- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Myotonic Dystrophy 1
Total 6989 results
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Cooperative International Neuromuscular Research...Completed
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Cooperative International Neuromuscular Research...Completed
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Alkeus Pharmaceuticals, Inc.RecruitingStargardt Disease | Stargardt Macular Degeneration | Stargardt Macular Dystrophy | Autosomal Recessive Stargardt Disease 1 (ABCA4-related)United States
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Alkeus Pharmaceuticals, Inc.Enrolling by invitationStargardt Disease | Stargardt Macular Degeneration | Stargardt Macular Dystrophy | Autosomal Recessive Stargardt Disease 1 (ABCA4-related)United States
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University Hospital, Clermont-FerrandEnrolling by invitationNeuroaxonal Dystrophy, AtypicalFrance
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University of TurkuUnknownUnverricht-Lundborg SyndromeFinland
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Sarepta Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Red Nucleus Enterprise Solutions, LLCRecruiting
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Egyptian Chinese UniversityBenha UniversityRecruitingDuchenne Muscular DystrophyEgypt
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ItalfarmacoRecruitingDuchenne Muscular DystrophyCanada, Italy, France, Belgium, Germany, Netherlands, United Kingdom
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Sarepta Therapeutics, Inc.Hoffmann-La RocheRecruitingDuchenne Muscular DystrophyUnited States, Japan, Spain, Italy
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Virginia Commonwealth UniversityNorthwestern University; University of RochesterRecruitingDuchenne Muscular DystrophyUnited States
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University of FloridaRecruiting
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Santhera PharmaceuticalsSanthera PharmaceuticalsActive, not recruitingDuchenne Muscular DystrophyCanada
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Sarepta Therapeutics, Inc.Active, not recruitingMuscular Dystrophy, DuchenneUnited States, Korea, Republic of, India, Slovenia, Turkey, United Kingdom, Germany, Switzerland, Spain, Czechia, France, Serbia, Taiwan, Netherlands, Mexico, Colombia, Denmark, New Zealand, Norway, Greece, Hungary, Ireland, Italy, Jo... and more
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PfizerActive, not recruitingDuchenne Muscular DystrophyUnited States, Spain, Belgium, Korea, Republic of, Taiwan, Canada, Australia, Germany, Japan, France, Italy, United Kingdom, Russian Federation, Israel, Switzerland
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Edgewise Therapeutics, Inc.Medpace, Inc.Enrolling by invitationBecker Muscular DystrophyUnited States, Netherlands
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Sheffield Children's NHS Foundation TrustSheffield Hallam University; National Institute for Health Research, United... and other collaboratorsActive, not recruiting
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Active, not recruitingDuchenne Muscular DystrophyKorea, Republic of, Chile, Japan, China, United Kingdom, Netherlands, Spain, Norway, Russian Federation, Australia, Greece, Italy, New Zealand, Turkey, Mexico, Czechia, Canada
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University College, LondonRadboud University Medical Center; Groupe Hospitalier Pitie-Salpetriere; Leiden... and other collaboratorsCompletedDuchenne Muscular DystrophyNetherlands, France, United Kingdom
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Santhera PharmaceuticalsAvailableDuchenne Muscular DystrophyUnited States, Canada, Israel
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophyKorea, Republic of, Chile, Taiwan, China, United States, United Kingdom, Netherlands, Spain, Australia, Norway, Russian Federation, Greece, Italy, Turkey, Mexico, Canada, Hong Kong, New Zealand, Ukraine
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Hacettepe UniversityCompletedDuchenne Muscular DystrophyTurkey
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.TerminatedMuscular Dystrophy, DuchenneUnited States, Canada
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ReveraGen BioPharma, Inc.University of Pittsburgh; Newcastle University; European Union; Cooperative International...CompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, United Kingdom, Spain, Netherlands, Sweden, Czechia, Australia, Greece, Israel
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Haukeland University HospitalExtrastiftelsenCompleted
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Phrixus Pharmaceuticals, Inc.Charley's FundTerminated
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Acceleron Pharma Inc. (a wholly owned subsidiary...Terminated
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Catabasis PharmaceuticalsCompletedMuscular Dystrophy, DuchenneUnited States
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Newcastle... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Germany, Italy
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ItalfarmacoSyneos HealthCompletedDuchenne Muscular DystrophyUnited States, Italy, Spain, Canada, Belgium, France, Germany, Israel, Netherlands, Serbia, United Kingdom
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Haukeland University HospitalOslo University Hospital; Norwegian School of Sport SciencesCompletedDuchenne Muscular DystrophyNorway
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NS Pharma, Inc.Cooperative International Neuromuscular Research Group; Nippon Shinyaku Co.... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada
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Santhera PharmaceuticalsTerminatedDuchenne Muscular DystrophyUnited States, Belgium, United Kingdom, Austria, France, Germany, Italy, Spain, Switzerland
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Charite University, Berlin, GermanyCompletedDuchenne Muscular DystrophyGermany
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Taiho Pharmaceutical Co., Ltd.Completed
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ReveraGen BioPharma, Inc.University of Pittsburgh; Cooperative International Neuromuscular Research...CompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Sweden, Australia, Israel
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Rare Disease Research, LLCSarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyUnited States
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Marmara UniversityUnknownDuchenne Muscular Dystrophy
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Children's Hospital Medical Center, CincinnatiIpsen; Charley's FundCompletedDuchenne Muscular DystrophyUnited States
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PfizerTerminatedDuchenne Muscular DystrophyUnited States, Australia, Canada, United Kingdom, Japan, Bulgaria, Italy, Poland
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Catabasis PharmaceuticalsTerminatedDuchenne Muscular DystrophyUnited States, Canada, Australia, United Kingdom, Germany, Sweden
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Processa PharmaceuticalsTerminatedDuchenne Muscular DystrophyUnited States
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Stem Cells ArabiaUnknownDuchenne Muscular DystrophyJordan
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National Center of Neurology and Psychiatry, JapanNippon Shinyaku Co., Ltd.Completed
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University Hospital, MontpellierHospital Clinical Research Project 2010; Association Amis FSH France; FSH Dutch...CompletedFacioscapulohumeral Muscular DystrophyFrance
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Cedars-Sinai Medical CenterCompletedBecker Muscular DystrophyUnited States
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Cedars-Sinai Medical CenterTerminatedMuscular DystrophyUnited States