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Clinical Trials on Muscular Dystrophy in United Kingdom
Total 17713 results
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Nationwide Children's HospitalBoston Children's Hospital; University of California, Davis; University of Minnesota and other collaboratorsCompletedCardiomyopathy | Duchenne Muscular Dystrophy (DMD)United States
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Hope Biosciences Stem Cell Research FoundationHope BiosciencesNo longer availableCongenital Muscular Dystrophy Due to Lamin A/C MutationUnited States
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Cooperative International Neuromuscular Research...Completed
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Skulpt, Inc.National Institute of Neurological Disorders and Stroke (NINDS)CompletedDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Korea, Republic of, Italy, United Kingdom, Canada, Poland, Spain, France, Germany, Belgium, Australia, Czechia, Serbia, Greece, Argentina, Bulgaria, Denmark, Hungary, India, Ireland, Israel, Mexico, Russian Federation, ...
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NS Pharma, Inc.Cooperative International Neuromuscular Research Group; Nippon Shinyaku Co.... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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PfizerActive, not recruitingDuchenne Muscular DystrophyUnited States
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Processa PharmaceuticalsTerminated
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Craig McDonald, MDCardero Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophySpain, United States, Russian Federation, Italy, China, Turkey
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Ohio State UniversityUniversity of Colorado, Denver; University of California, Los Angeles; Vanderbilt... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.Hoffmann-La RocheEnrolling by invitation
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Sarepta Therapeutics, Inc.Hoffmann-La RocheEnrolling by invitationDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Catabasis PharmaceuticalsCompletedMuscular Dystrophy, DuchenneUnited States
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Processa PharmaceuticalsTerminatedDuchenne Muscular DystrophyUnited States
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Avidity Biosciences, Inc.Enrolling by invitationDuchenne Muscular Dystrophy | DMD | Exon 44 | DuchenneUnited States
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Children's Hospital Medical Center, CincinnatiActive, not recruitingMusculoskeletal Abnormalities | Duchenne Muscular DystrophyUnited States
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National Human Genome Research Institute (NHGRI)TerminatedCommunication | Genetic DiseaseUnited States
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Sarepta Therapeutics, Inc.CompletedMuscular Dystrophy, DuchenneUnited States, Canada
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Wake Forest University Health SciencesMuscular Dystrophy AssociationCompletedMuscular Dystrophies, Limb-Girdle (GENETICALLY CONFIRMED)United States
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Dart Therapeutics. LLCCompletedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Washington University School of MedicineUniversity of California, Davis; Nationwide Children's Hospital; University of... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States
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Edgewise Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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GlaxoSmithKlineTerminatedMuscular DystrophiesFrance, Bulgaria, Denmark, Germany, Belgium, Canada, Spain, Turkey, United Kingdom, Korea, Republic of, Brazil, Netherlands, Italy, Japan, Czech Republic, Chile, Israel, Hungary, Russian Federation, Australia, Poland, Norway, Argentina and more
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Newcastle UniversityRecruiting
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Cooperative International Neuromuscular Research...Washington University School of Medicine; Children's National Research Institute and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Australia, Italy
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Cumberland PharmaceuticalsVanderbilt University Medical CenterRecruitingCardiomyopathy, Dilated | Duchenne Muscular Dystrophy CardiomyopathyUnited States
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PfizerActive, not recruitingMuscular Dystrophy, DuchenneUnited States, Australia
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Shriners Hospitals for ChildrenCompletedDuchenne Muscular DystrophyUnited States
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedFacioscapulohumeral Muscular DystrophyUnited States, Spain, Canada
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Capricor Inc.CompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States
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Santhera PharmaceuticalsNo longer availableDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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NS Pharma, Inc.Cooperative International Neuromuscular Research Group; Nippon Shinyaku Co.... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.RecruitingDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.CompletedMuscular Dystrophy, DuchenneUnited States
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Mayo ClinicNational Eye Institute (NEI)CompletedRetinal Disease | Best Vitelliform Macular Dystrophy | Bestrophinopathy | Adult Onset Vitelliform Macular Dystrophy | Autosomal Dominant VitreoretinalchoroidopathyUnited States
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Sarepta Therapeutics, Inc.TerminatedMuscular Dystrophy, DuchenneUnited States, Canada
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Cooperative International Neuromuscular Research...UnknownDuchenne Muscular DystrophyUnited States, Canada
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States
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AbiliTech Medical Inc.Richard M. Schulze Family FoundationRecruitingCerebral Palsy | Muscular Dystrophies | Duchenne Muscular Dystrophy | Becker Muscular Dystrophy | Spinal Muscular Atrophy | Limb Girdle Muscular Dystrophy | FSHDUnited States
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Avidity Biosciences, Inc.Active, not recruitingNervous System Diseases | Genetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Neurodegenerative Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Heredodegenerative Disorders, Nervous System | Myotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy... and other conditionsUnited States
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GlaxoSmithKlineCompletedMuscular DystrophiesUnited States
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Santhera PharmaceuticalsAvailableDuchenne Muscular DystrophyUnited States, Canada, Israel
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Edgewise Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Mallinckrodt ARD LLCTerminatedMuscular Dystrophy, DuchenneSpain, Bulgaria, Italy, United States, Mexico, Israel, Serbia, Turkey