- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Pantothenate Kinase-associated Neurodegeneration (PKAN)
Total 64 results
-
Susan J. HayflickOregon Health and Science University; Oregon Clinical and Translational Research...CompletedPantothenate Kinase-associated Neurodegeneration (PKAN)United States
-
LMU KlinikumSeventh Framework Programme; NBIA AllianceRecruitingNeurodegeneration With Brain Iron Accumulation (NBIA) | Pantothenate Kinase-associated Neurodegeneration (PKAN) | Aceruloplasminemia | Beta-Propeller Protein-Associated Neurodegeneration (BPAN) | Mitochondrial Membrane Protein Associated Neurodegeneration (MPAN) | Fatty Acid Hydroxylase-associated... and other conditionsCanada, Czechia, Germany, Italy, Netherlands, Poland, Serbia, Spain
-
ApoPharmaFood and Drug Administration (FDA)CompletedPantothenate Kinase-Associated NeurodegenerationUnited States, Germany, Italy, United Kingdom
-
Chiesi Canada CorpNo longer availablePantothenate Kinase-Associated Neurodegeneration
-
Travere Therapeutics, Inc.TerminatedPantothenate Kinase-Associated NeurodegenerationUnited States, Canada, Czechia, France, Germany, Italy, Norway, Poland, Spain
-
ApoPharmaCompletedPantothenate Kinase-Associated NeurodegenerationUnited States, Germany, Italy, United Kingdom
-
Oregon Health and Science UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsActive, not recruitingPantothenate Kinase-Associated NeurodegenerationUnited States
-
Susan J. HayflickOregon Health and Science UniversityRecruitingNeurodegeneration With Brain Iron Accumulation (NBIA)United States
-
University Hospital, BordeauxInstitut National de la Santé Et de la Recherche Médicale, FranceCompletedNeurodegeneration With Brain Iron Accumulation (NBIA)France
-
Ente Ospedaliero Ospedali GallieraActive, not recruitingIron Overload | Neurodegenerative DiseaseItaly
-
University College, LondonUnknownMitochondrial Diseases | Dystonia, Familial | Sporadic Dystonia | Parkinson Disease, Juvenile | Neurodegeneration With Brain Iron Accumulation 5
-
University Hospital, BordeauxRecruitingIntellectual Disability | Cystic Fibrosis | Neurodegeneration With Brain Iron Accumulation (NBIA) | Congenital Heart Defect | Albinism | Rubinstein-Taybi Syndrome | Periventricular Nodular HeterotopiaFrance
-
Tel-Aviv Sourasky Medical CenterUnited States Department of DefenseRecruitingEvaluation of the Frequency and Severity of Sleep Abnormalities in Patients With Parkinson's DiseaseParkinson Disease | GBA Gene Mutation | Leucine-rich Repeat Kinase 2 (LRRK2) Gene MutationIsrael
-
Escape Bio, Inc.Momentum Pharma; Science 37TerminatedPatients With Parkinson's Disease (PD) Caused by the p.Gly2019Ser (G2019S) Pathogenic Mutation of the Leucine-Rich Repeat Kinase 2 (LRRK2) GeneUnited States
-
University of Novi SadMerck Sharp & Dohme LLCRecruitingMetabolic Syndrome | Aging | HIV I Infection | HIV Associated LipodystrophySerbia
-
Institut de Sante Publique, d'Epidemiologie et...CompletedAlzheimer Disease or Associated Disorder | Mild to Moderately Severe DementiaFrance
-
Karuna TherapeuticsRecruitingPsychosis Associated With Alzheimer's DiseaseUnited States, Korea, Republic of, Chile, Greece, Poland
-
Karuna TherapeuticsRecruitingPsychosis Associated With Alzheimer's DiseaseUnited States, Spain, Slovakia, Bulgaria, France, Czechia, Italy, Serbia, Germany, Croatia
