- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Neuromuscular Diseases in Children in Italy
Total 737 results
-
Istituto Ortopedico RizzoliCompletedEntrapment Neuropathy, Carpal Tunnel | Compression Neuropathy, Carpal Tunnel | Median Neuropathy, Carpal TunnelItaly
-
National Cancer Institute (NCI)CompletedStage I Breast Cancer AJCC v7 | Stage IA Breast Cancer AJCC v7 | Stage IB Breast Cancer AJCC v7 | Stage II Breast Cancer AJCC v6 and v7 | Stage IIA Breast Cancer AJCC v6 and v7 | Stage IIB Breast Cancer AJCC v6 and v7 | Stage 0 Breast Cancer AJCC v6 and v7United States, Italy
-
argenxRecruitingCongenital Myasthenic SyndromeSpain, Italy, France, United Kingdom, United States, Canada
-
Mario Negri Institute for Pharmacological ResearchCompletedNeuropathic Pain | Tumor | Cancer Pain | Breakthrough Cancer PainItaly
-
Novartis PharmaceuticalsCompletedSpinal and Bulbar Muscular AtrophyUnited States, Germany, Italy, Denmark
-
University of GenovaUnknownCharcot-Marie-Tooth Disease | Charcot-Marie-Tooth Disease Type 1AItaly
-
argenxQuintiles, Inc.CompletedMyasthenia GravisItaly, United States, Belgium, Canada, Netherlands, Poland, Spain, Sweden
-
BioMarin PharmaceuticalCompletedDuchenne Muscular DystrophyBelgium, Netherlands, Italy, Sweden
-
Novartis PharmaceuticalsTerminatedIn Escalation: All Patients With Solid Tumors and Lymphoma | In Expansion: Melanoma, Non-small Cell Lung CancerUnited States, Italy, Taiwan, Belgium, Spain, Germany, Japan
-
PfizerCompletedTransthyretin-associated Amyloidosis With PolyneuropathyUnited States, France, Germany, Italy
-
Neuromed IRCCSIRCCS MultimedicaRecruitingMultiple Sclerosis | Parkinson Disease | Amyotrophic Lateral Sclerosis | Alzheimer DiseaseItaly
-
University of MilanCompletedMuscular Diseases | COVID-19 Acute Respiratory Distress SyndromeItaly
-
University of MessinaUniversità degli Studi di Ferrara; University of Pavia; Careggi Hospital; Fondazione...UnknownPatient-Reported Outcome Measures in Wild-Type and Variant Cardiac Transthyretin Amyloidosis (ITALY)Transthyretin AmyloidosisItaly
-
Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyBelgium, France, Italy, United Kingdom
-
BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyBelgium, Netherlands, Italy, Sweden
-
Ohio State UniversityVarian Medical Systems; Centro Diagnostico Milano, Co-PI: Pantaleo Romanelli...RecruitingSpasticity, Muscle | Spastic Cerebral Palsy | Spasticity as Sequela of StrokeUnited States, Italy
-
Virginia Commonwealth UniversityUniversity of Western Ontario, Canada, Children's Health Research Institute; Fondazione Serena Onlus - Centro Clinico NeMO MilanoRecruitingCongenital Myotonic DystrophyUnited States, Italy, Canada
-
BiogenRecruitingHealthy Volunteer | Muscular Atrophy, SpinalKorea, Republic of, Germany, Belgium, Netherlands, France, Italy, Poland, Canada, United Kingdom, Israel
-
Hiantis SrlSciensano; Genefirst LTDCompletedNeoplasms | Neoplasms by Histologic Type | Carcinoma in Situ | Neoplasm Cervix | Cervical Intraepithelial Neoplasia Grade 2/3 | Carcinoma Cervix UterineItaly, Ireland, United Kingdom
-
Politecnico di MilanoIRCCS Eugenio Medea; Villa Beretta Rehabilitation CenterCompletedMuscular Dystrophies | Muscular Dystrophy, Duchenne | Muscular Dystrophy, Becker | Muscular Dystrophy, Limb-Girdle Type 2Italy
-
IRCCS Eugenio MedeaCompletedCerebral Palsy | Acquired Brain Injury | Hereditary Spastic ParaplegiaItaly
-
BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyNetherlands, Belgium, Italy, Sweden
-
Dr. Rebecca SchuleGerman Federal Ministry of Education and Research; German Center for Neurodegenerative...RecruitingHereditary Spastic ParaplegiaAustria, Germany, Italy
-
Fondazione Policlinico Universitario Agostino Gemelli...RecruitingDescribe Typical Gray Scale/Color Doppler Ultrasound Features of Gestational Trophoblastic Neoplasia at the US Examination | To Assess if There Are Differences at the Baseline US Scan Between Low-risk and High-risk Patients | To Identify Ultrasound Predictors of Resistance to First-line... and other conditionsItaly
-
