorder | Growth Hormone Deficiency in ChildrenUnited States, Japan, Israel, India, Austria, Slovenia, Belgium, Brazil, France, Germany, Sweden, Turkey, Ukraine
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Genzyme, a Sanofi CompanyRecruitingGaucher Disease | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency DiseaseHungary, Croatia, United States, Australia, Belgium, Brazil, Bulgaria, Canada, Denmark, Germany, Greece, Hong Kong, India, Indonesia, Italy, Jordan, Korea, Republic of, Kuwait, Lebanon, Malaysia, Pakistan, Philippines, Poland, Saudi Arabia and more
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AstraZenecaRecruitingAdvanced Solid Tumours That Are MTAP DeficientUnited States, Spain, Korea, Republic of, Australia, Japan, China, Netherlands, France
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BeiGeneTerminatedMetastatic Castration-Resistant Prostate Cancer (mCRPC) | Homologous Recombination Deficiency (HRD)United States, Australia, Puerto Rico, Spain
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CSL BehringCompletedHereditary AngioedemaCanada, Australia, Germany, United States, Israel
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Grifols Therapeutics LLCCompletedPrimary ImmunodeficiencySpain, France, Germany, United Kingdom, Australia, Czechia, Hungary, Poland, Sweden
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Chiesi Farmaceutici S.p.A.CromsourceCompletedAlpha-MannosidosisFrance, Denmark, Austria, Germany, Italy
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Medical University of ViennaRecruitingHIV Infections | Sexually Transmitted Diseases | Chlamydia | Gonorrhea | Syphilis | HIV Pre-Exposure ProphylaxisAustria
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BioMarin PharmaceuticalActive, not recruitingHereditary Angioedema | HAESpain, United States, Australia
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Merck KGaA, Darmstadt, GermanyCompletedGrowth Hormone Deficiency | Turner SyndromeArgentina, Australia, Austria, Canada, France, Germany, Italy, Norway, Russian Federation, Singapore, Spain, Sweden, United Kingdom
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Glaxo WellcomeCompletedHIV InfectionsUnited States, Puerto Rico, Australia
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Novo Nordisk A/SCompletedGrowth Hormone Disorder | Adult Growth Hormone DeficiencyUnited States, Poland, India, Japan, Russian Federation, United Kingdom, Germany, Sweden, Israel, Malaysia, Turkey, South Africa, Australia, Latvia, Lithuania, Romania, Brazil, Norway, Ukraine
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Baxalta now part of ShireCompletedPrimary Immunodeficiency Diseases (PID)Germany, Austria, Hungary, Sweden, United Kingdom
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Marinus PharmaceuticalsCompletedCDKL5 Deficiency DisorderUnited States, Australia, France, Israel, Italy, Poland, Russian Federation, United Kingdom
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Ultragenyx Pharmaceutical IncTerminatedGlucose Transporter Type 1 Deficiency SyndromeUnited States, Spain, Denmark, United Kingdom, Australia
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Aeglea BiotherapeuticsTerminatedHomocystinuria Due to Cystathionine Beta-Synthase DeficiencyUnited States, United Kingdom, Australia
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ErydelRecruitingAtaxia TelangiectasiaUnited States, Australia, Belgium, Germany, India, Italy, Poland, Spain, Tunisia
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ShireTakeda Development Center Americas, Inc.RecruitingHereditary Angioedema (HAE)France, Austria, Australia, Spain, Czechia, Italy, United Kingdom, Germany, Israel, Ireland, Brazil, Denmark, Greece, Sweden
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Kirby InstituteThe University of New South WalesTerminatedHIV InfectionsArgentina, Israel, Australia
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Medical University of GrazActive, not recruitingPrimary Immunodeficiency | Immune Thrombocytopenia | Autoimmune Hemolytic Anemia | Evans SyndromeAustria
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Bristol-Myers SquibbCompletedHIV Infections | AIDS Dementia ComplexUnited States, Australia, United Kingdom
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TakedaCompletedHereditary Angioedema (HAE)France, Germany, Austria, Greece
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Kyowa Kirin Pharmaceutical Development LtdCompletedX-linked Hypophosphatemia (XLH)Sweden, Spain, United Kingdom, Italy, Austria, France
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BioCryst PharmaceuticalsActive, not recruitingHereditary Angioedema | PediatricSpain, Austria, Canada, France, Germany, Israel, Italy, Poland, Romania, United Kingdom
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CSL BehringActive, not recruitingHereditary AngioedemaAustralia, Canada, United States, New Zealand, Germany, Hong Kong, Netherlands, Taiwan, Czechia, Israel, Hungary, Japan, Russian Federation, Spain
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Medical University of GrazCompletedSkin Cancer | Basal Cell Nevus Syndrome | Xeroderma PigmentosumAustria
