- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Muscular Dystrophy in United States
Total 17803 results
-
National Human Genome Research Institute (NHGRI)TerminatedCommunication | Genetic DiseaseUnited States
-
Bioblast Pharma Ltd.CompletedOculopharyngeal Muscular DystrophyUnited States, Israel, Canada
-
PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, United Kingdom
-
Edgewise Therapeutics, Inc.Worldwide Clinical TrialsCompletedBecker Muscular Dystrophy | Healthy VolunteerUnited States
-
Sarepta Therapeutics, Inc.CompletedMuscular Dystrophy, DuchenneUnited States
-
Solid Biosciences Inc.RecruitingDuchenne Muscular DystrophyUnited States
-
Solid Biosciences Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States
-
The Emmes Company, LLCJain Foundation; Coalition to Cure Calpain 3 (C3)Terminated
-
Benitec Biopharma, Inc.RecruitingOculopharyngeal Muscular DystrophyUnited States
-
University of FloridaCompleted
-
Craig McDonald, MDCardero Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
-
Sarepta Therapeutics, Inc.University College, London; Catholic University of the Sacred Heart; University... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited Kingdom, United States, France, Italy
-
Sarepta Therapeutics, Inc.Active, not recruiting
-
Virginia Commonwealth UniversityUniversity of Colorado, Denver; Washington University School of Medicine; University... and other collaboratorsRecruitingLimb Girdle Muscular Dystrophy | Calpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2A | Limb Girdle Muscular Dystrophy Type R1 | LGMD2AUnited States, Netherlands, United Kingdom
-
Wake Forest University Health SciencesMuscular Dystrophy AssociationCompletedMuscular Dystrophies, Limb-Girdle (GENETICALLY CONFIRMED)United States
-
Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
-
Nationwide Children's HospitalNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes...CompletedDuchenne Muscular DystrophyUnited States
-
Epirium Bio Inc.CompletedBecker Muscular DystrophyUnited States
-
Newcastle-upon-Tyne Hospitals NHS TrustRecruitingBethlem Myopathy | Ullrich Congenital Muscular Dystrophy 1, Digenic, Col6A1/Col6A2 | Ullrich Congenital Muscular Dystrophy 1, Autosomal Recessive | Ullrich Congenital Muscular Dystrophy 1, Autosomal Dominant | Bethlem Myopathy 1, Autosomal Recessive | UCMD | BTHLM1United Kingdom
-
Sarepta Therapeutics, Inc.CompletedDuchenne Muscular Dystrophy (DMD)United States
-
Fulcrum TherapeuticsActive, not recruitingFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Canada, France, Spain
-
Fulcrum TherapeuticsCompletedFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Canada, France, Spain
-
ML Bio Solutions, Inc.RecruitingLimb-Girdle Muscular Dystrophy Type 2I (LGMD2I)United States, Netherlands, United Kingdom, Denmark, Australia, Italy, Norway
-
Sarepta Therapeutics, Inc.CompletedDuchenne Muscular Dystrophy (DMD)United States
-
AbiliTech Medical Inc.Richard M. Schulze Family FoundationRecruitingCerebral Palsy | Muscular Dystrophies | Duchenne Muscular Dystrophy | Becker Muscular Dystrophy | Spinal Muscular Atrophy | Limb Girdle Muscular Dystrophy | FSHDUnited States
-
Anne M. ConnollyAnn & Robert H Lurie Children's Hospital of Chicago; Children's Hospital Medical... and other collaboratorsRecruiting
-
Skulpt, Inc.National Institute of Neurological Disorders and Stroke (NINDS)CompletedDuchenne Muscular DystrophyUnited States
-
Sarepta Therapeutics, Inc.RecruitingLimb-girdle Muscular DystrophyUnited States
-
Catabasis PharmaceuticalsCompletedMuscular Dystrophy, DuchenneUnited States
-
Processa PharmaceuticalsTerminatedDuchenne Muscular DystrophyUnited States
-
Fulcrum TherapeuticsActive, not recruitingFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Spain, Italy, Denmark, Canada, Germany, France, Netherlands, United Kingdom
-
PfizerRecruitingDuchenne Muscular DystrophyUnited States
-
Akashi TherapeuticsTerminatedDuchenne Muscular DystrophyUnited States
-
PfizerActive, not recruitingDuchenne Muscular DystrophyUnited States
-
Processa PharmaceuticalsTerminated
-
Nationwide Children's HospitalBoston Children's Hospital; University of California, Davis; University of Minnesota and other collaboratorsCompletedCardiomyopathy | Duchenne Muscular Dystrophy (DMD)United States
-
Mayo ClinicNational Eye Institute (NEI)CompletedRetinal Disease | Best Vitelliform Macular Dystrophy | Bestrophinopathy | Adult Onset Vitelliform Macular Dystrophy | Autosomal Dominant VitreoretinalchoroidopathyUnited States
-
Shriners Hospitals for ChildrenCompletedDuchenne Muscular DystrophyUnited States
-
Capricor Inc.Active, not recruiting
-
Sarepta Therapeutics, Inc.Hoffmann-La RocheEnrolling by invitation
-
Sarepta Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
-
PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
-
Wave Life Sciences Ltd.CompletedDuchenne Muscular DystrophyBelgium, United Kingdom, France, United States, Italy, Canada, Netherlands
-
REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
-
NS Pharma, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Canada
-
PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
-
Nationwide Children's HospitalParent Project Muscular DystrophyCompletedBecker Muscular Dystrophy | Sporadic Inclusion Body MyositisUnited States
-
National Eye Institute (NEI)National Cancer Institute (NCI)RecruitingStargardt-Like Macular DystrophyUnited States
-
Dyne TherapeuticsRecruitingDuchenne Muscular Dystrophy (DMD)United States, Belgium, Canada, United Kingdom, Australia, Spain, Italy
-
Washington University School of MedicineUniversity of California, Davis; Nationwide Children's Hospital; University of... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States