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- US Clinical Trials Registry
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Clinical Trials on Myotonic Dystrophy in United States
Total 812 results
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States, Belgium, Israel, Spain, Canada, Australia, Switzerland, United Kingdom, France, China, Netherlands, Italy, Austria, Czechia
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VA Office of Research and DevelopmentNot yet recruitingMotoric Cognitive Risk SyndromeUnited States
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Ascidian Therapeutics, IncRecruitingStargardt Disease | Stargardt Disease 1 | Juvenile Macular Degeneration | Cone Rod DystrophyUnited States
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Ascidian Therapeutics, IncRecruitingStargardt Disease | Stargardt Disease 1 | Juvenile Macular Degeneration | Cone Rod DystrophyUnited States
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University College, LondonUniversity of North Carolina, Chapel Hill; NYU Grossman School of MedicineRecruitingDentatorubral-Pallidoluysian AtrophyUnited States, United Kingdom
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University of SouthamptonUnknownKeratoconus | Fuchs Dystrophy | Corneal DiseaseUnited Kingdom
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Sarepta Therapeutics, Inc.TerminatedAn Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular DystrophyDuchenne Muscular DystrophyUnited States, Belgium, Canada, Spain, United Kingdom, Czechia, Germany, Israel, Bulgaria, France, Italy, Poland, Sweden
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PfizerActive, not recruitingDuchenne Muscular DystrophyUnited States, Spain, Belgium, Korea, Republic of, Taiwan, Canada, Australia, Germany, Japan, France, Italy, United Kingdom, Russian Federation, Israel, Switzerland
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Sarepta Therapeutics, Inc.Hoffmann-La RocheActive, not recruitingDuchenne Muscular DystrophyUnited States, Japan, Taiwan, Belgium, Spain, Germany, Hong Kong, Italy, United Kingdom
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National Eye Institute (NEI)TerminatedInherited Retinal Degeneration | Inherited Ophthalmic DiseasesUnited States
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Hoffmann-La RocheCompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, Australia, Japan, France, Netherlands, Spain, Argentina, Germany, Italy, United Kingdom, Sweden
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PTC TherapeuticsParexel; Dohmen Life Science ServicesApproved for marketingDuchenne Muscular DystrophyUnited States
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Santhera PharmaceuticalsCompletedMuscular Dystrophy, Duchenne | Ambulatory CareUnited States, Spain, Austria, Belgium, France, Germany, Italy, Netherlands, Sweden, Switzerland
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Cooperative International Neuromuscular Research...United States Department of Defense; National Institutes of Health (NIH); U.S... and other collaboratorsUnknownDuchenne Muscular DystrophyUnited States, Canada, Australia, India, Israel, Argentina, Italy, Sweden
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Columbia UniversityMuscular Dystrophy Association; Stevens Institute of TechnologyCompletedDuchenne Muscular Dystrophy | Spinal Muscular Atrophy Type 3United States
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Eli Lilly and CompanyTerminatedMuscular Dystrophy, DuchenneGermany, United States, Spain, Belgium, France, Italy, Taiwan, Netherlands, Turkey, Korea, Republic of, Argentina, Canada, Japan, Puerto Rico, Russian Federation, United Kingdom
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Astellas Institute for Regenerative MedicineCompleted
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University Hospital, Basel, SwitzerlandCompletedDuchenne Muscular DystrophyFrance, Spain, Germany, Netherlands, Switzerland, United Kingdom
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ML Bio Solutions, Inc.Active, not recruiting
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States, Spain, Canada, Australia, China, Italy, Belgium, France, Netherlands, Austria, United Kingdom
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Astellas Institute for Regenerative MedicineCompleted
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Benha UniversityUnknownDystrophy, RetinalUnited Arab Emirates
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ItalfarmacoFortreaRecruitingDuchenne Muscular DystrophyBelgium, Netherlands, Canada, Italy, France, Germany, United Kingdom
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GlaxoSmithKlineCompletedMuscular DystrophiesGermany, Belgium, Turkey, Netherlands, Spain, Israel, Australia, France, United Kingdom
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Bionano GenomicsColumbia University; University of Iowa; Medical College of Wisconsin; Augusta... and other collaboratorsRecruitingIntellectual Disability | Autism Spectrum Disorder | Fragile X Syndrome | Developmental Disability | Congenital Anomaly | Facioscapulohumeral Muscular Dystrophy 1United States
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National Institute of Neurological Disorders and...Completed
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Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Korea, Republic of, Italy, United Kingdom, Canada, Poland, Spain, France, Germany, Belgium, Australia, Czechia, Serbia, Greece, Argentina, Bulgaria, Denmark, Hungary, India, Ireland, Israel, Mexico, Russian Federation, ...
