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Clinical Trials on Myotonic Muscular Dystrophy
Total 50976 results
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, United Kingdom
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, Belgium, Australia, Canada, France, Germany, Israel, Italy, Spain, Sweden, United Kingdom
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University Hospital, AngersFederico II University; University of Modena and Reggio EmiliaNot yet recruitingFacioscapulohumeral Muscular Dystrophy
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Centre Hospitalier Universitaire de NiceCompletedMuscular DystrophiesFrance
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University of RochesterCompletedFacioscapulohumeral Muscular DystrophyUnited States
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University of Kansas Medical CenterNational Institutes of Health (NIH)CompletedFacioscapulohumeral Muscular DystrophyUnited States
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Istanbul University - Cerrahpasa (IUC)CompletedFacioscapulohumeral Muscular DystrophyTurkey
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Hugo W. Moser Research Institute at Kennedy Krieger...Active, not recruitingFacioscapulohumeral Muscular DystrophyUnited States
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular DystrophyUnited States, Italy, Netherlands
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedFacioscapulohumeral Muscular DystrophyUnited States, Spain, Canada
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University of New MexicoUniversity of FloridaWithdrawnOculopharyngeal Muscular Dystrophy
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Bioblast Pharma Ltd.CompletedOculopharyngeal Muscular DystrophyUnited States, Israel, Canada
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Nationwide Children's HospitalBoston Children's Hospital; University of California, Davis; University of Minnesota and other collaboratorsCompletedCardiomyopathy | Duchenne Muscular Dystrophy (DMD)United States
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Centre Hospitalier Universitaire de NiceCompletedFacio-Scapulo-Humeral DystrophyFrance
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Institut de Myologie, FranceAssociation Française contre les Myopathies (AFM), ParisNot yet recruitingMerosin Deficient Congenital Muscular DystrophyFrance
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Prothelia, Inc.Cure CMD; The Bönnemann Laboratory, NINDS, National Institutes of Health; Oscar... and other collaboratorsCompletedMerosin Deficient Congenital Muscular DystrophyUnited States
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IRCCS San RaffaeleRecruiting
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ENCellNot yet recruitingDuchenne Muscular DystrophyKorea, Republic of
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Not yet recruiting
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Percheron TherapeuticsRecruitingDuchenne Muscular DystrophyTurkey, United Kingdom, Australia, Serbia, Bulgaria
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Sqy TherapeuticsBiotrialRecruitingDuchenne Muscular DystrophyFrance
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The Emmes Company, LLCUltragenyx Pharmaceutical Inc; Parent Project Muscular Dystrophy; Department...RecruitingDuchenne Muscular DystrophyUnited States
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REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
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PfizerRecruitingDuchenne Muscular DystrophyUnited States
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Gülsena UtkuRecruiting
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Anne M. ConnollyAnn & Robert H Lurie Children's Hospital of Chicago; Children's Hospital Medical... and other collaboratorsRecruiting
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Samsung Medical CenterRecruitingDuchenne Muscular DystrophyKorea, Republic of
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Sohag UniversityNot yet recruitingDuchenne Muscular DystrophyEgypt
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Massachusetts General HospitalBoston Children's HospitalRecruitingDuchenne Muscular DystrophyUnited States
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University of PittsburghRecruitingDuchenne Muscular DystrophyUnited States
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Ning Wang, MD., PhD.Recruiting
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CHU de Quebec-Universite LavalRecruitingDuchenne Muscular DystrophyCanada
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.Hoffmann-La RocheEnrolling by invitationDuchenne Muscular DystrophyUnited States
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States, Belgium, Israel, Spain, Canada, Australia, Switzerland, United Kingdom, France, China, Netherlands, Italy, Austria, Czechia
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Daiichi Sankyo Co., Ltd.Orphan Disease Treatment Institute Co., Ltd.Completed
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Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Belgium, Spain, United Kingdom, Netherlands, Germany, Canada, Italy
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Lokman Hekim ÜniversitesiCompletedDuchenne Muscular DystrophyTurkey
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Capricor Inc.Active, not recruiting
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Sarepta Therapeutics, Inc.CompletedMuscular Dystrophy, DuchenneUnited States
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Jerry R. MendellDuchenne Alliance; Milo TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Children's National Research InstituteFoundation to Eradicate DuchenneActive, not recruitingDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.TerminatedAn Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular DystrophyDuchenne Muscular DystrophyUnited States, Belgium, Canada, Spain, United Kingdom, Czechia, Germany, Israel, Bulgaria, France, Italy, Poland, Sweden
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Daiichi Sankyo Co., Ltd.Active, not recruitingDuchenne Muscular DystrophyJapan
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophySpain, United States, Russian Federation, Italy, China, Turkey
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Santhera PharmaceuticalsNo longer availableDuchenne Muscular DystrophyUnited States
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PfizerCompletedDuchenne Muscular DystrophyChina
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ENCellCompletedDuchenne Muscular DystrophyKorea, Republic of
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NS Pharma, Inc.Cooperative International Neuromuscular Research Group; Nippon Shinyaku Co.... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada
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Hacettepe UniversityActive, not recruitingDuchenne Muscular DystrophyTurkey