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- US Clinical Trials Registry
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Clinical Trials on Myotonic Dystrophy in United Kingdom
Total 797 results
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Cornea Research Foundation of AmericaPrice Vision Group; North Carolina Lion's Eye BankCompletedCorneal Edema | Fuchs Endothelial DystrophyUnited States
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Capricor Inc.CompletedDuchenne Muscular DystrophyUnited States
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Trefoil Therapeutics, Inc.CompletedFuchs' Endothelial Dystrophy | Fuchs Dystrophy | FuchsUnited States
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Edgewise Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Jett Foundation, Inc.Pfizer; Hoffmann-La Roche; Italfarmaco; Nationwide Children's Hospital; Capricor... and other collaboratorsCompletedDuchenne Muscular Dystrophy | Rare Diseases | Disability Physical | Burden, Dependency | Impairment | Disease ManagementUnited States
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Mallinckrodt ARD LLCTerminatedMuscular Dystrophy, DuchenneSpain, Bulgaria, Italy, United States, Mexico, Israel, Serbia, Turkey
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MeiraGTx UK II LtdJanssen, LPActive, not recruitingRetinitis PigmentosaUnited States, United Kingdom, Canada
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National Institute of Neurological Disorders and...Completed
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Spark TherapeuticsActive, not recruitingConfirmed Biallelic RPE65 Mutation-associated Retinal DystrophyUnited States
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Sarepta Therapeutics, Inc.RecruitingLimb-girdle Muscular DystrophyUnited States, Brazil, Belgium, Canada, Germany, Italy, Spain, Sweden, Turkey, United Kingdom
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Keratoplasty Alliance InternationalRecruitingCorneal Disease | Corneal Transplant Failure | Endothelial Corneal Dystrophy | Corneal Transplant RejectionUnited States
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Subha RamanBallou SkiesCompletedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsTerminatedLimb-Girdle Muscular DystrophyUnited States, Norway, Canada, Sweden, Russian Federation, Denmark, France, Germany
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PTC TherapeuticsParexel; Dohmen Life Science ServicesApproved for marketingDuchenne Muscular DystrophyUnited States
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Santhera PharmaceuticalsCompleted
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Capricor Inc.CompletedDuchenne Muscular Dystrophy | CardiomyopathyUnited States
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Capricor Inc.RecruitingNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States
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Adam Fedyk, MD, FACSAlcon ResearchRecruitingCataract | Fuchs DystrophyUnited States
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SparingVisionRecruiting
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National Institute of Allergy and Infectious Diseases...RecruitingAlopecia Areata | Autoimmune Polyendocrinopathy Candidiasis Ectodermal Dystrophy (Apeced)United States
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University of PittsburghRespirtech, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Stealth BioTherapeutics Inc.CompletedFuchs' Corneal Endothelial Dystrophy (FCED)United States
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The Cleveland ClinicNational Eye Institute (NEI)CompletedRetinal Detachment | Epiretinal Membrane | Fuchs Endothelial Dystrophy | Macular HoleUnited States
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyUnited States, Netherlands, Belgium, Germany, Argentina, Brazil, France, Italy, Sweden, Turkey
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Food and Drug Administration (FDA)National Eye Institute (NEI)RecruitingAge-Related Macular Degeneration | Retinal Degeneration | Retinitis Pigmentosa | Usher Syndromes | Cone Dystrophy | Rod Dystrophy | Cone Rod Dystrophy | Hydroxychloroquine Retinopathy | Late-Onset Retinal Degeneration | Rod Cone DystrophyUnited States
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Santhera PharmaceuticalsCompletedMuscular Dystrophy, Duchenne | Ambulatory CareUnited States, Spain, Austria, Belgium, France, Germany, Italy, Netherlands, Sweden, Switzerland
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Cooperative International Neuromuscular Research...United States Department of Defense; National Institutes of Health (NIH); U.S... and other collaboratorsUnknownDuchenne Muscular DystrophyUnited States, Canada, Australia, India, Israel, Argentina, Italy, Sweden
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GlaxoSmithKlineCompletedMuscular DystrophiesFrance, United States
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Nationwide Children's HospitalRecruiting
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Asklepios Biopharmaceutical, Inc.RecruitingMuscular Dystrophy | Limb Girdle Muscular Dystrophy | LGMD2I | LGMD | Limb-Girdle Muscular Dystrophy Type 2 | LGMD2 | FKRP | FKRP Mutation | Fukutin Related ProteinUnited States
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Sarepta Therapeutics, Inc.Active, not recruitingLimb-Girdle Muscular Dystrophy, Type 2EUnited States
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Jazz PharmaceuticalsCompletedEpilepsy | Dravet SyndromeUnited States, United Kingdom
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Stanford UniversityNational Heart, Lung, and Blood Institute (NHLBI); University of California... and other collaboratorsCompletedMuscular Dystrophy, DuchenneUnited States
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Cambridge University Hospitals NHS Foundation TrustUnknownStroke | Osteoarthritis | Back Pain | Sciatica | Fibromyalgia | Complex Regional Pain Syndromes | Traumatic Brain InjuryUnited Kingdom
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Sarepta Therapeutics, Inc.Active, not recruiting
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Wake Forest University Health SciencesTerminatedFuchs Dystrophy | Cystoid Macular EdemaUnited States
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States
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PTC TherapeuticsCooperative International Neuromuscular Research Group; The John Walton Muscular...Active, not recruitingMuscular Dystrophy, DuchenneGermany, France, United Kingdom, Brazil, Italy, Austria, Sweden, Czechia, Greece, Hungary, Israel, Latvia, Norway, Portugal, Romania, Slovenia
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Price Vision GroupKala Pharmaceuticals, Inc.CompletedCorneal Edema | Corneal Endothelial DystrophyUnited States
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Tufts UniversityBoston Older Americans Independence Center; Somerville Council on Aging, MassachusettsCompleted
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Stichting Epilepsie Instellingen NederlandEpilepsiefondsCompleted
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The Cleveland ClinicNational Eye Institute (NEI)RecruitingRetinal Diseases | Retinal Detachment | Epiretinal Membrane | Fuchs Endothelial Dystrophy | Macular HoleUnited States
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Kevin FlaniganMuscular Dystrophy AssociationTerminated
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); Cure CMDCompletedCongenital Muscular DystrophyUnited States
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PTC TherapeuticsEnrolling by invitationDuchenne Muscular DystrophyUnited States, Canada
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Autifony Therapeutics LimitedCompletedMyoclonus Epilepsies, ProgressiveUnited States
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Bionano GenomicsColumbia University; University of Iowa; Medical College of Wisconsin; Augusta... and other collaboratorsRecruitingIntellectual Disability | Autism Spectrum Disorder | Fragile X Syndrome | Developmental Disability | Congenital Anomaly | Facioscapulohumeral Muscular Dystrophy 1United States
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University of Texas Southwestern Medical CenterRecruitingDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Dilated Cardiomyopathy | Cardiomyopathy, Hypertrophic | Heart Failure With Reduced Ejection Fraction | Cardiac Sarcoidosis | Heart Failure With Preserved Ejection FractionUnited States
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Oregon Health and Science UniversityNational Eye Institute (NEI)RecruitingCorneal Opacities (Scar and Stromal Dystrophy)United States