Clinical Trials on Mucopolysaccharidosis I in United States
Total 1275 results
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Masonic Cancer Center, University of MinnesotaRecruitingMucopolysaccharidosis Type I | Hematopoietic Cell TransplantationUnited States
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REGENXBIO Inc.Active, not recruitingHurler Syndrome | Hurler-Scheie Syndrome | Mucopolysaccharidosis Type I (MPS I)United States, Brazil, Israel
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Immusoft of CA, Inc.RecruitingMucopolysaccharidosis IH/S | Mucopolysaccharidosis ISUnited States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedMucopolysaccharidosis Type IUnited States
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Masonic Cancer Center, University of MinnesotaTerminatedHurler Syndrome | Mucopolysaccharidosis Type IH | MPS IUnited States
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Genzyme, a Sanofi CompanyRecruitingMucopolysaccharidosis I (MPS I)Croatia, United States, Argentina, Australia, Belgium, Brazil, Canada, Denmark, France, Hong Kong, India, Indonesia, Korea, Republic of, Kuwait, Lebanon, Malaysia, Netherlands, Pakistan, Philippines, Poland, Saudi Arabia, Singapore, Slovaki... and more
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Masonic Cancer Center, University of MinnesotaCompleted
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Sangamo TherapeuticsTerminated
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Lundquist Institute for Biomedical Innovation at...CompletedMucopolysaccharidosis Type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VIUnited States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedMucopolysaccharidosis Type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VI | Mucopolysaccharidosis Type IV | Mucopolysaccharidosis Type VIIUnited States, Canada
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University of ChicagoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedKrabbe Disease | Mucopolysaccharidosis Type II (MPS II) | Mucopolysaccharidosis Type I (MPS I) | Mucopolysaccharidosis Type III (MPS III) | Mucopolysaccharidosis Type VI (MPS VI)United States
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Orchard TherapeuticsRecruitingMPS-IH (Hurler Syndrome)Netherlands, United States, Italy, United Kingdom
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JCR Pharmaceuticals Co., Ltd.Active, not recruitingMucopolysaccharidosis IUnited States, Brazil, Japan
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JCR Pharmaceuticals Co., Ltd.CompletedMucopolysaccharidosis IUnited States, Brazil, Japan
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REGENXBIO Inc.Enrolling by invitation
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ArmaGen, IncCompletedMucopolysaccharidosis IUnited States
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Masonic Cancer Center, University of MinnesotaCompletedMucopolysaccharidosis I | Mucopolysaccharidosis VI | Mannosidosis | Mucolipidosis Type II (I-cell Disease)United States
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Masonic Cancer Center, University of MinnesotaCompletedMucopolysaccharidosis I | Hurler SyndromeUnited States
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Lundquist Institute for Biomedical Innovation at...Active, not recruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIUnited States
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agnes chenUniversity of California, Los Angeles; National Institute of Neurological Disorders... and other collaboratorsTerminatedMucopolysaccharidosis I | Cognitive DeclineUnited States
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National MPS SocietyMediResource Inc.TerminatedMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidoses | Mucopolysaccharidosis VI | Mucopolysaccharidosis IVUnited States
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Nationwide Children's HospitalSanfilippo Children's Research Foundation; The Sanfilippo Research Foundation; The Children's Medical Research FoundationCompletedMucopolysaccharidosis Type IIIA | Mucopolysaccharidosis Type IIIBUnited States
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Lundquist Institute for Biomedical Innovation at...TerminatedMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIUnited States
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Sanguine BiosciencesDenali Therapeutics Inc.RecruitingMucopolysaccharidosis III-AUnited States
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Patricia I. Dickson, M.D.University of California, Los Angeles; FDA Office of Orphan Products Development and other collaboratorsTerminatedMucopolysaccharidosis I | Lysosomal Storage Diseases | Spinal Cord CompressionUnited States, Finland
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Hurler's Syndrome | Hurler-Scheie Syndrome | Scheie's SyndromeUnited States
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Abeona Therapeutics, IncTerminatedMucopolysaccharidosis III-BUnited States, Germany, France
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Scheie Syndrome | Hurler Syndrome | Hurler-Scheie SyndromeNetherlands, France, Germany, United Kingdom
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Hurler-Scheie Syndrome | Hurlers SyndromeUnited States, Canada, Germany
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Children's Hospitals and Clinics of MinnesotaBioMarin Pharmaceutical; Gillette Children's Specialty Healthcare; Greenwood...CompletedMucopolysaccharidosis VI | Mucopolysaccharidosis IV AUnited States
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncEnrolling by invitationMucopolysaccharidosis III-AUnited States, Australia, Spain
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Abeona Therapeutics, IncTerminatedMucopolysaccharidosis Type 3 BUnited States, Germany, France, Spain
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Allievex CorporationCompletedMucopolysaccharidosis Type IIIB | Mucopolysaccharidosis Type 3 B | MPS III B | MPS 3 BUnited States, Spain, Turkey, Taiwan, Australia, Colombia, Germany, United Kingdom
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedHurler Syndrome | Sanfilippo Syndrome Type A | Sanfilippo Syndrome Type BUnited States
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Alexion PharmaceuticalsCompletedMucopolysaccharidosis IIIBUnited States, United Kingdom, Spain
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Scheie Syndrome | Hurler's Syndrome | Hurler-Scheie SyndromeUnited States, Canada, United Kingdom, Brazil, Germany, Italy, Netherlands
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Masonic Cancer Center, University of MinnesotaCompleted
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Lundquist Institute for Biomedical Innovation at...Swedish Orphan Biovitrum; Cure Sanfilippo FoundationCompleted
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BioMarin PharmaceuticalCompleted
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BioMarin PharmaceuticalCompletedMucopolysaccharidosis VIUnited States
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BioMarin PharmaceuticalCompletedMucopolysaccharidosis VIUnited States
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BioMarin PharmaceuticalCompletedMucopolysaccharidosis VIUnited States
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LYSOGENEActive, not recruitingMucopolysaccharidosis Type IIIAGermany, United States, United Kingdom, France, Netherlands
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Allievex CorporationCompletedMucopolysaccharidosis Type IIIB | MPS III BUnited States, Taiwan, Spain, Colombia, Germany, United Kingdom, Turkey
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ShireTerminatedSanfilippo Syndrome | Mucopolysaccharidosis (MPS)United States, United Kingdom, Spain, Germany, France, Italy, Netherlands
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Denali Therapeutics Inc.RecruitingMucopolysaccharidosis Type IIIAUnited States
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Emory UniversityBioMarin PharmaceuticalTerminatedMucopolysaccharidosis Type IVAUnited States
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Patricia I. Dickson, M.D.National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University... and other collaboratorsCompletedMucopolysaccharidosis I | Scheie Syndrome | Lysosomal Storage Disease | Cognitive Decline | Hurler-Scheie SyndromeUnited States
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Allievex CorporationActive, not recruitingMucopolysaccharidosis Type IIIB | MPS III BGermany, United States, Turkey, United Kingdom, Colombia, Spain, Taiwan
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Emory UniversityBioMarin PharmaceuticalCompletedMPS - Mucopolysaccharidosis | Morquio DiseaseUnited States