Azienda Unità Sanitaria Locale di PiacenzaBEACMED s.r.l.RecruitingMuscle Weakness Condition | Pelvic Floor Muscle Weakness | Incontinence Stress | Electricity; EffectsItaly
-
Alexion Pharmaceuticals, Inc.RecruitingGeneralized Myasthenia Gravis | gMGSpain, Italy, United States, France, Switzerland, Serbia, Japan, Netherlands
-
Sarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyBelgium, France, Italy, United Kingdom
-
BiogenActive, not recruitingMuscular Atrophy, SpinalUnited States, Spain, Germany, Italy, Israel
-
Valerion Therapeutics, LLCInstitut de Myologie, France; GenethonCompletedMyotubular MyopathyFrance, Belgium, United States, Canada, Germany, Italy, Spain
-
Hoffmann-La RocheCompletedMuscular Atrophy, SpinalBelgium, United Kingdom, Germany, France, Italy, Netherlands, Poland
-
argenxRecruitingGeneralized Myasthenia GravisUnited Kingdom, Spain, United States, Austria, Germany, Belgium, Italy, Netherlands, France, Georgia, Poland, Canada
-
BioMarin PharmaceuticalRecruitingDuchenne Muscular DystrophySpain, Turkey, United Kingdom, Italy
-
Hoffmann-La RocheTerminatedMuscular Atrophy, SpinalFrance, Turkey, Canada, United States, Italy, Netherlands, Sweden, Switzerland, United Kingdom
-
Weill Medical College of Cornell UniversityMuscular Dystrophy AssociationCompletedFamilial Amyotrophic Lateral SclerosisUnited States, Germany, Italy, Sweden
-
Hoffmann-La RocheActive, not recruitingSpinal Muscular AtrophyBelgium, United States, United Kingdom, France, Poland, Italy, Switzerland, Netherlands, Germany
-
Radiotherapy Oncology Centre "Santa Maria" HospitalPaola Anselmo,MD; Michelina Casale,PhD; Fabio Trippa,MDRecruitingNSCLC | Non Small Cell Lung Cancer | EGF-R Positive Non-Small Cell Lung Cancer | Non Small Cell Lung Cancer Metastatic | NSCLC Stage IV | Oligometastatic Disease | Non-Small Cell Squamous Lung Cancer | Non-Small Cell Lung Cancer With Mutation in Epidermal Growth Factor Receptor | Non-Small Cell Adenocarcinoma and other conditionsItaly
-
SanofiTerminatedMyasthenia GravisItaly, Hungary, United States, Canada, China, Japan, Poland, Spain, United Kingdom
-
EspeRare FoundationCompletedMuscular Dystrophy, DuchenneItaly, France, Spain, United Kingdom
-
Sarepta Therapeutics, Inc.University College, London; Catholic University of the Sacred Heart; University... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited Kingdom, United States, France, Italy
-
BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyBelgium, Netherlands, France, United Kingdom, Italy
-
NMD Pharma A/SRecruitingSpinal Muscular AtrophyUnited States, Spain, Belgium, Denmark, Germany, Netherlands, Italy, Canada
-
IRCCS Azienda Ospedaliero-Universitaria di BolognaNiguarda HospitalRecruitingRespiratory Distress Syndrome in Premature Infant | Patent Ductus Arteriosus After Premature Birth | Perinatal MorbidityItaly
-
UCB Biopharma SRLCompletedGeneralized Myasthenia GravisUnited States, Canada, Georgia, Germany, Italy, Japan, Poland, Serbia, Spain, United Kingdom
-
Mount Sinai Hospital, CanadaCambridge University Hospitals NHS Foundation Trust; University of Cambridge; Jaeb Center for Health Research and other collaboratorsCompletedType 1 Diabetics Who Are Pregnant or Planning PregnancyCanada, United Kingdom, Spain, United States, Ireland, Italy
-
Pierre Fabre MedicamentCompletedFibromyalgia SyndromeSpain, Italy, Portugal, France, Czech Republic, Finland, Germany, Norway, Romania, Sweden
-
Italian Sarcoma GroupFrench Sarcoma Group; Grupo Espanol de Investigacion en SarcomasActive, not recruitingLocalized High-risk Soft Tissue Sarcomas of the Extremities and Trunk Wall in AdultsSpain, Italy
-
Dompé Farmaceutici S.p.ACompletedIslet Transplantation in Diabetes Mellitus Type 1United States, Czechia, Italy, Sweden, United Kingdom
-
BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyUnited Kingdom, Italy, Belgium, Netherlands, France
-
Alnylam PharmaceuticalsRecruitingPolyneuropathy | Hereditary Transthyretin-mediated (hATTR) AmyloidosisNetherlands, Spain, United States, Germany, France, Italy, Portugal
-
Novartis PharmaceuticalsCompletedSpinal Muscular AtrophyTaiwan, Belgium, Canada, United States, Australia, France, Italy, Portugal, United Kingdom