- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Neuroaxonal Dystrophy, Atypical
Total 1639 results
-
ItalfarmacoCompletedBecker Muscular DystrophyNetherlands, Italy
-
Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyBelgium, France, Italy, United Kingdom
-
Craig McDonald, MDCardero Therapeutics, Inc.Completed
-
University of North Carolina, Chapel HillNational Institute of Neurological Disorders and Stroke (NINDS)CompletedMuscular Dystrophy, DuchenneUnited States
-
Wave Life Sciences Ltd.TerminatedDuchenne Muscular DystrophyUnited States, Belgium, United Kingdom, Czechia, Canada, France, Italy, Sweden
-
Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
-
University of Sao PauloCompletedDuchenne Muscular Dystrophy
-
University of Sao PauloCompletedDuchenne Muscular DystrophyBrazil
-
PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
-
University of FloridaEngage Health Inc.CompletedDuchenne Muscular DystrophyUnited States
-
Taiho Pharmaceutical Co., Ltd.Completed
-
Hacettepe UniversityUnknownDuchenne Muscular DystrophyTurkey
-
Summit TherapeuticsTerminatedDuchenne Muscular DystrophyUnited States, United Kingdom
-
Ohio State UniversityUniversity of Colorado, Denver; University of California, Los Angeles; Vanderbilt... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States
-
University Medical Center NijmegenLeiden University Medical Center; Princess Beatrix Muscle FoundationCompletedPediatric Disorder | Facioscapulohumeral Muscular Dystrophy | Neurological ObservationsNetherlands
-
EspeRare FoundationCompletedMuscular Dystrophy, DuchenneItaly, France, Spain, United Kingdom
-
University of FloridaCureDuchenneCompletedMuscular Dystrophy, DuchenneUnited States
-
Akashi TherapeuticsTerminatedDuchenne Muscular DystrophyUnited States
-
GlaxoSmithKlineCompletedMuscular DystrophiesFrance, Denmark, Germany, Belgium, Spain, Turkey, Korea, Republic of, Brazil, Netherlands, Italy, Chile, Japan, Canada, Hungary, Russian Federation, Czechia, Poland, Norway, Argentina, Taiwan
-
Cedars-Sinai Medical CenterCompleted
-
University of MinnesotaFairview Health ServicesWithdrawnDuchenne Muscular Dystrophy
-
PTC TherapeuticsParexel; Dohmen Life Science ServicesApproved for marketingDuchenne Muscular DystrophyUnited States
-
University of FloridaUnited States Department of DefenseCompletedDuchenne Muscular DystrophyUnited States
-
PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
-
BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyBelgium, Netherlands, Italy, Sweden
-
Jerry R. MendellEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedDuchenne Muscular DystrophyUnited States
-
Boston Children's HospitalBeth Israel Deaconess Medical CenterCompletedDuchenne Muscular DystrophyUnited States
-
University of GaziantepIstınye University, Cukurova University, Yıldırım Beyazıt University, Gaziantep...UnknownDuchenne Muscular DystrophyTurkey
-
GlaxoSmithKlineWithdrawnMuscular Dystrophies
-
Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedDuchenne Muscular DystrophyCanada
-
Shenzhen Beike Bio-Technology Co., Ltd.The Second Affiliated Hospital of Kunming Medical UniversityUnknownDuchenne Muscular DystrophyChina
-
Nationwide Children's HospitalNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes...CompletedDuchenne Muscular DystrophyUnited States
-
Cooperative International Neuromuscular Research...Completed
-
Cooperative International Neuromuscular Research...Completed
-
Mayo ClinicRecruitingBreast Carcinoma | Breast Atypical Ductal Hyperplasia | Breast Atypical Lobular Hyperplasia | Breast Lobular Carcinoma In SituUnited States
-
Sarepta Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
-
Red Nucleus Enterprise Solutions, LLCRecruiting
-
Egyptian Chinese UniversityBenha UniversityRecruitingDuchenne Muscular DystrophyEgypt
-
ItalfarmacoRecruitingDuchenne Muscular DystrophyCanada, Italy, France, Belgium, Germany, Netherlands, United Kingdom
-
Sarepta Therapeutics, Inc.Hoffmann-La RocheRecruitingDuchenne Muscular DystrophyBelgium, United States, Japan, Spain, Italy, United Kingdom
-
Virginia Commonwealth UniversityNorthwestern University; University of RochesterRecruitingDuchenne Muscular DystrophyUnited States
-
University of FloridaRecruiting
-
Edgewise Therapeutics, Inc.Medpace, Inc.Enrolling by invitationBecker Muscular DystrophyUnited States, Netherlands, United Kingdom
-
Santhera PharmaceuticalsSanthera PharmaceuticalsActive, not recruitingDuchenne Muscular DystrophyCanada
-
Sarepta Therapeutics, Inc.Active, not recruitingMuscular Dystrophy, DuchenneUnited States, Korea, Republic of, India, Slovenia, Turkey, United Kingdom, Germany, Switzerland, Spain, Czechia, France, Serbia, Taiwan, Netherlands, Mexico, Colombia, Denmark, New Zealand, Norway, Greece, Hungary, Ireland, Italy, Jo... and more
-
PfizerActive, not recruitingDuchenne Muscular DystrophyUnited States, Spain, Belgium, Korea, Republic of, Taiwan, Canada, Australia, Germany, Japan, France, Italy, United Kingdom, Russian Federation, Israel, Switzerland
-
Sheffield Children's NHS Foundation TrustSheffield Hallam University; National Institute for Health Research, United... and other collaboratorsActive, not recruiting
-
NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Active, not recruitingDuchenne Muscular DystrophyKorea, Republic of, Chile, Japan, China, United Kingdom, Netherlands, Spain, Norway, Russian Federation, Australia, Greece, Italy, New Zealand, Turkey, Mexico, Czechia, Canada
-
University College, LondonRadboud University Medical Center; Groupe Hospitalier Pitie-Salpetriere; Leiden... and other collaboratorsCompletedDuchenne Muscular DystrophyNetherlands, France, United Kingdom
-
Santhera PharmaceuticalsAvailableDuchenne Muscular DystrophyUnited States, Canada, Israel