- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Muscular Dystrophy in United States
Total 17803 results
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National Eye Institute (NEI)National Cancer Institute (NCI)RecruitingStargardt-Like Macular DystrophyUnited States
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Washington University School of MedicineUniversity of California, Davis; Nationwide Children's Hospital; University of... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States
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Dart Therapeutics. LLCCompletedDuchenne Muscular DystrophyUnited States
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedMuscular DystrophiesUnited States
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Vanderbilt University Medical CenterRecruitingDuchenne Muscular DystrophyUnited States
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Vanderbilt University Medical CenterRecruitingDuchenne Muscular DystrophyUnited States
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NS Pharma, Inc.Cooperative International Neuromuscular Research Group; Nippon Shinyaku Co.... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Santhera PharmaceuticalsCompleted
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophySpain, United States, Russian Federation, Italy, China, Turkey
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Ohio State UniversityUniversity of Colorado, Denver; University of California, Los Angeles; Vanderbilt... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States
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Cooperative International Neuromuscular Research...Washington University School of Medicine; Children's National Research Institute and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Australia, Italy
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Jett Foundation, Inc.Pfizer; Hoffmann-La Roche; Italfarmaco; Nationwide Children's Hospital; Capricor... and other collaboratorsCompletedDuchenne Muscular Dystrophy | Rare Diseases | Disability Physical | Burden, Dependency | Impairment | Disease ManagementUnited States
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Great Ormond Street Hospital for Children NHS Foundation...Catholic University of the Sacred Heart; Università degli Studi di Ferrara; Universidad... and other collaboratorsRecruitingDuchenne Muscular Dystrophy | Becker Muscular DystrophyDenmark, France, Italy, Netherlands, Spain, United Kingdom
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PTC TherapeuticsMuscular Dystrophy AssociationCompletedDuchenne Muscular DystrophyUnited States
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Edgewise Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Capricor Inc.CompletedDuchenne Muscular DystrophyUnited States
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NS Pharma, Inc.Cooperative International Neuromuscular Research Group; Nippon Shinyaku Co.... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular DystrophyUnited States
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Newcastle UniversityRecruitingFacioscapulohumeral Muscular DystrophyUnited Kingdom
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Sarepta Therapeutics, Inc.CompletedMuscular Dystrophy, DuchenneUnited States, Canada
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Santhera PharmaceuticalsTerminatedDuchenne Muscular Dystrophy (DMD)United States, Spain, Netherlands, Sweden, Germany, France, Belgium, United Kingdom, Italy, Ireland, Switzerland, Austria, Bulgaria, Hungary, Israel
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Summit TherapeuticsTerminatedDuchenne Muscular DystrophyUnited States, United Kingdom
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ReveraGen BioPharma, Inc.University of Pittsburgh; Cooperative International Neuromuscular Research...CompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Sweden, Australia, Israel
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ReveraGen BioPharma, Inc.National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Sweden, Australia, Israel
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ReveraGen BioPharma, Inc.National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Sweden, Australia, Israel
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PfizerActive, not recruitingMuscular Dystrophy, DuchenneUnited States, Australia
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Sarepta Therapeutics, Inc.TerminatedMuscular Dystrophy, DuchenneUnited States, Canada
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Capricor Inc.CompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States
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University of PittsburghRespirtech, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.Hoffmann-La RocheEnrolling by invitationDuchenne Muscular DystrophyUnited States
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Cooperative International Neuromuscular Research...UnknownDuchenne Muscular DystrophyUnited States, Canada
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Sarepta Therapeutics, Inc.Completed
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Subha RamanBallou SkiesCompletedDuchenne Muscular DystrophyUnited States
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.RecruitingDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.CompletedMuscular Dystrophy, DuchenneUnited States
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States
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Great Ormond Street Hospital for Children NHS Foundation...Catholic University of the Sacred Heart; Università degli Studi di Ferrara; Universidad... and other collaboratorsRecruitingDuchenne Muscular Dystrophy | Becker Muscular DystrophyDenmark, France, Italy, Spain, United Kingdom, Netherlands
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Capricor Inc.CompletedDuchenne Muscular Dystrophy | CardiomyopathyUnited States
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Cumberland PharmaceuticalsVanderbilt University Medical CenterRecruitingCardiomyopathy, Dilated | Duchenne Muscular Dystrophy CardiomyopathyUnited States
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Sarepta Therapeutics, Inc.Active, not recruiting
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, Germany, Spain, Sweden, Canada, Italy, Australia, Belgium, France, Israel, United Kingdom
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Cooperative International Neuromuscular Research...UnknownBecker Muscular DystrophyUnited States, Canada, Italy, United Kingdom
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Santhera PharmaceuticalsNo longer availableDuchenne Muscular DystrophyUnited States
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Cooperative International Neuromuscular Research...aTyr Pharma, Inc.; Muscular Dystrophy Canada; FSHD Global Research Foundation; FSH...CompletedFacioscapulohumeral Muscular DystrophyUnited States, Canada, Australia, Sweden, United Kingdom
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GlaxoSmithKlineCompletedMuscular DystrophiesFrance, United States
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Avidity Biosciences, Inc.Active, not recruitingNervous System Diseases | Genetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Neurodegenerative Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Heredodegenerative Disorders, Nervous System | Myotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy... and other conditionsUnited States
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Wave Life Sciences Ltd.TerminatedDuchenne Muscular DystrophyUnited States, Belgium, United Kingdom, Czechia, Canada, France, Italy, Sweden
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Imperial College LondonSarepta Therapeutics, Inc.; Department of Health, United KingdomCompletedDuchenne Muscular DystrophyUnited Kingdom