-
Karuna TherapeuticsEnrolling by invitationPsychosis Associated With Alzheimer's DiseaseUnited States, Czechia, Slovakia
-
SunovionCompletedMotor OFF Episodes Associated With Parkinson's DiseaseSpain, United Kingdom, Germany, Italy, Austria, France
-
Beth Israel Deaconess Medical CenterMichael J. Fox Foundation for Parkinson's ResearchCompletedVoice Quality and Voice Loudness Associated With Parkinson's DiseaseUnited States
-
Novartis PharmaceuticalsAvailableAcute Myeloid Leukemia | Mast Cell Leukemia | Aggressive Systemic Mastocytosis | Systemic Mastocytosis With an Associated Hematologic Neoplasm | FMS-Like Tyrosine Kinase 3 (FLT3)-Mutated Acute Myeloid Leukemia
-
InSightecRecruitingTremor Associated With Tremor Dominant Parkinson's DiseaseUnited States
-
Otsuka Pharmaceutical Development & Commercialization...H. Lundbeck A/SCompletedAlzheimer Dementia | Agitation Associated With Alzheimer's DementiaUnited States
-
Otsuka Pharmaceutical Development & Commercialization...H. Lundbeck A/SCompletedNervous System Diseases | Alzheimer's Disease | Mental Disorder | Agitation Associated With | Alzheimer's TypeSpain, United States, Germany, Croatia, Serbia, Russian Federation, Ukraine
-
BiogenRecruitingAmyotrophic Lateral Sclerosis Associated With a SOD1 Gene MutationUnited States, Canada, Spain, Australia, Germany, Italy, Japan, Korea, Republic of, United Kingdom, Belgium, Brazil, France, Poland, Sweden
-
University of BernNovartis; University Hospital Inselspital, Berne; Schweizerische Multiple Sklerose... and other collaboratorsRecruitingMultiple Sclerosis | Optic Neuritis | Neuromyelitis Optica Spectrum Disorder | CNS Sarcoidosis | CNS Vasculitis | Transverse Myelitis | Rasmussen Encephalitis | Acute Disseminated Encephalomyelitis | Anti-NMDAR Encephalitis | Anti-GAD65 Associated Autoimmune Encephalitis | Anti-AMPAR-1/2 Associated Autoimmune... and other conditionsSwitzerland
-
Luye Pharma Group Ltd.Not yet recruitingNegative Symptoms of Schizophrenia | Hallucinations and Delusions Associated With Alzheimer's Disease Psychosis | Hallucinations and Delusions Associated With Parkinson Disease PsychosisChina
-
Otsuka Pharmaceutical Co., Ltd.CompletedAgitation Associated With Dementia of the Alzheimer's TypeJapan
-
Otsuka Pharmaceutical Co., Ltd.CompletedAgitation Associated With Dementia of the Alzheimer's TypeJapan
-
Otsuka Pharmaceutical Development & Commercialization...H. Lundbeck A/SCompletedNervous System Diseases | Alzheimer's Disease | Mental Disorder | Agitation Associated With | Alzheimer's TypeFrance, United States, Bulgaria, Slovenia, United Kingdom, Russian Federation, Ukraine, Finland, Canada
-
Otsuka Pharmaceutical Co., Ltd.TerminatedAgitation Associated With Dementia of the Alzheimer's TypeJapan
-
Atara BiotherapeuticsRecruitingHigh-grade B-cell Lymphoma | MCL | Diffuse Large B-cell Lymphoma (DLBCL) | Relapsed/Refractory B-cell Non-Hodgkin Lymphoma | DLBCL/High-grade B-cell Lymphoma With MYC and BCL2 Rearrangements | Anaplastic Lymphoma Kinase-Positive Large B-Cell Lymphoma | LBCL With IRF4 Rearrangement | High-grade B-cell... and other conditionsUnited States
-
