- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Non-Dystrophic Myotonia
Total 18578 results
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyBelgium, Netherlands, Italy, Sweden
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Jerry R. MendellEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedDuchenne Muscular DystrophyUnited States
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Boston Children's HospitalBeth Israel Deaconess Medical CenterCompletedDuchenne Muscular DystrophyUnited States
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University of GaziantepIstınye University, Cukurova University, Yıldırım Beyazıt University, Gaziantep...UnknownDuchenne Muscular DystrophyTurkey
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GlaxoSmithKlineWithdrawnMuscular Dystrophies
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedDuchenne Muscular DystrophyCanada
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Shenzhen Beike Bio-Technology Co., Ltd.The Second Affiliated Hospital of Kunming Medical UniversityUnknownDuchenne Muscular DystrophyChina
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Nationwide Children's HospitalNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes...CompletedDuchenne Muscular DystrophyUnited States
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Cooperative International Neuromuscular Research...Completed
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Cooperative International Neuromuscular Research...Completed
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Great Ormond Street Hospital for Children NHS Foundation...Catholic University of the Sacred Heart; Università degli Studi di Ferrara; Universidad... and other collaboratorsRecruitingDuchenne Muscular Dystrophy | Becker Muscular DystrophyDenmark, France, Italy, Spain, United Kingdom, Netherlands
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National Eye Institute (NEI)TerminatedInherited Retinal Degeneration | Inherited Ophthalmic DiseasesUnited States
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BioMarin PharmaceuticalRecruitingDuchenne Muscular DystrophySpain, United Kingdom
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Solid Biosciences Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Hoffmann-La RocheSarepta Therapeutics, Inc.Recruiting
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West China HospitalRecruiting
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Hacettepe UniversityNot yet recruitingDuchenne Muscular DystrophyTurkey
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Edgewise Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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PepGen IncRecruitingDuchenne Muscular DystrophyCanada
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.RecruitingDuchenne Muscular DystrophyUnited States
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Beni-Suef UniversityNot yet recruitingDuchenne Muscular Dystrophy
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingStudy of Genotype and Phenotype Characterization in Duchenne Muscular Dystrophy With Small MutationsMuscular Dystrophy, DuchenneItaly
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REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Muş Alparlan UniversityHacettepe UniversityRecruitingDuchenne Muscular DystrophyTurkey
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Edgewise Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Edgewise Therapeutics, Inc.Medpace, Inc.; SYSNAV; ImagingNMDRecruitingBecker Muscular DystrophyUnited States, Netherlands, United Kingdom
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ReveraGen BioPharma, Inc.Santhera PharmaceuticalsRecruitingBecker Muscular DystrophyUnited States, Italy
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Taiho Pharmaceutical Co., Ltd.RecruitingDuchenne Muscular DystrophyJapan
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GenethonRecruiting
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Halic UniversityIstanbul University; Biruni UniversityCompletedDuchenne Muscular DystrophyTurkey
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Edgewise Therapeutics, Inc.Medpace, Inc.CompletedBecker Muscular DystrophyUnited States
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PfizerActive, not recruitingMuscular Dystrophy, DuchenneUnited States, Australia
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Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Korea, Republic of, Italy, United Kingdom, Canada, Poland, Spain, France, Germany, Belgium, Australia, Czechia, Serbia, Greece, Argentina, Bulgaria, Denmark, Hungary, India, Ireland, Israel, Mexico, Russian Federation, ...
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Sarepta Therapeutics, Inc.Hansa Biopharma ABActive, not recruitingDuchenne Muscular DystrophySpain
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Wave Life Sciences Ltd.Active, not recruitingDuchenne Muscular DystrophyJordan, United Kingdom
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Hacettepe UniversityCompleted
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Çağtay MadenCompleted
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Hacettepe UniversityCompleted
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FibroGenActive, not recruitingDuchenne Muscular DystrophyUnited States, Spain, Canada, Australia, China, Italy, Belgium, France, Netherlands, Austria, United Kingdom
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Sarepta Therapeutics, Inc.Hoffmann-La RocheActive, not recruitingDuchenne Muscular DystrophyUnited States, Japan, Taiwan, Belgium, Spain, Germany, Hong Kong, Italy, United Kingdom
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ItalfarmacoCromsourceEnrolling by invitationDuchenne Muscular DystrophySpain, United States, Canada, Belgium, France, Israel, Italy, Netherlands, Serbia, Germany, United Kingdom
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Kevin FlaniganSarepta Therapeutics, Inc.Completed
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Solid Biosciences Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States
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Kevin FlaniganActive, not recruitingDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyBelgium, France, Italy, United Kingdom
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Solid Biosciences Inc.CompletedDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.Hoffmann-La RocheEnrolling by invitation
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Megan WaldropAudentes TherapeuticsActive, not recruitingDuchenne Muscular DystrophyUnited States
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University Hospital, Basel, SwitzerlandCompletedDuchenne Muscular DystrophyFrance, Spain, Germany, Netherlands, Switzerland, United Kingdom