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Clinical Trials on Neuromuscular; Disorder, Hereditary
Total 153268 results
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University of BariCompletedCharcot-Marie-Tooth DiseaseItaly
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Juha PeltonenUnknownNeurofibromatosis 1
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Memorial Medical CenterUnited States Department of DefenseCompleted
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Mayo ClinicCompletedNeurofibromatosis
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Medical University of ViennaUnknownCutaneous NeurofibromasAustria
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Stealth BioTherapeutics Inc.CompletedFuchs' Corneal Endothelial Dystrophy (FCED)United States
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Institute of Biophysics and Cell Engineering of...Belarusian State Medical UniversityCompletedCorneal Ulcer | Corneal Dystrophy | Corneal DiseaseBelarus
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Medical College of WisconsinCompletedCataract | Fuchs' Corneal DystrophyUnited States
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University Hospital, ToursCompletedNeuromuscular Diseases in Children | Neuromuscular Diseases in InfantsFrance
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General Hospital of Chinese Armed Police ForcesUnknownHereditary Cerebellar Ataxia.China
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University Medical Centre LjubljanaRecruitingPeripheral Nervous System Diseases | Carpal Tunnel Syndrome | Nerve Compression SyndromesSlovenia
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Kristina HardyChildren's Hospital Los Angeles; Sydney Children's Hospitals Network; Royal Children... and other collaboratorsCompletedNeurofibromatosis Type 1United States
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Erasmus Medical CenterUniversitaire Ziekenhuizen KU Leuven; ZonMw: The Netherlands Organisation for... and other collaboratorsTerminatedNeurofibromatosis Type 1Spain, Belgium, Netherlands
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John Jay High SchoolUnknownNeurofibromatosis Type 1United States
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The Hong Kong Polytechnic UniversityCompletedNeuromuscular Diseases | Extraocular Muscle DisorderHong Kong
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KalVista Pharmaceuticals, Ltd.RecruitingHereditary AngioedemaUnited States, Bulgaria, France, Greece, Israel, Netherlands, Spain, United Kingdom, Australia, Germany, South Africa, Slovakia, Austria, New Zealand, Romania, Canada, Japan
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KalVista Pharmaceuticals, Ltd.RecruitingHereditary AngioedemaUnited States, Bulgaria, France, Greece, Hungary, Israel, Italy, Netherlands, New Zealand, North Macedonia, Poland, Spain, United Kingdom, Australia, Germany, South Africa, Austria, Portugal, Slovakia, Romania, Canada, Saudi Arabia, Japa...
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Pharming Technologies B.V.US Hereditary Angioedema AssociationCompleted
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BioCryst PharmaceuticalsActive, not recruitingHereditary Angioedema | PediatricSpain, Austria, Canada, France, Germany, Israel, Italy, Poland, Romania, United Kingdom
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Ionis Pharmaceuticals, Inc.Active, not recruitingHereditary AngioedemaNetherlands, United States
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KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited States, Australia, Bulgaria, Canada, France, Germany, Greece, Hungary, Israel, Italy, Japan, Netherlands, New Zealand, North Macedonia, Poland, Portugal, Puerto Rico, Romania, Slovakia, Spain, United Kingdom
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TakedaCompletedAngioedemas, HereditaryArgentina
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BioCryst PharmaceuticalsCompletedHereditary Angioedema | HAEUnited States, Austria, Canada, Czechia, France, Germany, Hungary, North Macedonia, Romania, Spain, United Kingdom
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ShireCompletedHereditary AngioedemaUnited States
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ShireJerini AGCompletedHereditary AngioedemaSpain, Argentina, Austria, Denmark, France, Germany, Israel, Italy, Switzerland, United Kingdom
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BioCryst PharmaceuticalsCompletedHereditary AngioedemaUnited Kingdom
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Assistance Publique - Hôpitaux de ParisCompleted
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BioCryst PharmaceuticalsCompletedHereditary Angioedema | HAEFrance, United Kingdom, Germany, United States, Belgium, Hungary, Italy, Canada
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Johann Wolfgang Goethe University HospitalCSL Behring; University of Milan; PharmaPart; Clinical trial center Rhine-Main; ZKI... and other collaboratorsCompletedHereditary AngioedemaGermany
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Ionis Pharmaceuticals, Inc.RecruitingHereditary AngioedemaUnited States, Puerto Rico, Belgium, Bulgaria, Canada, France, Germany, Israel, Italy, Netherlands, Poland, Spain, Turkey, United Kingdom
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Intellia TherapeuticsEnrolling by invitationHereditary AngioedemaFrance, New Zealand, United Kingdom, Netherlands
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BioMarin PharmaceuticalActive, not recruitingHereditary Angioedema | HAESpain, United States, Australia
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Pharming Technologies B.V.CompletedHereditary AngioedemaIsrael, Italy, United States, Czechia, Germany, Hungary, Poland, Romania, Slovakia, North Macedonia
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Astria Therapeutics, Inc.Completed
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Ionis Pharmaceuticals, Inc.CompletedHereditary AngioedemaUnited States, France, Netherlands, Spain, United Kingdom, Belgium, Bulgaria, Canada, Denmark, Germany, Israel, Italy, Poland, Turkey
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CSL BehringCompletedHereditary AngioedemaUnited States, Germany, Japan, Hungary, Canada, Netherlands, Israel
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TakedaCompletedHereditary AngioedemaBelgium, Bulgaria, Estonia, Spain, Hungary, Israel, Germany, Czechia, Portugal, Greece, Lithuania, Poland, Latvia, Croatia, Slovakia, Austria, Canada, Ireland, North Macedonia, Romania, Serbia, Slovenia
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TakedaCompletedHereditary AngioedemaJapan
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CSL BehringCompletedHereditary AngioedemaCanada, Australia, Germany, United States, Israel
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ShireCompletedHereditary AngioedemaUnited States, Canada, Germany, Hungary, Spain
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TakedaCompletedHereditary AngioedemaJapan
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CENTOGENE GmbH RostockTerminated
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KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited Kingdom
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AO GENERIUMWithdrawnHereditary AngioedemaRussian Federation
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ShireCompletedHereditary AngioedemaUnited States
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ShireCompletedHereditary AngioedemaUnited States
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ShireCompletedHereditary AngioedemaUnited States, Australia, Israel, Canada, Hungary, Romania, Russian Federation, South Africa, Ukraine
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ShireCompletedHereditary AngioedemaItaly
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ShireCompletedHereditary AngioedemaUnited States
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AO GENERIUMCompletedHereditary AngioedemaRussian Federation