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National Institute of Nursing Research (NINR)CompletedCerebral Palsy | Neuromuscular DiseaseUnited States
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MD Stem CellsUnknownGlaucoma | Macular Degeneration | Retinal Disease | Hereditary Retinal Dystrophy | Optic Nerve DiseaseUnited States
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Spark Therapeutics, Inc.Children's Hospital of Philadelphia; University of IowaActive, not recruitingLeber Congenital Amaurosis | Inherited Retinal Dystrophy Due to RPE65 MutationsUnited States
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Active, not recruitingDuchenne Muscular DystrophyKorea, Republic of, Chile, Japan, China, United Kingdom, Netherlands, Spain, Norway, Russian Federation, Australia, Greece, Italy, New Zealand, Turkey, Mexico, Czechia, Canada
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Newcastle-upon-Tyne Hospitals NHS TrustCompletedDuchenne Muscular DystrophyUnited Kingdom
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Astellas Pharma Global Development, Inc.Active, not recruitingStargardt's Macular DystrophyItaly, United States, Israel, United Kingdom, Germany, Spain, Hungary, France
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Massachusetts Eye and Ear InfirmaryCompletedFuchs' Endothelial DystrophyUnited States
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Oregon Health and Science UniversityTerminated
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Hoffmann-La RocheTerminatedMuscular Dystrophy (DMD)United States, Canada
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National Institute of Neurological Disorders and...Completed
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Johns Hopkins UniversityRecruitingGranular Dystrophy, CornealUnited States
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Virginia Commonwealth UniversityWashington University School of Medicine; University of Iowa; University of Minnesota and other collaboratorsActive, not recruitingMuscular Dystrophies | Limb Girdle Muscular DystrophyUnited States, United Kingdom
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Vanderbilt University Medical CenterApproved for marketing
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National Institute of Neurological Disorders and...Completed
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Price Vision GroupTerminatedFuchs' Endothelial DystrophyUnited States
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PTC TherapeuticsEnrolling by invitationDuchenne Muscular DystrophyUnited States, Canada
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GlaxoSmithKlineTerminatedMuscular DystrophiesFrance, Bulgaria, Denmark, Germany, Belgium, Canada, Spain, Turkey, United Kingdom, Korea, Republic of, Brazil, Netherlands, Italy, Japan, Czech Republic, Chile, Israel, Hungary, Russian Federation, Australia, Poland, Norway, Argentina and more
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Cornea Research Foundation of AmericaCompletedFuchs' Endothelial Dystrophy | Bullous KeratopathyUnited States
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University of FloridaNational Institute of Neurological Disorders and Stroke (NINDS)Recruiting
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Manhattan Eye, Ear & Throat HospitalGenentech, Inc.CompletedPolypoidal Choroidal Vasculopathy | Pseudoxanthoma Elasticum | Pathological Myopia | Retinal Angiomatous Proliferation | Coats' Disease | Idiopathic Retinal Telangiectasia | Multi-focal Choroiditis | Rubeosis Iridis | Von Hippel Lindau Disease | BEST VITELLIFORM MACULAR DYSTROPHY, MULTIFOCAL (Disorder)United States
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University of FloridaNational Institute of Neurological Disorders and Stroke (NINDS)CompletedDystonia | TremorUnited States