- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Mucopolysaccharidosis VI
Total 232 results
-
CENTOGENE GmbH RostockWithdrawnLung Diseases | Eye Abnormalities | Lysosomal Storage Disease | Macroglossia | Obstructive Sleep ApnoeaGermany, India, Sri Lanka, Egypt
-
University of ManchesterManchester University NHS Foundation Trust; Great Ormond Street Hospital for... and other collaboratorsRecruiting
-
GC Biopharma CorpRecruitingMucopolysaccharidosis II | Hunter SyndromeKorea, Republic of
-
Homology Medicines, IncWithdrawnMucopolysaccharidosis IIUnited States, Canada
-
JCR Pharmaceuticals Co., Ltd.Active, not recruitingMucopolysaccharidosis IIBrazil
-
ShireCompletedMucopolysaccharidosis IIUnited States, United Kingdom, Brazil, Germany
-
GlaxoSmithKlineCompletedMucopolysaccharidosis IIJapan
-
Green Cross CorporationUnknownMucopolysaccharidosis II
-
TakedaRecruiting
-
University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedMucopolysaccharidosesUnited States
-
Lundquist Institute for Biomedical Innovation at...National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedMucopolysaccharidosesUnited States
-
Sangamo TherapeuticsActive, not recruitingHemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis IIUnited States
-
Lysosomal and Rare Disorders Research and Treatment...Team SanfilippoRecruitingSanfilippo Syndrome | MPS3United States
-
Allievex CorporationEnrolling by invitationMPS III BUnited States, Germany, Turkey, United Kingdom, Colombia
-
SanofiCompletedOsteochondrodysplasiaUnited States
-
BioMarin PharmaceuticalCompleted
-
Green Cross CorporationCompleted
-
Green Cross CorporationUnknownThe Long-term Safety Study of Idursulfase-beta in Hunter Syndrome(Mucopolysaccharidosis II) PatientsHunter SyndromeKorea, Republic of
-
Patricia I. Dickson, M.D.The Ryan FoundationTerminatedMucopolysaccharidosis I | Scheie Syndrome | Lysosomal Storage Disease | Spinal Cord Compression | Hurler-Scheie SyndromeFinland, United States
-
Duke UniversityRecruiting
-
BioMarin PharmaceuticalCompletedMPS IV AUnited States, Canada, France, United Kingdom, Taiwan, Argentina, Colombia, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, Germany, Portugal, Italy, Qatar
-
Masonic Cancer Center, University of MinnesotaCompleted
-
CENTOGENE GmbH RostockCompletedMorquio DiseasePakistan
-
Alexion PharmaceuticalsCompletedMPS IIIB (Sanfilippo B Syndrome)United Kingdom
-
Samsung Medical CenterNot yet recruitingSanfilippo Syndrome A
-
ShireCompletedSanfilippo SyndromeUnited States, Spain, United Kingdom, Argentina, France, Germany, Italy, Netherlands
-
UniQure Biopharma B.V.Institut Pasteur; Venn Life SciencesCompleted
-
SanofiRecruitingOsteochondrodysplasiaAustralia, Spain, Korea, Republic of, China, Italy
-
Phoenix NestNational Institute of Neurological Disorders and Stroke (NINDS)Enrolling by invitationSanfilippo Syndrome Type DUnited States
-
Swedish Orphan BiovitrumCompletedSanfilippo Syndrome Type A (MPS IIIA)United States, Turkey
-
Swedish Orphan BiovitrumCompletedSanfilippo Syndrome Type A (MPS IIIA)United States, Germany, Turkey
-
ShireTerminatedSanfilippo SyndromeNetherlands, United Kingdom
-
Oregon Health and Science UniversityUniversity of Utah; BioMarin PharmaceuticalCompleted
-
ShireCovance; PRA Health Sciences; PharmaNetCompletedMucopolysaccharidosis II | Hunter Syndrome | MPS IIBrazil, Poland, Taiwan
-
CENTOGENE GmbH RostockTerminatedMucopolysaccharidosis II | Hunter Syndrome | Hunter's Syndrome, Mild Form | Hunter's Canal SyndromeMexico
-
ShireCompletedSanfilippo Syndrome Type AUnited States
-
Masonic Cancer Center, University of MinnesotaRecruitingHurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Metachromatic Leukodystrophy | Alpha-Mannosidosis | Hunter Syndrome | Mucopolysaccharidosis Disorders | Maroteaux Lamy Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Glycoprotein Metabolic Disorders | Recessive Leukodystrophies | Globoid... and other conditionsUnited States
-
Children's Hospital of Orange CountyUltragenyx Pharmaceutical IncRecruitingInflammation | Mucopolysaccharidoses | Cardiac Disease | Carotid DiseaseUnited States
-
CENTOGENE GmbH RostockWithdrawnDevelopmental Delay | Splenomegaly | Hepatomegaly | Skeletal AbnormalitiesGermany, India, Sri Lanka, Egypt
-
Clínica de Hidroterapia e Recuperacao FuncionalIntegrated Faculty of RecifeTerminatedMorquio's Disease
-
Masonic Cancer Center, University of MinnesotaTerminatedSphingolipidoses | Niemann-Pick Disease, Type C | Krabbe Disease | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Hurler's Syndrome | Maroteaux-Lamy Syndrome | Wolman's Disease | Niemann-Pick Disease Type BUnited States
-
Duke UniversityKriya TherapeuticsRecruitingGlycogen Storage Disease VI | GLYCOGEN STORAGE DISEASE IXa1 | GLYCOGEN STORAGE DISEASE IXa2 | Glycogen Storage Disease IXB | Glycogen Storage Disease IXC | GSD 9 (All Subtypes) | GSD 6United States
-
CENTOGENE GmbH RostockWithdrawnMorquio Syndrome A | Morquio Syndrome | Morquio B Disease | Accumulation of MucopolysaccharidesGermany, India, Sri Lanka, Egypt
-
St. Jude Children's Research HospitalRecruitingMucopolysaccharidosis I | Severe Combined Immunodeficiency | Neuroblastoma | Neoplasm | Malignancy, HematologicUnited States
-
ShireCompleted
-
TakedaTakeda Development Center Americas, Inc.Active, not recruitingHunter SyndromeUnited States, Germany, Malaysia, Philippines, Thailand, Dominican Republic, Serbia, Vietnam
-
Fairview University Medical CenterUnknownMucopolysaccharidosis I | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Pulmonary Complications | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Mannosidosis | I Cell DiseaseUnited States
-
TakedaAvailableHunter SyndromeUnited States, Australia, Mexico, Spain, United Kingdom
-
Green Cross CorporationCompleted