- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Polymorphism, Genetic in Colombia
Total 921 results
-
BayerCompletedHemophilia AUnited States, Japan, United Kingdom, Spain
-
University of UtahUniversity of British Columbia; Children's Hospital Medical Center, Cincinnati and other collaboratorsTerminatedNeurofibromatosis Type 1 (NF1)United States, Canada
-
ItalfarmacoSyneos HealthCompletedDuchenne Muscular DystrophyUnited States, Italy, Spain, Canada, Belgium, France, Germany, Israel, Netherlands, Serbia, United Kingdom
-
PfizerTerminatedDuchenne Muscular DystrophyUnited States, Australia, Canada, United Kingdom, Japan, Bulgaria, Italy, Poland
-
Eli Lilly and CompanyDermira, Inc.CompletedAtopic DermatitisUnited States
-
Incyte CorporationCompletedAtopic DermatitisUnited States, Canada
-
Ionis Pharmaceuticals, Inc.CompletedHuntington's DiseaseCanada, United Kingdom, Germany
-
Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type IIUnited States, France, Netherlands
-
Dermavant Sciences GmbHCompletedAtopic DermatitisUnited States, Canada
-
LEO PharmaCompletedAtopic DermatitisUnited States, Germany, Belgium, Canada, Spain, United Kingdom, Poland, Netherlands
-
Boston Children's HospitalUniversity of California, San Diego; Food and Drug Administration (FDA); Angelman... and other collaboratorsRecruiting
-
PharmaxisCompleted
-
Baxalta now part of ShireCompleted
-
PTC TherapeuticsParexel; Dohmen Life Science ServicesApproved for marketingDuchenne Muscular DystrophyUnited States
-
Mendel TuchmanChildren's Hospital of Philadelphia; University of California, Los Angeles; Icahn... and other collaboratorsCompletedMethylmalonic Acidemia | Carbamoyl-Phosphate Synthase I Deficiency Disease | Propionic Acidemia, Type I and/or Type II | Ornithine Carbamoyltransferase DeficiencyUnited States
-
Sarepta Therapeutics, Inc.Active, not recruitingMuscular Dystrophy, DuchenneUnited States, Korea, Republic of, India, Slovenia, Turkey, United Kingdom, Germany, Switzerland, Spain, Czechia, France, Serbia, Taiwan, Netherlands, Mexico, Colombia, Denmark, New Zealand, Norway, Greece, Hungary, Ireland, Italy, Jo... and more
-
CENTOGENE GmbH RostockWithdrawnFructose Metabolism, Inborn Errors | Glycogen Storage Disease Type II | Glycogen Storage Disease | Glycogen Storage Disease Type V | Glycogen Storage Disease Type I | Glycogen Storage Disease Type III | Glycogen Storage Disease Type VII | Glycogen Storage Disease Type IV | Glycogen Storage Disease Type... and other conditionsGermany, India, Sri Lanka
-
BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
-
Hoffmann-La RocheCompleted
-
Monica BhatiaCompletedSickle Cell Disease | Graft Versus Host DiseaseUnited States
-
Novartis PharmaceuticalsCompletedSickle Cell Disease (SCD)United States
-
Bioverativ, a Sanofi companySwedish Orphan BiovitrumCompletedHemophilia BUnited States, Italy, Ireland, New Zealand, United Kingdom, Australia, Netherlands, Denmark, Poland, Sweden, France
-
Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
-
Seaside Therapeutics, Inc.TerminatedFragile X SyndromeUnited States
-
CENTOGENE GmbH RostockWithdrawnMetabolism, Inborn Errors | Mucopolysaccharidosis Type I | GargoylismGermany, India, Sri Lanka, Egypt
-
Children's Hospital Medical Center, CincinnatiRecruitingSickle Cell Anemia | Children, OnlyUnited States
-
Dermavant Sciences GmbHCompletedAtopic DermatitisUnited States, Canada
-
AnaptysBio, Inc.RecruitingAtopic Dermatitis EczemaGeorgia, United States, Australia, Canada, Czechia, New Zealand, Poland
-
National Institute of Allergy and Infectious Diseases...CompletedCongenital Heart Defects | Situs Inversus | Kartagener Syndrome | Ciliary Dyskinesia, PrimaryUnited States
-
Arcutis Biotherapeutics, Inc.CompletedAtopic Dermatitis EczemaUnited States, Canada
-
National Cancer Institute (NCI)Active, not recruitingNeurofibromatosis 1 | Neurofibroma, Plexiform | Neurofibromatosis Type 1 | NF1United States
-
Genzyme, a Sanofi CompanyCompleted
-
Montreal Heart InstituteCanadian Institutes of Health Research (CIHR)Enrolling by invitationCardiomyopathies | Hypertrophic Cardiomyopathy | Hypertrophic Obstructive Cardiomyopathy | Familial Hypertrophic CardiomyopathyCanada
-
BioMarin PharmaceuticalCompletedSickle Cell DiseaseUnited States
-
LEO PharmaRecruitingAtopic DermatitisUnited States, Canada, France, Germany, Japan, Poland, United Kingdom, Czechia, Spain, Romania, Hungary
-
Swedish Orphan BiovitrumBioverativ Therapeutics Inc.CompletedHemophilia AIreland, United Kingdom, Germany, United States, Canada, Slovenia, Sweden
-
Genzyme, a Sanofi CompanyCompletedFabry DiseaseUnited States, Poland, Netherlands, Canada, Argentina, United Kingdom, Norway, Brazil, Czech Republic
-
PfizerCompletedAtopic DermatitisGermany, United States, Canada, Denmark, Hungary, Australia, Latvia, Poland, Bulgaria, Japan
-
Hoffmann-La RocheCompletedAtopic DermatitisUnited States, Korea, Republic of, Canada, United Kingdom, Germany, Australia, Poland, Finland, France, Spain, Switzerland, Czechia, Netherlands, Taiwan
-
PfizerCompletedAtopic DermatitisUnited States, Canada, Australia, Germany, Hungary
-
ShireCompletedHunter SyndromeUnited States, United Kingdom, Canada
-
CENTOGENE GmbH RostockWithdrawnLipoprotein Lipase Deficiency | Inborn Error of Lipid Metabolism | Corneal ArcusGermany, India, Sri Lanka
-
CSL BehringActive, not recruitingHemophilia BUnited States, Belgium, Netherlands, Denmark, Germany, Ireland, Sweden, United Kingdom
-
Regeneron PharmaceuticalsSanofiActive, not recruitingDermatitis, AtopicUnited States, Canada
-
Regeneron PharmaceuticalsSanofiCompletedDermatitis, AtopicUnited States, France, Poland, United Kingdom, Germany, Hong Kong, Canada, Korea, Republic of, Italy, Lithuania, Sweden
-
Annexon, Inc.CompletedHuntington DiseaseUnited States
-
PfizerCompletedDermatitis, AtopicUnited States, Hungary, Canada, Germany, Australia, Czechia, Poland, United Kingdom
-
Forma Therapeutics, Inc.RecruitingSickle Cell Disease | ThalassemiaUnited States, Lebanon, Canada
-
Sarepta Therapeutics, Inc.Completed
-
National Cancer Institute (NCI)RecruitingNeurofibromatosis 1 | Plexiform NeurofibromasUnited States