Solvay PharmaceuticalsTerminatedPsychosis and Behavioral Disturbances Associated With Dementia of the Alzheimer's TypeUnited States, Czech Republic, Estonia, Israel, Poland
-
Otsuka Pharmaceutical Development & Commercialization...H. Lundbeck A/SCompletedNervous System Diseases | Mental Disorder | Alzheimer's Type | Agitation Associated With Alzheimer's DiseaseUnited States, Germany, France, Bulgaria, Spain, Slovenia, Croatia, Serbia, Russian Federation, Ukraine, Canada, United Kingdom
-
Helse Stavanger HFKing's College London; Lund UniversityCompletedDementia With Lewy Bodies | Dementia Associated With Parkinson's DiseaseUnited Kingdom, Norway, Sweden
-
Hospices Civils de LyonRecruitingAutoimmune Encephalitis Associated With Anti-CAPR2 AntibodiesFrance
-
Hospices Civils de LyonRecruitingNMDAR Antibody-associated Auto-immune EncephalitisFrance
-
Jazz PharmaceuticalsRecruitingTuberous Sclerosis Complex Associated Neuropsychiatric DiseaseUnited States, United Kingdom, Poland
-
Auspex Pharmaceuticals, Inc.CompletedChorea Associated With Huntington DiseaseUnited States, Australia, Canada
-
Assistance Publique - Hôpitaux de ParisCompletedMPA | PAN or EGPA With FFS=0 | At Diagnosis or Within the First 15 Days Following Initiation of CorticosteroidsFrance
-
Shanghai Pulmonary Hospital, Shanghai, ChinaRecruitingThymoma | Myasthenia Gravis Associated With Thymoma | ThymectomyChina
-
Novartis PharmaceuticalsCompletedTuberous Sclerosis Complex-associated Refractory SeizuresUnited States, Colombia, Belgium, France, Japan, Taiwan, Turkey, Spain, Thailand, Korea, Republic of, Australia, Hungary, United Kingdom, Canada, Norway, Germany, Italy, Russian Federation, Denmark, Argentina, Netherlands, Greece, P... and more
-
First Affiliated Hospital, Sun Yat-Sen UniversityCompletedMyasthenia Gravis Associated With Thymoma
-
Novartis PharmaceuticalsTerminatedPlexiform Neurofibroma Associated With Neurofibromatosis Type 1Israel
-
SpringWorks Therapeutics, Inc.AvailableNeurofibromatosis Type 1-Associated Plexiform Neurofibromas | Histiocytic Neoplasm | Other MAP-K Pathway Driven Diseases
-
National Institute of Mental Health (NIMH)TerminatedHIV Infections | Healthy | AIDS Dementia Complex | AIDS-Related Dementia Complex | HIV-Associated Cognitive Motor Complex | HIV-Dementia | AIDS EncephalopathyUnited States
-
Peter MerkelNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsRecruitingVasculitis | Eosinophilic Granulomatosis With Polyangiitis (EGPA) | Cryoglobulinemic Vasculitis (CV) | Drug-induced Vasculitis | IgA Vasculitis | Isolated Cutaneous Vasculitis | Granulomatosis With Polyangiitis (GPA) | Microscopic Polyangiitis (MPA) | Polyarteritis Nodosa (PAN) | Urticarial VasculitisUnited States, Canada
-
Memorial Sloan Kettering Cancer CenterRecruitingSolid Tumor | Neuroblastoma | Solid Tumor, Adult | Primary Brain Tumor | Solid Carcinoma | Low-grade Glioma | Central Nervous System Tumor | Refractory Cancer | CNS Tumor, Adult | CNS Tumors | NF1 | Plexiform Neurofibroma | CNS Tumor, Childhood | Optic Pathway Gliomas | MAP Kinase Family Gene MutationUnited States
-
Xuanwu Hospital, BeijingRecruitingMultiple Sclerosis | Myasthenia Gravis | Autoimmune Encephalitis | Acute Disseminated Encephalomyelitis | NMO Spectrum Disorder | Myelin Oligodendrocyte Glycoprotein Antibody-associated DiseaseChina