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Clinical Trials on Neurodegenerative Disease, Hereditary
Total 377834 results
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State University of New York at BuffaloActive, not recruitingFuchs DystrophyUnited States
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University of PennsylvaniaCompletedHereditary Hemorrhagic Telangiectasia (HHT)United States
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Centre Hospitalier Universitaire de Saint EtienneKyoto University, Graduate School of MedicineNot yet recruitingCorneal DystrophiesFrance
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Children's Hospital of Fudan UniversityRecruitingGenetic Predisposition to Disease | Newborn | Defect, Congenital | Hereditary DiseaseChina
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KalVista Pharmaceuticals, Ltd.TerminatedAngioedema, Hereditary, Types I and IIUnited States, Czechia, Germany, Hungary, Italy, North Macedonia, United Kingdom, Australia, Bulgaria, Canada, France, New Zealand, Puerto Rico
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Price Vision GroupNot yet recruitingCorneal Edema | Fuchs' Endothelial DystrophyUnited States
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Massachusetts Eye and Ear InfirmaryRecruitingFuchs Endothelial Corneal DystrophyUnited States
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Kowa Research Institute, Inc.RecruitingFuchs Endothelial Corneal DystrophyUnited States, United Kingdom, Spain, Germany, Canada, Denmark
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Hospices Civils de LyonCompletedLiver Transplant | Hereditary Haemorrhagic Telangiectasia
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Maastricht University Medical CenterRadboud University Medical CenterUnknown
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Universitat de LleidaHospital Clinic of Barcelona; Universitat Internacional de CatalunyaNot yet recruitingCerebellar Ataxia | Spinocerebellar Degenerations | Hereditary Ataxia
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingHereditary Transthyretin AmyloidosisItaly
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis | Amyloidosis, HereditaryUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Cyprus, France, Germany, Greece, Italy, Japan, Korea, Republic of, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Taiwan, United Kingdom
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Hasan Kalyoncu UniversityCompleted
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Peking University Third HospitalRecruitingBietti's Crystalline DystrophyChina
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Price Vision GroupCompletedFuchs Endothelial DystrophyUnited States
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Cornea Research Foundation of AmericaPrice Vision Group; North Carolina Lion's Eye BankCompletedCorneal Edema | Fuchs Endothelial DystrophyUnited States
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Fundacion para la Investigacion Biomedica del Hospital...CompletedCataract | Fuchs' Endothelial DystrophySpain
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Tissue Tech Inc.CompletedCorneal Dystrophy, Epithelial Basement MembraneUnited States
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Motric BioRecruitingStroke | Multiple Sclerosis | Cerebral Palsy | Spinal Cord Injuries | Dystonia | Muscle Spasticity | Hereditary Spastic Paraplegia | Hypertonia, MuscleUnited States
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Hospices Civils de LyonCompleted
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Washington University School of MedicineEnrolling by invitation
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Queen's UniversityWithdrawnCataracts | Fuch's Endothelial DystrophyCanada
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Howard UniversityCompleted
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Universitat Internacional de CatalunyaUniversitat de LleidaCompletedCerebellar Ataxia | Spinocerebellar Degenerations | Hereditary AtaxiaSpain
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Children's Hospital of PhiladelphiaUniversity of Wisconsin, Madison; Ionis Pharmaceuticals, Inc.; Pennsylvania Department...Recruiting
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Ionis Pharmaceuticals, Inc.RecruitingAlexander DiseaseUnited States, United Kingdom, Australia, Canada, Israel, Italy, Japan, Netherlands
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Myrtelle Inc.RecruitingCanavan DiseaseUnited States
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University of FloridaUniversity of Miami; University of Massachusetts, WorcesterNo longer available
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Ospedale Santo StefanoIstituto di Fisica ApplicataCompletedCorneal Opacity | Keratoconus | Corneal DystrophiesItaly
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University Hospital, Strasbourg, FranceTerminated
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Cairo UniversityRecruitingEntrapment NeuropathiesEgypt
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NYU Langone HealthNational Eye Institute (NEI)Active, not recruitingFuch's Dystrophy | Corneal Disorders | Prior SurgeryUnited States
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NYU Langone HealthUniversitätsklinikum Hamburg-EppendorfCompleted
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Shaare Zedek Medical CenterUnknown
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Nanoscope Therapeutics Inc.CompletedEye Diseases | Retinal Degeneration | Retinal Diseases | Retinitis Pigmentosa | Retinitis | Eye Diseases, Hereditary | Retinal DystrophiesUnited States, Puerto Rico
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Medical College of WisconsinCompletedCataract | Fuchs' Corneal DystrophyUnited States
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Medical University of ViennaUnknownRetina Disorder | Macula; Degeneration, Congenital or Hereditary
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AstraZenecaRecruiting
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Chiesi Canada CorpNo longer availablePantothenate Kinase-Associated Neurodegeneration
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Travere Therapeutics, Inc.TerminatedPantothenate Kinase-Associated NeurodegenerationUnited States, Canada, Czechia, France, Germany, Italy, Norway, Poland, Spain
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ApoPharmaCompletedPantothenate Kinase-Associated NeurodegenerationUnited States, Germany, Italy, United Kingdom
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Intellia TherapeuticsNot yet recruitingHereditary AngioedemaFrance, New Zealand, United Kingdom
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Ionis Pharmaceuticals, Inc.RecruitingHereditary AngioedemaUnited States, Puerto Rico, Belgium, Bulgaria, Canada, France, Germany, Israel, Italy, Netherlands, Poland, Spain, Turkey, United Kingdom
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BioMarin PharmaceuticalRecruitingHereditary Angioedema | HAEUnited States, Spain, Australia
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Pharming Technologies B.V.CompletedHereditary AngioedemaIsrael, Italy, United States, Czechia, Germany, Hungary, Poland, Romania, Slovakia, North Macedonia
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Astria Therapeutics, Inc.Completed
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Ionis Pharmaceuticals, Inc.CompletedHereditary AngioedemaUnited States, France, Netherlands, Spain, United Kingdom, Belgium, Bulgaria, Canada, Denmark, Germany, Israel, Italy, Poland, Turkey
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CSL BehringCompletedHereditary AngioedemaUnited States, Germany, Japan, Hungary, Canada, Netherlands, Israel
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TakedaCompletedHereditary AngioedemaBelgium, Bulgaria, Estonia, Spain, Hungary, Israel, Germany, Czechia, Portugal, Greece, Lithuania, Poland, Latvia, Croatia, Slovakia, Austria, Canada, Ireland, North Macedonia, Romania, Serbia, Slovenia