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Clinical Trials on Muscular Dystrophy, Duchenne in United States
Total 17803 results
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Cure CMDRecruitingEmery-Dreifuss Muscular Dystrophy | Congenital Myasthenic Syndrome | Limb-Girdle Muscular Dystrophy | Congenital Muscular Dystrophy With ITGA7 (Integrin Alpha-7) Deficiency | Alpha-Dystroglycanopathy (Congenital Muscular Dystrophy and Abnormal Glycosylation of Dystroglycan With Severe Epilepsy) and other conditionsUnited States
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Stanford UniversityBiogenActive, not recruitingMyotonic Dystrophy 1United States
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Legacy Health SystemDevers Eye Institute; Lions Eye Bank of Oregon Vision Research Laboratory; Fischer...UnknownFuchs' Corneal Endothelial DystrophyUnited States
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Wake Forest University Health SciencesNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMyotonic Dystrophy Type 2United States
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Vertex Pharmaceuticals IncorporatedRecruitingMyotonic Dystrophy Type 1 (DM1)United Kingdom, Canada, Australia
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Gillette Children's Specialty HealthcareUniversity of MinnesotaCompletedSpinal Muscular Dystrophy | Neuromuscular DisabilityUnited States
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Boston Children's HospitalMuscular Dystrophy AssociationRecruitingCentronuclear Myopathy | Myotubular Myopathy | Nemaline Myopathy | Central Core Disease | Congenital Fiber Type Disproportion | Multiminicore Disease | Rigid Spine Muscular Dystrophy | Undefined Congenital MyopathyUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedCardiomyopathy, Hypertrophic | Muscular Dystrophy, OculopharyngealUnited States
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Dyne TherapeuticsRecruitingMyotonic Dystrophy Type 1 (DM1)United Kingdom, France, Netherlands, Italy, Germany, New Zealand
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State University of New York at BuffaloActive, not recruitingFuchs DystrophyUnited States
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Sarepta Therapeutics, Inc.RecruitingLimb-girdle Muscular DystrophyUnited States, Brazil, Belgium, Canada, Germany, Italy, Spain, Sweden, Turkey, United Kingdom
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); University... and other collaboratorsCompletedMyotonic Dystrophy Type 1United States
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Medical College of WisconsinCompletedCataract | Fuchs' Corneal DystrophyUnited States
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Wake Forest University Health SciencesTerminatedFuchs Dystrophy | Cystoid Macular EdemaUnited States
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GlaxoSmithKlineCompleted
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FDA Office of Orphan Products DevelopmentCompletedMuscular DystrophiesUnited States
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Cornea Research Foundation of AmericaCompletedBullous Keratopathy | Fuchs' Endothelial Corneal Dystrophy | Iridocorneal Endothelial Syndrome | Posterior Polymorphous DystrophyUnited States
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Edgewise Therapeutics, Inc.CompletedMuscular DystrophiesUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Terminated
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University of Texas Southwestern Medical CenterWithdrawnCorneal Epithelial DystrophyUnited States
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Massachusetts Eye and Ear InfirmaryRecruitingFuchs' Endothelial Corneal DystrophyUnited States
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Ionis Pharmaceuticals, Inc.CompletedMyotonic Dystrophy Type 1United States
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Wake Forest University Health SciencesCompleted
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Katherine MathewsNational Institute of Neurological Disorders and Stroke (NINDS)Recruiting
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Edgewise Therapeutics, Inc.CompletedNervous System Diseases | Genetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Healthy VolunteerUnited States
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AMO Pharma LimitedCompletedCongenital Myotonic DystrophyUnited States, Canada, New Zealand, Australia, United Kingdom
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ML Bio Solutions, Inc.Active, not recruiting
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Astellas Institute for Regenerative MedicineCompleted
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Massachusetts Eye and Ear InfirmaryRecruitingFuchs Endothelial Corneal DystrophyUnited States
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Astellas Institute for Regenerative MedicineCompleted
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Duke UniversityCompleted
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Food and Drug Administration (FDA)National Eye Institute (NEI)RecruitingAge-Related Macular Degeneration | Retinal Degeneration | Retinitis Pigmentosa | Usher Syndromes | Cone Dystrophy | Rod Dystrophy | Cone Rod Dystrophy | Hydroxychloroquine Retinopathy | Late-Onset Retinal Degeneration | Rod Cone DystrophyUnited States
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AMO Pharma LimitedCompletedMyotonic Dystrophy 1United Kingdom
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Insmed IncorporatedMuscular Dystrophy AssociationCompleted
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Children's National Research InstituteActive, not recruitingGenetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Dystrophies | Cardiac FibrosisUnited States
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AMO Pharma LimitedRecruitingCongenital Myotonic DystrophyUnited States, Canada, Australia, New Zealand
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Newcastle UniversityLudwig-Maximilians - University of Munich; LGMD2i Research Fund; CureLGMD2iRecruitingLimb Girdle Muscular Dystrophy | Congenital Muscular Dystrophy | LGMDR9 | LGMD2I | Walker-Warburg Syndrome | Muscle-Eye-Brain Disease | FKRP Gene MutationUnited Kingdom
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The Cleveland ClinicNational Eye Institute (NEI)CompletedRetinal Detachment | Epiretinal Membrane | Fuchs Endothelial Dystrophy | Macular HoleUnited States
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Astellas Pharma Global Development, Inc.Active, not recruitingStargardt's Macular DystrophyItaly, United States, Israel, United Kingdom, Germany, Spain, Hungary, France
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Cornea Research Foundation of AmericaCompletedCorneal Edema | Fuchs' DystrophyUnited States
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Trefoil Therapeutics, Inc.CompletedEndothelial Dysfunction | Corneal Endothelial Dystrophy | Pseudophakic Bullous Keratopathy | Fuchs Endothelial Corneal DystrophyUnited States
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Eunice Kennedy Shriver National Institute of Child...National Institutes of Health Clinical Center (CC); National Institute of Neurological... and other collaboratorsActive, not recruitingGenetic DisorderUnited States
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Newcastle-upon-Tyne Hospitals NHS TrustCompletedMyotonic Dystrophy Type 1United Kingdom
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Price Vision GroupCompletedBullous Keratopathy | Fuchs' DystrophyUnited States, Germany
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Harmony Biosciences, LLCActive, not recruitingMyotonic Dystrophy 1 | Excessive Daytime SleepinessUnited States, Canada
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NYU Langone HealthNational Eye Institute (NEI)Active, not recruitingFuch's Dystrophy | Corneal Disorders | Prior SurgeryUnited States
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University of LiverpoolBournemouth University; Robert Jones and Agnes Hunt Orthopaedic and District... and other collaboratorsRecruitingNeuromuscular Diseases | Shoulder Injuries | Shoulder Pain | Upper Extremity Problem | Facio-Scapulo-Humeral DystrophyUnited Kingdom
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Manhattan Eye, Ear & Throat HospitalGenentech, Inc.CompletedPolypoidal Choroidal Vasculopathy | Pseudoxanthoma Elasticum | Pathological Myopia | Retinal Angiomatous Proliferation | Coats' Disease | Idiopathic Retinal Telangiectasia | Multi-focal Choroiditis | Rubeosis Iridis | Von Hippel Lindau Disease | BEST VITELLIFORM MACULAR DYSTROPHY, MULTIFOCAL (Disorder)United States
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedCharcot-Marie-Tooth Disease | Facioscapulohumeral Muscular DystrophyUnited States, Spain, Canada
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Retrotope, Inc.CompletedInfantile Neuroaxonal Dystrophy | INADUnited States