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Clinical Trials on Niemann-Pick Disease, Type A
Total 58546 results
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Khon Kaen UniversityCompletedMusical Therapy as a Complementary Treatment of HypertensionThailand
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University Hospital, BonnSwedish Orphan BiovitrumRecruitingHaemophilia A | Synovitis | Hemophilia Arthropathy | SonographyGermany
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia B | Relatives to/Carers of PatientsBrazil
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DiaSorin Molecular LLCCompletedCoronavirus Disease 2019 | Influenza A | Influenza Type BAustralia
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Boston Scientific CorporationCompletedBradycardia | Sinus Node DysfunctionUnited States, Israel, Singapore, Malaysia, Australia, Canada, China
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Swedish Orphan BiovitrumCompletedHaemophilia A | Haemophilia BGermany
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BayerCompletedHemophilia A; Hemophilia BIsrael
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Novo Nordisk A/SCompletedHaemophilia A | Haemophilia BUnited States
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Kansas State UniversityNational Institute for Medical Research, Tanzania; United States Department... and other collaboratorsCompletedAnemia, Iron-Deficiency | Deficiency, Vitamin A
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Centre Hospitalier Universitaire de Saint EtiennePfizer; Ecole Normale Supérieure des Mines de Saint-EtienneCompletedHaemophilia A | Haemophilia BFrance
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Biotronik SE & Co. KGTerminatedSinus Node DiseaseSpain, Hungary, Taiwan, Korea, Republic of, India, Singapore, Italy, China, Malaysia
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Silence Therapeutics plcMedpace, Inc.CompletedDyslipidemias | Hyperlipidemias | Elevated Lp(a)United States, Australia, United Kingdom, Netherlands
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University Hospital, Clermont-FerrandCompletedPatients With Systemic Inflammatory Diseases Receiving for the First Time a Protracted General Corticostroid TherapyFrance
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American Thrombosis and Hemostasis NetworkBioMarin PharmaceuticalCompletedLiver Transplantation | Hemophilia A and BUnited States
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Baxalta now part of ShireBaxalta Innovations GmbH, now part of ShireCompletedAcquired Hemophilia AUnited States
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Tulane University School of MedicineCompletedHemophilia A With InhibitorsUnited States
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University of OxfordImperial College London; Public Health EnglandUnknownInvasive Streptococcal Infection | Invasive Group A Streptococcal Disease | Invasive Group B Streptococcal Disease | Necrotising FasciitisUnited Kingdom
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TakedaCompleted
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JCR Pharmaceuticals Co., Ltd.RecruitingMucopolysaccharidosis III-AGermany
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Shengxian FanCompletedThe Clinical Incidence of Low Triiodothyronine Syndrome
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University of AbujaUniversity of CambridgeCompletedA Feasibility Study on Hypertensive Heart Failure TreatmentNigeria
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University College, LondonRecruiting
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University of British ColumbiaBiogenCompletedHemophilia A, Congenital | Hemophilia B, CongenitalCanada
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Fondation LenvalNot yet recruitingPediatric Triage in a Pediatric Emergency DepartmentFrance
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Eli Lilly and CompanyRecruitingElevated Lp(a) | Atherosclerotic Cardiovascular Disease (ASCVD)United States, Australia, Spain, Canada, Argentina, China, Italy, France, Japan, Taiwan, Korea, Republic of, Denmark, Germany, Hungary, Israel, Austria, Belgium, Netherlands, Brazil, Mexico, Romania, United Kingdom, Greece, Czechia, Poland and more
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McGill University Health Centre/Research Institute...CHU de Quebec-Universite LavalUnknownType2 Diabetes | Islet Cell Transplantation | Type1 Diabetes MellitusCanada
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GlaxoSmithKlineCompletedHepatitis BUnited States, Australia, Canada, New Zealand
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The First Affiliated Hospital with Nanjing Medical...Zhejiang UniversityUnknownAtrial Fibrillation | Sinus Node DysfunctionChina
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University of Missouri-ColumbiaRecruiting
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University Health Network, TorontoWeston Brain InstituteRecruitingFrontotemporal Dementia | Deep Brain StimulationCanada
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Boston University Charles River CampusMassachusetts General Hospital; University of Michigan; National Institute on...RecruitingAphasia, Primary Progressive | Stuttering, DevelopmentalUnited States
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University Hospital, ToulouseRecruitingPrimary Progressive AphasiaFrance
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Novartis PharmaceuticalsTerminatedc-MET Inhibitor; PI3K Inhibitor, PTEN Mutations, Homozygous Del. of PTEN or PTEN Neg. by IHC, c-Met Ampli. by FISH, INC280, BKM120, Buparlisib; Recurrent GBMSpain, Switzerland, Germany, United States, Netherlands
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Stanford UniversityNational Cancer Institute (NCI)TerminatedRecurrent Hepatocellular Carcinoma | Child-Pugh Class A | Child-Pugh Class BUnited States, Japan
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Cliniques universitaires Saint-Luc- Université...CompletedHaemophilia A | Haemophilia BBelgium
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Massachusetts General HospitalAlzheimer's Drug Discovery FoundationRecruitingFrontotemporal DementiaUnited States, Italy
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Alector Inc.Active, not recruitingFrontotemporal DementiaSpain, United States, Portugal, United Kingdom, France, Germany, Netherlands, Belgium, Australia, Italy, Turkey, Switzerland, Argentina, Canada, Greece, Sweden
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Samsung Medical CenterActive, not recruitingFrontotemporal DementiaKorea, Republic of
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Denali Therapeutics Inc.TakedaActive, not recruitingFrontotemporal DementiaSpain, Turkey, France, Belgium, Netherlands, Portugal, Italy, Colombia, Czechia, Brazil, United Kingdom, Serbia
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Lawson Health Research InstituteCanadian Institutes of Health Research (CIHR); Berry Consultants; Weston Brain...Active, not recruitingFrontotemporal DementiaUnited States, Canada
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CENTOGENE GmbH RostockActive, not recruitingFrontotemporal DementiaItaly, Spain, Belgium, Turkey, Portugal, Germany, Greece
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Avid RadiopharmaceuticalsCompleted
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Lawson Health Research InstituteCanadian Institutes of Health Research (CIHR)CompletedFrontotemporal DementiaCanada
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Sunnybrook Health Sciences CentreAlzheimer Society of CanadaCompletedFrontotemporal DementiaCanada
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Nantes University HospitalCompleted
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Jiangsu Province Centers for Disease Control and...Royal (Wuxi) Biological Co., LTDCompletedGroup A, C Polysaccharide Meningitis | Type b Haemophilus InfluenzaChina
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedHurler Syndrome | Sanfilippo Syndrome Type A | Sanfilippo Syndrome Type BUnited States
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Medtronic Bakken Research CenterCompletedHeart Failure | Heart Block | Arrhythmia | Sinus Node DiseaseBelgium, Russian Federation, Former Serbia and Montenegro, India, Kuwait, Saudi Arabia
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Baxalta now part of ShireCompletedHemophilia A | Hemophilia B | Hemophilia A or B With InhibitorsPoland, United States, Bulgaria, Romania, Japan, Russian Federation, New Zealand, Croatia, Ukraine, Brazil
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Bastyr UniversityRecruitingParkinson's Disease | Parkinsonism | Corticobasal Degeneration | Shy-Drager Syndrome | Progressive Supranuclear Palsy | Dementia With Lewy Bodies | MSA - Multiple System Atrophy | Olivopontocerebellar Atrophies | Pick DiseaseUnited States