- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Mucopolysaccharidosis Type II
Total 56779 results
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Tehran University of Medical SciencesUnknownMucopolysaccharidosisIran, Islamic Republic of
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Shrouk Shaban BakrRecruiting
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ShireTerminatedMucopolysaccharidosis (MPS)United States, Canada, United Kingdom, Turkey, Italy, Mexico, Spain
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ShireCompleted
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TakedaTakeda Development Center Americas, Inc.Active, not recruitingHunter SyndromeUnited States, Germany, Malaysia, Philippines, Thailand, Dominican Republic, Serbia, Vietnam
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Phoenix NestNational Institute of Neurological Disorders and Stroke (NINDS)Enrolling by invitationSanfilippo Syndrome Type DUnited States
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Swedish Orphan BiovitrumCompletedSanfilippo Syndrome Type A (MPS IIIA)United States, Turkey
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Swedish Orphan BiovitrumCompletedSanfilippo Syndrome Type A (MPS IIIA)United States, Germany, Turkey
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ShireTerminatedSanfilippo SyndromeNetherlands, United Kingdom
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Manchester Royal Eye HospitalBioMarin PharmaceuticalUnknownMucopolysaccharidosesUnited Kingdom
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ShireCompletedSanfilippo Syndrome Type AUnited States
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Mackay Memorial HospitalSanofi Taiwan Co. LtdRecruiting
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Hasan Kalyoncu UniversityCompleted
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Children's Hospital of Eastern OntarioCompleted
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TakedaAvailableHunter SyndromeUnited States, Australia, Mexico, Spain, United Kingdom
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Green Cross CorporationCompleted
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Masonic Cancer Center, University of MinnesotaCompletedMucopolysaccharidosis | Hurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Krabbe Disease | Adrenoleukodystrophy (ALD) | Hunter Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Metachromatic Leukodystrophy (MLD) | Maroteaux-Lamy SyndromeUnited States
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ShireActive, not recruitingHunter SyndromeUnited States, Spain, Canada, United Kingdom, Mexico, Australia, France
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ShireCompleted
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ShireCompletedHunter SyndromeUnited States, United Kingdom
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University Hospital, ToursCompletedMucopolysaccharidosesFrance
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Patricia I. Dickson, M.D.National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University... and other collaboratorsCompletedMucopolysaccharidosis I | Scheie Syndrome | Lysosomal Storage Disease | Cognitive Decline | Hurler-Scheie SyndromeUnited States
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Greenwood Genetic CenterShriners Hospitals for Children; BioMarin PharmaceuticalCompletedMPS IVA | Maroteaux Lamy Syndrome | MPS VI | Morquio Syndrome AUnited States
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University of California, San FranciscoRecruiting
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BioMarin PharmaceuticalCompletedMPS VIUnited States, Australia, France, Brazil, Germany, Portugal, United Kingdom
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ShireCompleted
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedMucopolysaccharidosesUnited States
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Lundquist Institute for Biomedical Innovation at...National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedMucopolysaccharidosesUnited States
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Lysosomal and Rare Disorders Research and Treatment...Team SanfilippoRecruitingSanfilippo Syndrome | MPS3United States
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Allievex CorporationEnrolling by invitationMPS III BUnited States, Germany, Turkey, United Kingdom, Colombia
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ShireCompletedHunter SyndromeUnited Kingdom, United States, Brazil
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SanofiCompletedOsteochondrodysplasiaUnited States
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BioMarin PharmaceuticalCompleted
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Patricia I. Dickson, M.D.The Ryan FoundationTerminatedMucopolysaccharidosis I | Scheie Syndrome | Lysosomal Storage Disease | Spinal Cord Compression | Hurler-Scheie SyndromeFinland, United States
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Masonic Cancer Center, University of MinnesotaBioMarin PharmaceuticalTerminated
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BioMarin PharmaceuticalCompletedMPS IV AUnited States, Canada, France, United Kingdom, Taiwan, Argentina, Colombia, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, Germany, Portugal, Italy, Qatar
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TakedaRecruitingHunter SyndromeCanada, France
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Masonic Cancer Center, University of MinnesotaCompleted
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CENTOGENE GmbH RostockCompletedMorquio DiseasePakistan
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Alexion PharmaceuticalsCompletedMPS IIIB (Sanfilippo B Syndrome)United Kingdom
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ShireCompletedHunter SyndromeSpain, United States, Canada, United Kingdom, France, Australia, Mexico
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Samsung Medical CenterNot yet recruitingSanfilippo Syndrome A
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ShireCompletedSanfilippo SyndromeUnited States, Spain, United Kingdom, Argentina, France, Germany, Italy, Netherlands
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UniQure Biopharma B.V.Institut Pasteur; Venn Life SciencesCompleted
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ShireActive, not recruitingHunter SyndromeUnited States, United Kingdom, Canada
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SanofiRecruitingOsteochondrodysplasiaAustralia, Spain, Korea, Republic of, China, Italy
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Oregon Health and Science UniversityUniversity of Utah; BioMarin PharmaceuticalCompleted
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Japan Tobacco Inc.CompletedType II HyperlipidaemiaNetherlands
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St. Jude Children's Research HospitalRecruitingMucopolysaccharidosis I | Severe Combined Immunodeficiency | Neuroblastoma | Neoplasm | Malignancy, HematologicUnited States
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Microbio Co LtdCompleted