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Clinical Trials on Pediatric: Genetic Syndrome
Total 47655 results
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Longboard PharmaceuticalsAvailableDravet Syndrome | Lennox Gastaut Syndrome | Developmental and Epileptic EncephalopathiesUnited States
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TakedaOvid Therapeutics Inc.CompletedEpilepsy | Dravet Syndrome | Lennox-Gastaut SyndromeUnited States, Canada, Israel, Poland, Spain, Australia, China, Portugal
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Longboard PharmaceuticalsCompletedDravet Syndrome | Lennox Gastaut Syndrome | Developmental and Epileptic EncephalopathyUnited States, Australia
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University of CalgaryCanadian Institutes of Health Research (CIHR); Alberta Children's Hospital; Stollery... and other collaboratorsNot yet recruitingPediatric Cancer | Pediatric Hematology
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National Taiwan University HospitalUnknownPalliative Care | Pediatric Cancer | Nursing Caries | Oncology | Pediatric PopulationTaiwan
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Peking Union Medical College HospitalShengjing Hospital; The Affiliated Hospital of Qingdao University; Children's... and other collaboratorsRecruitingPediatric ALL | Sjogren's SyndromeChina
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Ryan St. Pierre-HetzActive, not recruitingQuality of Life | Pediatric Disorder | Central Line Complication | Short Gut Syndrome | Central Line Infection | Central Line-Associated Infection | Central Line SepsisUnited States
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Children's Healthcare of AtlantaEmory UniversityCompletedPediatric Preoperative Anxiety, Pediatric CopingUnited States
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Lundbeck LLCCompletedEpilepsy | Epilepsy, Generalized | SeizuresUnited States, Belarus, India, Australia, Lithuania
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Lundbeck LLCCompletedEpilepsy | Epilepsy, Generalized | SeizuresUnited States
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National Cancer Institute (NCI)RecruitingNeoplasms | Li-Fraumeni Syndrome | Tp53 MutationsUnited States
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Phoenix Children's HospitalCompletedMyelodysplastic Syndromes | Vitamin D Deficiency | Pediatric Cancer | Aplastic Anemia | Stem Cell Transplant Complications | Sickle Cell Anemia in Children | Thalassemia in Children | Blood Disorder | Pediatric Acute Myeloid Leukemia | Pediatric Acute Lymphoid LeukemiaUnited States
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Rabin Medical CenterUnknownLynch Syndrome | BRCA1 Syndrome | BRCA2 SyndromeIsrael
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Hospices Civils de LyonUnknownCancer | Paraneoplastic Syndromes | Neurologic Disorder | Immune System and Related Disorders | Tumor GeneticsFrance
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National Institute of Arthritis and Musculoskeletal...Terminated
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Grifols Therapeutics LLCCompletedImmunologic Deficiency SyndromeUnited States, Canada
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Green Cross CorporationAtlantic Research GroupCompletedImmunologic Deficiency SyndromeUnited States, Canada
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Sheba Medical CenterCompletedDry Eye Syndrome | Ptosis | DermatochalasisIsrael
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China Medical University HospitalRecruiting
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Children's Mercy Hospital Kansas CityKatherine Berry Richardson FoundationCompleted
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National Center for Research Resources (NCRR)Completed
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Dana-Farber Cancer InstituteNational Cancer Institute (NCI); Baylor College of Medicine; City of Hope Medical...RecruitingTP53 Gene Mutation | Li-Fraumeni Syndrome | Hereditary Cancer Syndrome | Mosaicism | Clonal HematopoiesisUnited States
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Hadassah Medical OrganizationUnknown
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National Institute of Allergy and Infectious Diseases...Completed
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National Institute of Allergy and Infectious Diseases...Clinical Trials in Organ Transplantation in ChildrenCompletedPediatric Heart Transplantation | Pediatric Heart Transplant RecipientsUnited States, Canada
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Rady Pediatric Genomics & Systems Medicine InstituteEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsActive, not recruitingGenetic Diseases | Genetic Syndrome | Mendelian DisordersUnited States
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National Institute of Allergy and Infectious Diseases...TerminatedAutosomal-dominant Hyper-IgE SyndromeUnited States
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Gulhane Training and Research HospitalRecruitingThe Study Addressed the Most Common Geriatric Syndromes and Chronic Diseases at Age 90 Years and Older and Their AssociationTurkey
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)CompletedHigh-Frequency Microsatellite Instability | Mismatch Repair Gene Mutation | Mutation-Negative Lynch Syndrome | Mutation-Positive Lynch SyndromeUnited States
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Izmir Katip Celebi UniversityNot yet recruiting
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Yonsei UniversityCompleted
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Catalyst Pharmaceuticals, Inc.No longer availableLambert-Eaton Myasthenic Syndrome | Congenital Myasthenic Syndrome | Nystagmus, AcquiredUnited States
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University Medical Center GroningenCompletedRespiratory Failure | Respiration, Artificial | Ventilator Weaning | Pediatrics | Pediatric Respiratory Diseases | Work of BreathingNetherlands
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Assiut UniversityNot yet recruitingNeurocutaneous Syndromes
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National Institute of Allergy and Infectious Diseases...Active, not recruitingHypersensitivity, Immediate | Autoinflammatory Syndromes | Physical Urticaria | Familial Cold Autoinflammatory SyndromeUnited States
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Zomagen Biosciences, LtdCompletedCryopyrin Associated Periodic SyndromeUnited States
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Federico II UniversityUnknown
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Charite University, Berlin, GermanyCompletedSchnitzler Syndrome | Muckle-Wells SyndromeGermany
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National Human Genome Research Institute (NHGRI)Active, not recruitingWiskott- Aldrich Syndrome | ADA Deficient SCIDUnited States
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International Rett Syndrome FoundationBaylor College of Medicine; Children's Hospital of Philadelphia; University of... and other collaboratorsRecruitingNervous System Diseases | Neurologic Manifestations | Neurobehavioral Manifestations | Genetic Diseases, X-Linked | Intellectual Disability | Neurodevelopmental Disorders | Neurologic Disorder | Rett Syndrome | Genetic Disease | Rett Syndrome, AtypicalUnited States
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National Cancer Institute (NCI)CompletedPediatric Leukemia | Other Pediatric CancersUnited States
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Massachusetts General HospitalNational Cancer Institute (NCI); Boston Medical CenterCompletedGenetic TestingUnited States
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Boston Children's HospitalRecruitingGenetic Predisposition to Disease | Genetic Disease | Development, Infant | Genetic Syndrome | Development, ChildUnited States
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Hospital de la RiberaUniversity of ValenciaWithdrawnFrailty | Functional Recovery | Geriatric SyndromesSpain
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Shandong Cancer Hospital and InstituteRecruitingPediatric CancerChina
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Koç UniversityNot yet recruitingPediatric Population
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University of California, San DiegoNational Cancer Institute (NCI); Dana-Farber Cancer Institute; University of... and other collaboratorsRecruiting
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Immune Oncology Research InstituteRecruitingContinuous Infusion of First-Generation 5-HT3 Receptor Antagonists in Combination With DexamethasonePediatric CancerArmenia
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Connecticut Children's Medical CenterThe Hospital for Sick ChildrenRecruitingPediatric CancerUnited States