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- US Clinical Trials Registry
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Clinical Trials on Microcephalic Primordial Dwarfism
Total 337 results
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University of California, Los AngelesTerminatedGrowth Hormone Deficiency | Small for Gestational Age | Idiopathic Short StatureUnited States
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PfizerCompletedGrowth Hormone Deficiency | Growth RetardationFrance
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Zhejiang UniversityCompletedCongenital Hypothyroidism | L-Thyroxine | Follow-Up
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QED Therapeutics, Inc.RecruitingAchondroplasiaUnited States, Spain, Singapore, Canada, United Kingdom, France, Australia, Norway, Argentina, Germany, Italy
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BioMarin PharmaceuticalCompletedAchondroplasiaSpain, Denmark, Italy, Austria, Germany, Sweden
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McGill UniversityEthiopian Health and Nutrition Research Institute; Micronutrient InitiativeCompletedGoiter | Iodine Deficiency | CretinismCanada
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The University of Texas Health Science Center,...Terminated
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Novo Nordisk A/SCompleted
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Virginia Polytechnic Institute and State UniversityAmerican Academy for Cerebral Palsy and Developmental MedicineCompletedMicrocephaly | Global Developmental Delay | Hyperkinesis With Developmental DelayUnited States
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InnoskelRecruitingSEDC | Hypochondrogenesis | Semd, Strudwick Type | Kniest DysplasiaFrance, Spain
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Andrew DauberActive, not recruiting
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Insmed IncorporatedCompletedLaron Syndrome | Growth Hormone Insensitivity Syndrome (GHIS)United States, Argentina, Australia, Brazil, China, Egypt, Germany, Israel, Italy, Norway, Peru, Slovakia, Turkey, United Kingdom
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Genentech, Inc.CompletedDwarfism, Pituitary | Turner Syndrome
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IpsenUniversity of OklahomaCompleted
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National Human Genome Research Institute (NHGRI)CompletedDwarfism | AchondroplasiaUnited States
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Merck KGaA, Darmstadt, GermanyMerck Serono S.A.S, FranceCompleted
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BioMarin PharmaceuticalRecruitingHypochondroplasiaUnited States, Spain, Canada, France, Japan, Australia, Italy, Argentina, Brazil, Germany, United Kingdom
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Eunice Kennedy Shriver National Institute of Child...TerminatedObesity | Growth Hormone Deficiency | Short StatureUnited States
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Merck KGaA, Darmstadt, GermanyCompletedGrowth Hormone Deficiency | Turner SyndromeArgentina, Australia, Austria, Canada, France, Germany, Italy, Norway, Russian Federation, Singapore, Spain, Sweden, United Kingdom
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Oswaldo Cruz FoundationConselho Nacional de Desenvolvimento Científico e Tecnológico; Rio de Janeiro...UnknownMicrocephaly | Child Development | ZIKA VIRUS INFECTIONBrazil
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B.P. Koirala Institute of Health SciencesCompletedMaternal Hypotension After Spinal AnesthesiaNepal
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Cairo UniversityUnknownHypomineralization of Enamel | Hypomineralization Molar Incisor | Short StatureEgypt
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Eunice Kennedy Shriver National Institute of Child...CompletedOsteogenesis Imperfecta | Short StatureUnited States
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IpsenCompletedGrowth Disorders | Insulin-Like Growth Factor-1 DeficiencyUnited States
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National Human Genome Research Institute (NHGRI)CompletedDwarfism | Developmental Bone Disease | Skeletal DysplasiasUnited States
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Meir Medical CenterUnknown
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University of Texas Southwestern Medical CenterCure SPG50RecruitingMicrocephaly | Spasticity, Muscle | Growth Retardation | Intellectual Deficiency | SPG50 | Spastic ParaplegiaUnited States
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National Human Genome Research Institute (NHGRI)CompletedMicrocephaly | Failure to Thrive | Abnormalities | Mental RetardationUnited States
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University of California, Los AngelesWithdrawnGrowth Failure | Chronic Liver Disease
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Assiut UniversityNot yet recruiting
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GeneScience Pharmaceuticals Co., Ltd.Peking University First Hospital; Shengjing Hospital; The First Affiliated Hospital... and other collaboratorsUnknown
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Novo Nordisk A/SCompletedTurner Syndrome | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Genetic DisorderJapan
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University Hospital, AngersUniversity of Angers, AngersUnknownIsolated Growth Hormone Deficiency | Turner Syndrome | Pediatrics | Social Cognition | Cognitive Functions
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Novo Nordisk A/SCompletedTurner Syndrome | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Genetic DisorderIsrael
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Universidade Federal de PernambucoCompletedMicrocephaly | Zika Virus InfectionBrazil
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Rambam Health Care CampusCompleted
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Fondazione IRCCS Ca' Granda, Ospedale Maggiore...RecruitingAchondroplasia | HypochondroplasiaItaly
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Assistance Publique - Hôpitaux de ParisUnknownPregnant Women Requiring AmniocentesisFrance
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Assistance Publique - Hôpitaux de ParisCompletedCongenital HypothyroidismFrance
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Universitätsklinikum Hamburg-EppendorfPfizer; Bundesverband Kleinwüchsige Menschen und ihre Familien e.V.RecruitingGrowth Hormone Deficiency | Achondroplasia | Small for Gestational AgeGermany
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Chunxiu GongThe First Affiliated Hospital with Nanjing Medical University; Tongji Hospital and other collaboratorsNot yet recruitingGenetic Diseases, Inborn | Small for Gestational Age Infant | Silver-Russell Syndrome
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Eunice Kennedy Shriver National Institute of Child...National Institutes of Health (NIH)TerminatedShort Stature | Growth Disorder | Syndromic Growth Disorder | Tall StatureUnited States
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SanofiRecruitingOsteochondrodysplasiaAustralia, Spain, Korea, Republic of, China, Italy
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QED Therapeutics, Inc.RecruitingHypochondroplasiaUnited States, Australia, Norway, Portugal, Singapore, Spain, Canada, France, Germany, Sweden, United Kingdom
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Eli Lilly and CompanyCompletedGrowth Hormone (GH) Deficiency | Short Stature Homeobox Containing Gene (SHOX) Deficiency | SHOX Deficiency-related Disorder | Non-GH-deficient Growth Disorders
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University Hospital, Strasbourg, FranceRecruiting
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HaEmek Medical Center, IsraelWithdrawnHearing Loss | Congenital HypothyroidismIsrael
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Virginia Polytechnic Institute and State UniversityRecruitingCerebral Palsy | Microcephaly | Acquired Brain Injury | Autism | Trauma, Brain | Neuromotor Impairments | Pediatric StrokeUnited States
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DNage B.V.CompletedCockayne SyndromeUnited States
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DNage B.V.TerminatedCockayne SyndromeUnited States, France, United Kingdom