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Clinical Trials on Pompe Disease (Late-onset)
Total 982 results
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Avera McKennan Hospital & University Health CenterCompletedAlzheimer's Disease | AgitationUnited States
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St George's, University of LondonMRC/UVRI and LSHTM Uganda Research Unit; MU-JHU CAREActive, not recruitingGroup B Streptococcus Carrier in Childbirth | Group B Streptococcal Infection, Late-Onset | Group B Streptococcal Infection, Early-Onset | Group B Streptococcus Neonatal Sepsis | Group B Strep InfectionUganda
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St George's, University of LondonMRC/UVRI and LSHTM Uganda Research Unit; MU-JHU CARECompletedGroup B Streptococcus Carrier in Childbirth | Group B Streptococcal Infection, Late-Onset | Group B Streptococcal Infection, Early-Onset | Group B Streptococcus Neonatal Sepsis | Group B Strep InfectionUganda
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University of OxfordNational Institute for Health Research, United KingdomCompletedPremature Birth | Necrotizing Enterocolitis | Late-onset Invasive InfectionUnited Kingdom, Ireland
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University of British ColumbiaUniversity of Toronto; University of Calgary; Children's Hospital of Eastern... and other collaboratorsRecruitingAntimicrobial Resistance | Multi-Drug Resistant Organisms | Late-Onset Sepsis, NeonatalCanada
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Orthogyn Medical Center, BulgariaCompletedLate-onset Fetal Growth Restriction
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St George's, University of LondonAssistance Publique - Hôpitaux de Paris; MRC/UVRI and LSHTM Uganda Research... and other collaboratorsRecruitingGroup B Streptococcus Carrier in Childbirth | Group B Streptococcal Infection, Late-Onset | Group B Streptococcal Infection, Early-Onset | Group B Streptococcus Neonatal Sepsis | Group B Strep InfectionFrance, Italy, Malawi, Netherlands, Uganda, United Kingdom
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Michael MorowitzEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingMicrobial Colonization | Late-Onset Neonatal Sepsis | Necrotizing Enterocolitis of Newborn | Extreme Prematurity | Death; Neonatal | Early-Onset Neonatal SepsisUnited States, Canada
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Pompe Disease Infantile-OnsetUnited States, France, South Africa
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National Heart, Lung, and Blood Institute (NHLBI)CompletedParkinson Disease 6, Early-Onset | Parkinson Disease (Autosomal Recessive, Early Onset) 7, Human | Parkinson Disease Autosomal Recessive, Early Onset | Parkinson Disease, Autosomal Recessive Early-Onset, Digenic, Pink1/Dj1United States
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Mount Sinai Hospital, CanadaThe Hospital for Sick Children; Sunnybrook Health Sciences Centre; University... and other collaboratorsRecruitingLate-Onset Neonatal Sepsis | Neonatal Hypotension | Extreme PrematurityCanada, United States, Ireland, Israel
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LMU KlinikumCompletedHealthy | Myotonic Dystrophy Type 2 | Pompe Disease (Late-onset) | Spinal Muscular Atrophy Type 3 | Myotonic Dystrophy Type 1 (DM1) | Facioscapulohumeral Muscular Dystrophy 1 | Inclusion Body Myositis, SporadicGermany
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Central Hospital, Nancy, FranceRecruitingPompe's Disease Juvenile OnsetFrance
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University of California, San FranciscoDuke UniversityRecruitingWolman Disease | MPS IVA | Pompe Disease Infantile-Onset | Gaucher Disease, Type 2 | MPS VI | MPS I | Gaucher Disease, Type 3 | MPS II | Mps VIIUnited States
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Ankara UniversityCompletedVery Low Birth Weight Infants | Necrotising Enterocolitis | Late Onset Neonatal SepsisTurkey
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Aristotle University Of ThessalonikiNHS Pulmonary Clinic G. Papanikolaou Hospital, Thessaloniki, Greece; Pulmonary... and other collaboratorsActive, not recruitingSevere Asthma | Asthma; Eosinophilic | Late-Onset AsthmaGreece
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Emma Marie Caroline SlackUniversity of Zurich; University Children's Hospital, ZurichCompletedLate-Onset Neonatal Sepsis | Necrotising EnterocolitisSwitzerland
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Cairo UniversityNot yet recruitingEarly Disease Onset
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Second Xiangya Hospital of Central South UniversityRecruitingAdult Onset Still DiseaseChina
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Central Hospital, Nancy, FranceCompleted
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R-Pharm International, LLCData Management 365; Federal State Budgetary Educational Institution for Higher... and other collaboratorsWithdrawnAdult-Onset Still's Disease | AOSDRussian Federation
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Charite University, Berlin, GermanyTerminatedAdult-Onset Still´s DiseaseGermany
