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Clinical Trials on Muscular Dystrophy, Emery-Dreifuss
Total 736 results
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophySpain, United States, Russian Federation, Italy, China, Turkey
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Santhera PharmaceuticalsNo longer availableDuchenne Muscular DystrophyUnited States
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PfizerCompletedDuchenne Muscular DystrophyChina
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ENCellCompletedDuchenne Muscular DystrophyKorea, Republic of
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NS Pharma, Inc.Cooperative International Neuromuscular Research Group; Nippon Shinyaku Co.... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada
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Hacettepe UniversityActive, not recruitingDuchenne Muscular DystrophyTurkey
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NS Pharma, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Canada
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National Center of Neurology and Psychiatry, JapanNippon Shinyaku Co., Ltd.Completed
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Hacettepe UniversityCompletedMuscular Dystrophy, DuchenneTurkey
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Cure Rare Disease, IncUniversity of Massachusetts, WorcesterActive, not recruiting
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Hadassah Medical OrganizationCompletedDuchenne Muscular Dystrophy
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Sarepta Therapeutics, Inc.CompletedMuscular Dystrophy, DuchenneUnited States, Canada
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Catabasis PharmaceuticalsCompletedMuscular Dystrophy, DuchenneUnited States, Canada, Australia, United Kingdom, Germany, Ireland, Israel, Sweden
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Karadeniz Technical UniversityCompleted
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ItalfarmacoCompletedBecker Muscular DystrophyNetherlands, Italy
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyBelgium, France, Italy, United Kingdom
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Craig McDonald, MDCardero Therapeutics, Inc.Completed
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University of North Carolina, Chapel HillNational Institute of Neurological Disorders and Stroke (NINDS)CompletedMuscular Dystrophy, DuchenneUnited States
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Wave Life Sciences Ltd.TerminatedDuchenne Muscular DystrophyUnited States, Belgium, United Kingdom, Czechia, Canada, France, Italy, Sweden
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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University of Sao PauloCompletedDuchenne Muscular Dystrophy
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University of Sao PauloCompletedDuchenne Muscular DystrophyBrazil
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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University of FloridaEngage Health Inc.CompletedDuchenne Muscular DystrophyUnited States
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Taiho Pharmaceutical Co., Ltd.Completed
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Hacettepe UniversityUnknownDuchenne Muscular DystrophyTurkey
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Summit TherapeuticsTerminatedDuchenne Muscular DystrophyUnited States, United Kingdom
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Ohio State UniversityUniversity of Colorado, Denver; University of California, Los Angeles; Vanderbilt... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States
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University Medical Center NijmegenLeiden University Medical Center; Princess Beatrix Muscle FoundationCompletedPediatric Disorder | Facioscapulohumeral Muscular Dystrophy | Neurological ObservationsNetherlands
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EspeRare FoundationCompletedMuscular Dystrophy, DuchenneItaly, France, Spain, United Kingdom
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University of FloridaCureDuchenneCompletedMuscular Dystrophy, DuchenneUnited States
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Akashi TherapeuticsTerminatedDuchenne Muscular DystrophyUnited States
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GlaxoSmithKlineCompletedMuscular DystrophiesFrance, Denmark, Germany, Belgium, Spain, Turkey, Korea, Republic of, Brazil, Netherlands, Italy, Chile, Japan, Canada, Hungary, Russian Federation, Czechia, Poland, Norway, Argentina, Taiwan
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Cedars-Sinai Medical CenterCompleted
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University of MinnesotaFairview Health ServicesWithdrawnDuchenne Muscular Dystrophy
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PTC TherapeuticsParexel; Dohmen Life Science ServicesApproved for marketingDuchenne Muscular DystrophyUnited States
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University of FloridaUnited States Department of DefenseCompletedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyBelgium, Netherlands, Italy, Sweden
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Jerry R. MendellEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedDuchenne Muscular DystrophyUnited States
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Boston Children's HospitalBeth Israel Deaconess Medical CenterCompletedDuchenne Muscular DystrophyUnited States
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University of GaziantepIstınye University, Cukurova University, Yıldırım Beyazıt University, Gaziantep...UnknownDuchenne Muscular DystrophyTurkey
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GlaxoSmithKlineWithdrawnMuscular Dystrophies
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedDuchenne Muscular DystrophyCanada
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Shenzhen Beike Bio-Technology Co., Ltd.The Second Affiliated Hospital of Kunming Medical UniversityUnknownDuchenne Muscular DystrophyChina
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Nationwide Children's HospitalNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes...CompletedDuchenne Muscular DystrophyUnited States
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Cooperative International Neuromuscular Research...Completed
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Cooperative International Neuromuscular Research...Completed
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National Institute of Neurological Disorders and...CompletedMuscular Dystrophy | Muscular DiseaseUnited States
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedLimb-Girdle Muscular DystrophyUnited States