- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Myotonic Dystrophy
Total 1486 results
-
PYC TherapeuticsRecruitingRetinitis Pigmentosa | Eye Diseases, Hereditary | Retinal Dystrophies | Retinal Dystrophy Rod | Retinal Dystrophy Rod ProgressiveUnited States, Australia
-
Centre Hospitalier Universitaire de NiceCompletedMuscular DystrophiesFrance
-
University of RochesterCompletedFacioscapulohumeral Muscular DystrophyUnited States
-
University of UtahCompletedMacular Dystrophy, CornealUnited States
-
National Eye Institute (NEI)Bausch & Lomb Incorporated; Eye Bank Association of America; Midwest Eye Banks; Tissue Banks International and other collaboratorsCompletedCorneal Disease | Fuch's Dystrophy | Pseudophakic Corneal EdemaUnited States
-
University of Kansas Medical CenterNational Institutes of Health (NIH)CompletedFacioscapulohumeral Muscular DystrophyUnited States
-
University of British ColumbiaTerminatedJuvenile Myoclonic Epilepsy | Childhood Absence Epilepsy | Juvenile Absence EpilepsyCanada
-
IRCCS San Camillo, Venezia, ItalyUniversita di Verona; Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico and other collaboratorsEnrolling by invitationCalpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2AItaly
-
Istanbul University - Cerrahpasa (IUC)CompletedFacioscapulohumeral Muscular DystrophyTurkey
-
Hugo W. Moser Research Institute at Kennedy Krieger...Active, not recruitingFacioscapulohumeral Muscular DystrophyUnited States
-
aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular DystrophyUnited States, Italy, Netherlands
-
Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedFacioscapulohumeral Muscular DystrophyUnited States, Spain, Canada
-
University of New MexicoUniversity of FloridaWithdrawnOculopharyngeal Muscular Dystrophy
-
Bioblast Pharma Ltd.CompletedOculopharyngeal Muscular DystrophyUnited States, Israel, Canada
-
Institut de Myologie, FranceAssociation Française contre les Myopathies (AFM), ParisNot yet recruitingMerosin Deficient Congenital Muscular DystrophyFrance
-
Prothelia, Inc.Cure CMD; The Bönnemann Laboratory, NINDS, National Institutes of Health; Oscar... and other collaboratorsCompletedMerosin Deficient Congenital Muscular DystrophyUnited States
-
Neil LagaliLinkoeping University; Sahlgrenska University Hospital, Sweden; Region Östergötland and other collaboratorsTerminatedCorneal Dystrophy, Epithelial Basement Membrane | Epithelial Recurrent Erosion Dystrophy | Corneal ErosionsSweden
-
Cumberland PharmaceuticalsVanderbilt University Medical CenterRecruitingCardiomyopathy, Dilated | Duchenne Muscular Dystrophy CardiomyopathyUnited States
-
National Institute of Neurological Disorders and...CompletedPeripheral Nervous System Disease | Focal DystoniaUnited States
-
Fondazione G.B. Bietti, IRCCSRecruitingMacular Edema | Inherited Retinal Dystrophy | Laser RetinopathyItaly
-
IRCCS San RaffaeleRecruiting
-
ENCellNot yet recruitingDuchenne Muscular DystrophyKorea, Republic of
-
NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Not yet recruiting
-
Percheron TherapeuticsRecruitingDuchenne Muscular DystrophyTurkey, United Kingdom, Australia, Serbia, Bulgaria
-
Sqy TherapeuticsBiotrialRecruitingDuchenne Muscular DystrophyFrance
-
The Emmes Company, LLCUltragenyx Pharmaceutical Inc; Parent Project Muscular Dystrophy; Department...RecruitingDuchenne Muscular DystrophyUnited States
-
REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
-
PfizerRecruitingDuchenne Muscular DystrophyUnited States
-
Gülsena UtkuRecruiting
-
Anne M. ConnollyAnn & Robert H Lurie Children's Hospital of Chicago; Children's Hospital Medical... and other collaboratorsRecruiting
-
Samsung Medical CenterRecruitingDuchenne Muscular DystrophyKorea, Republic of
-
Sohag UniversityNot yet recruitingDuchenne Muscular DystrophyEgypt
-
Massachusetts General HospitalBoston Children's HospitalRecruitingDuchenne Muscular DystrophyUnited States
-
University of PittsburghRecruitingDuchenne Muscular DystrophyUnited States
-
Ning Wang, MD., PhD.Recruiting
-
CHU de Quebec-Universite LavalRecruitingDuchenne Muscular DystrophyCanada
-
Sarepta Therapeutics, Inc.Hoffmann-La RocheEnrolling by invitationDuchenne Muscular DystrophyUnited States
-
FibroGenTerminatedDuchenne Muscular DystrophyUnited States, Belgium, Israel, Spain, Canada, Australia, Switzerland, United Kingdom, France, China, Netherlands, Italy, Austria, Czechia
-
Daiichi Sankyo Co., Ltd.Orphan Disease Treatment Institute Co., Ltd.Completed
-
Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Belgium, Spain, United Kingdom, Netherlands, Germany, Canada, Italy
-
Lokman Hekim ÜniversitesiCompletedDuchenne Muscular DystrophyTurkey
-
Capricor Inc.Active, not recruiting
-
Sarepta Therapeutics, Inc.CompletedMuscular Dystrophy, DuchenneUnited States
-
Jerry R. MendellDuchenne Alliance; Milo TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
-
Children's National Research InstituteFoundation to Eradicate DuchenneActive, not recruitingDuchenne Muscular DystrophyUnited States
-
Sarepta Therapeutics, Inc.TerminatedAn Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular DystrophyDuchenne Muscular DystrophyUnited States, Belgium, Canada, Spain, United Kingdom, Czechia, Germany, Israel, Bulgaria, France, Italy, Poland, Sweden
-
Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
-
Daiichi Sankyo Co., Ltd.Active, not recruitingDuchenne Muscular DystrophyJapan
-
NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophySpain, United States, Russian Federation, Italy, China, Turkey
-
Santhera PharmaceuticalsNo longer availableDuchenne Muscular DystrophyUnited States