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Clinical Trials on Myotonic Dystrophy, Type 1 (DM1) in New Zealand
Total 542 results
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Avidity Biosciences, Inc.CompletedMyotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy Type 1 (DM1) | Myotonic Dystrophy 1 | Myotonic Muscular Dystrophy | DM1 | Dystrophy Myotonic | Steinert DiseaseUnited States
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Dyne TherapeuticsRecruitingMyotonic Dystrophy Type 1 (DM1)United Kingdom, France, Netherlands, Italy, Germany, New Zealand
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Avidity Biosciences, Inc.Active, not recruitingNervous System Diseases | Genetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Neurodegenerative Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Heredodegenerative Disorders, Nervous System | Myotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy... and other conditionsUnited States
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Virginia Commonwealth UniversityRadboud University Medical Center; University of California, Los Angeles; University... and other collaboratorsRecruitingMyotonic Dystrophy 1United States, Netherlands, United Kingdom, New Zealand, Germany, Italy, Canada, France
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Arrowhead PharmaceuticalsRecruitingMyotonic Dystrophy 1New Zealand, Australia
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMuscular Dystrophy | Myotonic Dystrophy Type 2 | Myotonic Dystrophy Type 1 | Myotonic Dystrophy | Facioscapulohumeral Muscular Dystrophy | Steinert's Disease | Congenital Myotonic Dystrophy | PROMM (Proximal Myotonic Myopathy) | Myotonic Muscular DystrophyUnited States
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PepGen IncRecruitingMyotonic Dystrophy 1United States, Canada
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University of RochesterCompletedMyotonic DystrophyUnited States
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Imsmed IncorporatedCompleted
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); University... and other collaboratorsCompletedMyotonic Dystrophy Type 1United States
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Harmony Biosciences, LLCActive, not recruitingMyotonic Dystrophy 1 | Excessive Daytime SleepinessUnited States, Canada
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Ionis Pharmaceuticals, Inc.CompletedMyotonic Dystrophy Type 1United States
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Insmed IncorporatedMuscular Dystrophy AssociationCompleted
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AMO Pharma LimitedRecruitingCongenital Myotonic DystrophyUnited States, Canada, Australia, New Zealand
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AMO Pharma LimitedCompletedCongenital Myotonic DystrophyUnited States, Canada, New Zealand, Australia, United Kingdom
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Virginia Commonwealth UniversityRecruitingCongenital Myotonic Dystrophy | Childhood Myotonic Dystrophy | CDM | CHDMUnited States, Italy
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Diatranz Otsuka LimitedCompleted
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Christchurch Clinical Studies Trust LtdMedtronicUnknownType1diabetesNew Zealand
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Richard Barohn, MDCompletedNon-Dystrophic Myotonia | MyotoniaUnited States, Canada, Italy, United Kingdom
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Avidity Biosciences, Inc.RecruitingPhase 1/2 Study of AOC 1020 in Adults With Facioscapulohumeral Muscular Dystrophy (FSHD) (FORTITUDE)Muscular Dystrophies | Muscular Dystrophy, Facioscapulohumeral | FSHD | Facio-Scapulo-Humeral Dystrophy | FMD | Facioscapulohumeral Muscular Dystrophy 1 | FSHD2 | FSHD1 | FMD2 | Fascioscapulohumeral Muscular Dystrophy | Fascioscapulohumeral Muscular Dystrophy Type 1 | Fascioscapulohumeral Muscular Dystrophy... and other conditionsUnited States, United Kingdom, Canada
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Melbourne HealthCompletedType 1 DiabetesAustralia, New Zealand
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular Dystrophy (DMD)United States
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Sarepta Therapeutics, Inc.Completed
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Passage Bio, Inc.Active, not recruitingGM1 Gangliosidosis | GM1 Gangliosidosis, Type I | GM1 Gangliosidosis, Type 2 | Beta-Galactosidase-1 (GLB1) DeficiencyUnited States, Canada, United Kingdom, Turkey, Brazil
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Dyne TherapeuticsRecruitingDuchenne Muscular Dystrophy (DMD)United States, Belgium, Canada, United Kingdom, Australia, Spain, Italy
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Santhera PharmaceuticalsTerminatedDuchenne Muscular Dystrophy (DMD)United States, Spain, Netherlands, Sweden, Germany, France, Belgium, United Kingdom, Italy, Ireland, Switzerland, Austria, Bulgaria, Hungary, Israel
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Yale UniversityHarvard UniversityCompletedType1 DiabetesUnited States
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University of SydneyNational Health and Medical Research Council, Australia; Mylan Pharmaceuticals... and other collaboratorsRecruitingDiabetic Retinopathy | Diabetic Nephropathies | Type 1 Diabetes MellitusAustralia, Hong Kong, New Zealand
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Eddii, Inc.Completed
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NYU Langone HealthNational Heart, Lung, and Blood Institute (NHLBI)Recruiting
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Yale UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)TerminatedType1 Diabetes MellitusUnited States
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Yale UniversityCompletedType 1 Diabetes MellitusUnited States
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Yale UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Completed
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University at BuffaloCompletedType 1 Diabetes MellitusUnited States
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State University of New York at BuffaloJuvenile Diabetes Research Foundation; University of GlasgowRecruiting
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Hackensack Meridian HealthVerizon FoundationSuspendedType 1 Diabetes MellitusUnited States
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Dartmouth-Hitchcock Medical CenterDartmouth CollegeCompletedType 1 Diabetes MellitusUnited States
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National Institute of Allergy and Infectious Diseases...PPD; Rho Federal Systems Division, Inc.; Immune Tolerance Network (ITN)CompletedType 1 Diabetes Mellitus | T1DM | T1D | New-onset Type 1 Diabetes MellitusUnited States, Australia
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HealthCore-NERIYale UniversityCompletedType1diabetes | Type1 Diabetes MellitusUnited States
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Jeffrey BluestoneYale UniversityCompleted
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University of California, San FranciscoNational Institute of Allergy and Infectious Diseases (NIAID); Juvenile Diabetes...CompletedType 1 Diabetes MellitusUnited States
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University of VirginiaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Novo... and other collaboratorsCompletedType1 Diabetes MellitusUnited States
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Medtronic DiabetesRecruitingType 1 DiabetesUnited States, Spain, New Zealand, Canada, France, Germany, Italy, Sweden, United Kingdom
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Insulet CorporationCompleted
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University of RochesterNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)TerminatedType 1 Diabetes Mellitus | HypercalciuriaUnited States
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National Institute of Diabetes and Digestive and...CompletedType 1 Diabetes | Preservation of Insulin Secretion | Newly Diagnosed Type 1 Diabetes | Canakinumab in Type 1 DiabetesUnited States, Canada
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Insulet CorporationCompletedType 1 Diabetes MellitusUnited States
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Yale UniversityJuvenile Diabetes Research FoundationCompletedHypo-unawareness | Type 1 Diabetes MellitusUnited States
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Yale UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Juvenile...Completed
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Dicerna Pharmaceuticals, Inc.CompletedKidney Diseases | Urologic Diseases | Genetic Disease | Primary Hyperoxaluria Type 1 (PH1) | Primary Hyperoxaluria Type 2 (PH2)Poland, United Kingdom, New Zealand, United States, Australia, Canada, France, Germany, Israel, Italy, Japan, Lebanon, Netherlands, Romania, Spain