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Clinical Trials on Mitochondrial Respiratory Chain Deficiencies in United States
Total 141 results
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University...RecruitingEnd Stage Liver Disease | Mitochondrial Diseases | Acute Liver Failure | Respiratory Chain Deficiencies, Mitochondrial | Disorder of Fatty Acid OxidationUnited States, Canada
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Abliva ABCompletedMitochondrial Diseases | Mitochondrial Myopathies | MELAS Syndrome | Mitochondrial Respiratory Chain DeficienciesUnited Kingdom
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National Human Genome Research Institute (NHGRI)RecruitingMitochondrial Disorders | Leigh Disease | Oxidative Phosphorylation Deficiencies | Electron Transport Chain Disorders, MitochondrialUnited States
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Millennium Pharmaceuticals, Inc.CompletedLight-Chain AmyloidosisUnited States, Canada, France, Germany, Italy
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Oregon Health and Science UniversityUniversity of PittsburghCompletedVery Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency | Carnitine Palmitoyltransferase 2 (CPT2) Deficiency | Mitochondrial Trifunctional Protein (TFP) Deficiency | Long-chain 3 hydroxyacylCoA Dehydrogenase (LCHAD) DeficiencyUnited States
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Criterium, Inc.AmgenCompletedAmyloidosis | Systemic Light Chain AmyloidosisUnited States
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Columbia UniversityNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMitochondrial Diseases | Mitochondrial Disorders | Mitochondrial Genetic Disorders | Disorder of Mitochondrial Respiratory Chain Complexes | Deletion and Duplication of Mitochondrial DNAUnited States, Canada
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Alfred Chung, MDAbbVie; Janssen PharmaceuticalsRecruitingAL Amyloidosis | Light Chain (AL) Amyloidosis | Systemic Light Chain DiseaseUnited States
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Millennium Pharmaceuticals, Inc.TerminatedRelapsed or Refractory Systemic Light Chain AmyloidosisUnited States, Canada, Spain, Israel, France, Australia, Denmark, Germany, Korea, Republic of, Greece, Netherlands, Brazil, Czechia, Italy, United Kingdom
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University of FloridaNo longer availableMitochondrial Enzyme DeficienciesUnited States
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Nexcella Inc.Not yet recruitingLight Chain (AL) AmyloidosisUnited States
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Memorial Sloan Kettering Cancer CenterMillennium Pharmaceuticals, Inc.CompletedAmyloidosis | Light Chain Deposition Disease (LCDD or MIDD) | Light Chain and Heavy Chain Deposition Disease (LHCDD or MIDD) | Monoclonal Immunoglobulin Deposition Disease (MIDD)United States
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Sorrento Therapeutics, Inc.RecruitingLight Chain (AL) AmyloidosisUnited States
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Cedars-Sinai Medical CenterEnrolling by invitationAmyloidosis, Immunoglobulin Light-chainUnited States, Canada
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Prothena Biosciences Ltd.RecruitingLight Chain (AL) AmyloidosisUnited States, Korea, Republic of, Australia, Denmark, France, Italy, Spain, Israel, Taiwan, Austria, Canada, Czechia, Germany, Greece, Hungary, Japan, Netherlands, Poland, Portugal, Turkey, United Kingdom, Belgium, Ireland
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Jerry Vockley, MD, PhDUltragenyx Pharmaceutical IncNo longer availableBarth Syndrome | Mitochondrial Trifunctional Protein Deficiency | Very Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency | Carnitine Palmitoyltransferase Deficiencies (CPT1, CPT2) | Long-chain Hydroxyacyl-CoA Dehydrogenase Deficiency | Glycogen Storage Disorders | Pyruvate Carboxylase Deficiency... and other conditionsUnited States
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The Cleveland ClinicCompletedAmyloidosis | Spinal Stenosis | Amyloid | Transthyretin Amyloidosis | Primary Amyloidosis of Light Chain TypeUnited States
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National Human Genome Research Institute (NHGRI)RecruitingMitochondrial DiseaseUnited States
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The Cleveland ClinicCompletedAmyloidosis | Transthyretin Amyloidosis | Trigger Finger | Primary Amyloidosis of Light Chain TypeUnited States
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National Cancer Institute (NCI)CompletedPrimary Systemic Amyloidosis | Light Chain Deposition DiseaseUnited States
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Tufts Medical CenterTerminatedAL AmyloidosisUnited States
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University of TennesseeFDA Office of Orphan Products DevelopmentCompleted
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Icahn School of Medicine at Mount SinaiMillennium Pharmaceuticals, Inc.CompletedAL AmyloidosisUnited States
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Boston Medical CenterJanssen PharmaceuticalsCompleted
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Andrew EisenbergerCompletedAmyloidosisUnited States
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University of TennesseeFood and Drug Administration (FDA)Completed
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Mayo ClinicRecruitingAL AmyloidosisUnited States
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Columbia UniversityCephalonCompletedAL AmyloidosisUnited States
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National Cancer Institute (NCI)TerminatedPrimary Systemic AmyloidosisUnited States
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Rajshekhar Chakraborty, MDGenentech, Inc.RecruitingAL AmyloidosisUnited States
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Boston Medical CenterCelgene CorporationCompletedAL AmyloidosisUnited States
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Boston Medical CenterTerminatedAL AmyloidosisUnited States
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University of TennesseeCompleted
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Boston Medical CenterSpectrum Pharmaceuticals, IncTerminatedAmyloidosis; SystemicUnited States
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Mayo ClinicCompletedAmyloidosisUnited States
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Weill Medical College of Cornell UniversityKaryopharm Therapeutics IncWithdrawnAL Amyloidosis | Amyloidosis | AmyloidUnited States
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Stanford UniversityCelgene CorporationCompletedLeukemia | AmyloidosisUnited States
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Stanford UniversityCompletedAmyloidosis | Blood and Marrow Transplant (BMT)United States
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SanofiRecruitingRelapsed/Refractory Multiple Myeloma | Amyloid Light-chain AmyloidosisItaly, Australia, Belgium, Hungary, Spain, United Kingdom, Czechia
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Medical College of WisconsinNational Heart, Lung, and Blood Institute (NHLBI)CompletedPrimary Systemic AmyloidosisUnited States
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Mayo ClinicCompletedPrimary Systemic AmyloidosisUnited States
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Alexion Pharmaceuticals, Inc.CompletedAL AmyloidosisUnited States
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University of Texas Southwestern Medical CenterGlaxoSmithKlineRecruitingAL Amyloidosis | AmyloidosisUnited States
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Prothena Biosciences Ltd.TerminatedAL AmyloidosisUnited States
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M.D. Anderson Cancer CenterCelgeneTerminatedMyelomaUnited States
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Prothena Biosciences Ltd.Amyloidosis Research Consortium; Amyloidosis Support Groups; Amyloidosis Foundation and other collaboratorsCompletedAL Amyloidosis | AmyloidosisUnited States
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Emory UniversityNational Cancer Institute (NCI); SanofiRecruitingAL AmyloidosisUnited States
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Oncopeptides ABPRA Health SciencesTerminatedAL AmyloidosisSpain, United Kingdom, Germany, Norway, Israel, France, United States, Czechia, Greece
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Barbara Ann Karmanos Cancer InstituteNational Cancer Institute (NCI)CompletedPrimary Systemic Amyloidosis | Light Chain Deposition DiseaseUnited States
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Memorial Sloan Kettering Cancer CenterVanderbilt University Medical Center; Tufts Medical CenterActive, not recruiting