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Clinical Trials on Phosphoglucomutase 1 Deficiency
Total 14282 results
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Indiana Hemophilia &Thrombosis Center, Inc.Active, not recruitingPlasminogen Activator Inhibitor-1 Deficiency | Cardiac FibrosisUnited States
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Wave Life Sciences Ltd.RecruitingAlpha-1 Antitrypsin DeficiencyUnited Kingdom
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Kamada, Ltd.Syneos HealthRecruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom, Sweden, Ireland, Netherlands, Belgium, Finland
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Alpha-1 FoundationRecruiting
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CSL BehringActive, not recruitingAlpha-1 Antitrypsin DeficiencyFrance
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyCompleted
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Baxalta now part of ShireCompletedAlpha 1-Antitrypsin DeficiencyNew Zealand, Australia
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Baxalta now part of ShireBaxter Healthcare, Ltd. (New Zealand), Baxter Healthcare Pty. Ltd. (Australia)CompletedAlpha 1-Antitrypsin DeficiencyAustralia, New Zealand
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Medical University of South CarolinaAlpha-1 FoundationCompleted
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National Jewish HealthMedical University of South CarolinaUnknownAlpha 1-Antitrypsin DeficiencyUnited States
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Biocerna LLCCompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Medical University of South CarolinaNational Center for Research Resources (NCRR); Alpha-1 FoundationCompletedAlpha-1 Antitrypsin DeficiencyUnited States
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Grifols Therapeutics LLCCompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Grifols Therapeutics LLCCompletedAlpha 1-Antitrypsin DeficiencyUnited States, United Kingdom
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National Center for Research Resources (NCRR)University of PittsburghTerminatedAlpha 1-Antitrypsin DeficiencyUnited States
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National Institute of Allergy and Infectious Diseases...Recruiting
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University of British ColumbiaUltragenyx Pharmaceutical IncUnknownGlucose Transporter Type 1 Deficiency SyndromeCanada
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Krystal Biotech, Inc.RecruitingAlpha 1-Antitrypsin DeficiencyUnited States
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Hospital Universitari Vall d'Hebron Research InstituteEuropean Respiratory SocietyRecruitingAlpha 1-Antitrypsin DeficiencySpain
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University of FloridaRecruitingAlpha-1 Antitrypsin DeficiencyUnited States
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyActive, not recruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom, United States, Ireland, Belgium, New Zealand, Spain, Netherlands, Portugal, Canada, Australia, France, Austria, Germany, Sweden
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St. Louis UniversityBoston University; University College, London; University of Massachusetts, Worcester and other collaboratorsActive, not recruiting
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Arrowhead PharmaceuticalsCompleted
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Arrowhead PharmaceuticalsTerminatedAlpha-1 Antitrypsin DeficiencyAustralia, Netherlands, Germany, United Kingdom
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Kamada, Ltd.CompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Beam Therapeutics Inc.Not yet recruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom
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Vertex Pharmaceuticals IncorporatedActive, not recruitingAlpha-1 Antitrypsin DeficiencyUnited States, United Kingdom, Germany, Ireland
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Vertex Pharmaceuticals IncorporatedCompleted
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Vertex Pharmaceuticals IncorporatedCompleted
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Arrowhead PharmaceuticalsCompletedAlpha 1-Antitrypsin DeficiencyUnited States, Spain, Netherlands, Germany, Italy, Portugal
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Adverum Biotechnologies, Inc.Completed
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Vertex Pharmaceuticals IncorporatedTerminatedAlpha 1-Antitrypsin DeficiencyUnited States, Germany, Canada, Ireland
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Kamada, Ltd.CompletedAlpha-1 Antitrypsin DeficiencyUnited States
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Fondazione Salvatore MaugeriAzienda Socio Sanitaria Territoriale degli Spedali Civili di Brescia; Grifols... and other collaboratorsCompletedAlpha-1 Antitrypsin Deficiency
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OctapharmaWithdrawn
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Arrowhead PharmaceuticalsWithdrawnAlpha-1 Antitrypsin DeficiencyIreland, Canada, Italy, Sweden
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Ultragenyx Pharmaceutical IncAvailableGlucose Transporter Type 1 Deficiency Syndrome (Glut1 DS)
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IpsenCompletedGrowth Disorders | Insulin-Like Growth Factor-1 DeficiencyUnited States
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Applied Genetic Technologies CorpNational Heart, Lung, and Blood Institute (NHLBI)CompletedAlpha-1 Antitrypsin DeficiencyUnited States, Ireland
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Juan PascualActive, not recruitingGlucose Transporter Type 1 Deficiency Syndrome | GLUT1DS1United States
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Janssen Sciences Ireland UCCompletedImmunodeficiency Virus Type 1, HumanUnited States, France, Poland, United Kingdom, Belgium, Germany, Spain, Canada, Russian Federation, Puerto Rico
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CSL BehringCompletedEmphysema | Alpha 1-proteinase Inhibitor DeficiencyAustralia, Canada, Czech Republic, Denmark, Estonia, Finland, Germany, Ireland, Poland, Romania, Sweden
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Adverum Biotechnologies, Inc.CompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Inhibrx, Inc.CompletedAlpha-1 Antitrypsin Deficiency | AATDUnited States, New Zealand, United Kingdom
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Coram Clinical TrialsCompletedAlpha-1 Anti-trypsin DeficiencyUnited States
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Arrowhead PharmaceuticalsActive, not recruitingAlpha 1-Antitrypsin DeficiencyAustria, Germany, United Kingdom
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Dicerna Pharmaceuticals, Inc.WithdrawnAlpha 1-Antitrypsin DeficiencyNew Zealand
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Mereo BioPharmaSyneos HealthCompletedEmphysema | Alpha 1-Antitrypsin Deficiency | COPDUnited Kingdom, Belgium, United States, Denmark, Canada, Sweden, Poland, Spain
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Ultragenyx Pharmaceutical IncCompletedGlucose Transporter Type 1 Deficiency Syndrome (Glut1 DS)United States, Spain, Australia, France, Israel, Italy, United Kingdom
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University of Massachusetts, WorcesterNational Heart, Lung, and Blood Institute (NHLBI); University of Florida; National... and other collaboratorsCompletedAlpha 1-Antitrypsin DeficiencyUnited States