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University of HelsinkiTurku University Hospital; Oulu University Hospital; Kuopio University Hospital; Helse Stavanger... and other collaboratorsCompletedTreatment of Refractory Adult-onset Still's Disease With Anakinra: a Randomized Study (NordicAOSD05)Adult-Onset Still's DiseaseSweden
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University College DublinWellcome Trust; Health Research Board, Ireland; National Maternity Hospital,... and other collaboratorsRecruitingLate-Onset Neonatal Sepsis | Necrotising Enterocolitis | Culture Negative Neonatal SepsisIreland
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Göteborg UniversityRecruitingPANS Pediatric Acute-Onset Neuropsychiatric SyndromeSweden
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Per Torp SangildCompletedNecrotizing Enterocolitis | Feeding Intolerance | Postnatal Growth | Late-Onset Neonatal SepsisChina
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Imperial College LondonChelsea and Westminster NHS Foundation Trust; National Heart and Lung Institute and other collaboratorsCompletedNecrotizing Enterocolitis | Premature Intestinal Microbiota | Late Onset Bloodstream InfectionUnited Kingdom
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Bin LiUnknownAcute LHON | Onset Within Three Months | Onset Between 3 to 6 Months | Onset Between 6 to 12 Months | Onset Between 12 to 24 Months | Onset Between 24 to 60 Months | Onset Over 60 MonthsChina
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Neurocrine BiosciencesTerminatedFocal Onset Seizure | Focal Onset EpilepsySpain, Australia, Belgium, Czechia, France, Hungary, Italy
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Emalex Biosciences Inc.Premier Research Group plc; University of California, RiversideCompletedChildhood-Onset Fluency Disorder (Stuttering)United States
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National Institute of Mental Health (NIMH)TerminatedPediatric Acute-onset Neuropsychiatric Syndrome (PANS)United States
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Neurocrine BiosciencesCompletedFocal Onset Seizure | Focal Onset EpilepsySpain, Belgium, Czechia, France, Italy, Australia, Hungary, United Kingdom
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Ain Shams UniversityCompletedFeeding; Difficult, Newborn | Necrotizing Enterocolitis of Newborn | Late Onset Neonatal SepsisEgypt
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IBSS Biomed S.A.Ministry of Science and Higher Education, PolandCompletedNecrotizing Enterocolitis | Infant, Very Low Birth Weight | Late Onset Neonatal Sepsis
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University Hospital, Gentofte, CopenhagenCompletedMaturity-Onset Diabetes of the Young, Type 3Denmark
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Taichung Veterans General HospitalNational Health Research Institutes, TaiwanRecruitingDiabetes Complications | Type 2 Diabetes | Maturity-Onset Diabetes of the Young (MODY)Taiwan
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Central Hospital, Nancy, FranceCompletedCritically Ill | Adult-Onset Still DiseaseFrance
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Novartis PharmaceuticalsActive, not recruitingAdult Onset Still's DiseaseJapan
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University of OxfordRecruitingAtrial Fibrillation | Atrial Fibrillation New Onset | New Onset Atrial FibrillationUnited Kingdom
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University of British ColumbiaNot yet recruitingPersistent Developmental Stutter | Childhood-Onset Fluency Disorder (Stuttering)
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Noema Pharma AGCompletedChildhood-Onset Fluency DisorderUnited States, Australia
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Gerald Maguire, MDUniversity of California Riverisde School of MedicineUnknownLanguage Disorders | Speech Disorders | Communication Disorder | Stuttering, Adult | Childhood-onset Fluency DisorderUnited States
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Per Torp SangildShenzhen People's Hospital; Sixth Affiliated Hospital, Sun Yat-sen University; Maternal and Child Health Hospital of Foshan and other collaboratorsCompletedNecrotizing Enterocolitis | Enteral Feeding Intolerance | Late-Onset Neonatal SepsisChina
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Centre for Analytical Biochemistry and Biomedical...University of GiessenRecruiting
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Steno Diabetes Center CopenhagenUniversity of CopenhagenCompletedType 2 Diabetes | Maturity-Onset Diabetes of the Young, Type 3Denmark
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National Institute of Mental Health (NIMH)TerminatedSchizophrenia | Childhood Onset Psychotic DisordersUnited States
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AB2 Bio Ltd.CompletedStill's Disease, Adult-OnsetGermany, France, Switzerland
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University of PalermoNot yet recruitingInduction of Labor Affected Fetus / Newborn | Pregnancy LateItaly
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Kasr El Aini HospitalCompletedQuality of Ocular Akinesia (Onset and Duration)Egypt
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedTay Sachs Disease | Sandhoff Disease | Late Onset Tay Sachs DiseaseUnited States