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ShireCompletedHereditary AngioedemaUnited States, Australia, Israel, Canada, Hungary, Romania, Russian Federation, South Africa, Ukraine
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OPKO Health, Inc.Active, not recruitingSafety and Efficacy Phase 3 Study of Long-acting hGH (MOD-4023) in Growth Hormone Deficient ChildrenPediatric Growth Hormone DeficiencyIsrael, United States, India, Korea, Republic of, Australia, Taiwan, Spain, Argentina, Belarus, Bulgaria, Canada, Colombia, Georgia, Greece, Mexico, New Zealand, Poland, Russian Federation, Ukraine, United Kingdom
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Boehringer IngelheimCompleted
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-Linked HypophosphatemiaKorea, Republic of, Canada, United States, Australia, Japan, United Kingdom, Sweden
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KalVista Pharmaceuticals, Ltd.RecruitingHereditary AngioedemaUnited States, Bulgaria, France, Greece, Israel, Netherlands, Spain, United Kingdom, Australia, Germany, South Africa, Slovakia, Austria, New Zealand, Romania, Canada, Japan
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Kirby InstituteCompletedHepatitis CAustralia, United States, United Kingdom, New Zealand, Switzerland, Canada, Germany, Netherlands
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ShireTakeda Development Center Americas, Inc.Active, not recruitingHereditary Angioedema (HAE)Germany, Switzerland, Spain, Israel, Italy, Austria, Portugal, Kuwait
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PedNet Haemophilia Research FoundationLund University HospitalRecruitingFactor IX Deficiency | Factor VIII DeficiencyNorway, Austria, Belgium, Canada, Czechia, Denmark, Finland, France, Germany, Greece, Ireland, Israel, Italy, Netherlands, Portugal, Spain, Sweden, Switzerland, United Kingdom
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Ascendis Pharma Endocrinology Division A/SCompletedEndocrine System Diseases | Growth Hormone Deficiency | Hormone DeficiencyUnited States, Armenia, Georgia, Turkey, Ukraine, Australia, Canada, Denmark, France, Germany, Greece, Israel, Italy, Japan, Korea, Republic of, Malaysia, Netherlands, New Zealand, Poland, Romania, Serbia, Slovakia, Spain, United Kingdom
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BioCryst PharmaceuticalsCompletedHereditary Angioedema (HAE)Austria, Denmark, France, Germany, Hungary, Israel, Italy, North Macedonia, Poland, Romania, Switzerland, United Kingdom
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KalVista Pharmaceuticals, Ltd.RecruitingHereditary AngioedemaUnited States, Bulgaria, France, Greece, Hungary, Israel, Italy, Netherlands, New Zealand, North Macedonia, Poland, Spain, United Kingdom, Australia, Germany, South Africa, Austria, Portugal, Slovakia, Romania, Canada, Saudi Arabia, Japa...
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Italy, Canada, France, United Kingdom, Austria, Germany
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Boehringer IngelheimCompletedHIV InfectionsRomania, Poland, Austria
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Teva Branded Pharmaceutical Products R&D, Inc.TerminatedGrowth Hormone DeficiencyUnited States, Austria, Czechia, Greece, Hungary, Italy, Slovakia, Spain
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CSL BehringCompletedHereditary Angioedema Types I and IIUnited States, Spain, Germany, Australia, Canada, Czechia, Hungary, Israel, Italy, Romania, United Kingdom
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Ascendis Pharma Endocrinology Division A/SCompletedEndocrine System Diseases | Pituitary Diseases | Hormones | Growth Hormone Deficiency, Pediatric | hGH (Human Growth Hormone)United States, Armenia, Australia, Belarus, Bulgaria, Georgia, Greece, Italy, New Zealand, Poland, Romania, Russian Federation, Turkey, Ukraine
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CSL BehringCompletedHereditary AngioedemaBulgaria, United States, Poland, Spain, Hungary, United Kingdom, Russian Federation, Macedonia, The Former Yugoslav Republic of, Argentina, Australia, Canada, Czech Republic, Israel, Romania, Sweden
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Quince Therapeutics S.p.A.CompletedGenetic Syndrome | Nervous System DiseaseIndia, United States, Australia, Germany, Italy, Norway, Poland, Spain, Tunisia, United Kingdom, Israel, Belgium
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OctapharmaCompletedPrimary and Secondary Immunodeficiency and Other Conditions Requiring Regular Administration of Octagam 5% or 10% IVIGCanada, Austria, France, Spain, United Kingdom
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Hoffmann-La RocheTrimerisCompletedHIV InfectionsSwitzerland, Spain, United Kingdom, Germany, Belgium, Australia, Sweden, Italy, Netherlands
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ShireJerini AGCompletedHereditary AngioedemaSpain, Argentina, Austria, Denmark, France, Germany, Israel, Italy, Switzerland, United Kingdom