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Clinical Trials on Pompe Disease Infantile-Onset
Total 900 results
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Medical College of WisconsinNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedDiabetes Mellitus, Type 2 | Diabetes Mellitus, Type II | Diabetes Mellitus, Adult-Onset | Diabetes Mellitus, Non-Insulin-Dependent | Diabetes Mellitus, Noninsulin DependentUnited States
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Insel Gruppe AG, University Hospital BernRecruitingTranscatheter Aortic Valve Replacement | Atrial Fibrillation New Onset | Pacemaker | ColchicineSwitzerland
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe DiseaseUnited States
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Semra Çevik, phDCompletedLabor Pain | Patient Satisfaction | Virtual Reality | Labor Onset | Breathing; TicTurkey
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Assaf-Harofeh Medical CenterUnknownAttention Deficit Hyperactivity Disorder | Sleep Onset InsomniaIsrael
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Nij Smellinghe HosptialCompletedLymphedema | Breast Cancer Stage II | Early Disease OnsetNetherlands
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Kansas City Heart Rhythm Research FoundationRecruitingAortic Stenosis | Heart Block | Atrial Fibrillation New OnsetUnited States
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe DiseaseUnited States, Israel, France, United Kingdom
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Genzyme, a Sanofi CompanyTerminatedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease | Glycogenesis 2 Acid Maltase DeficiencyUnited States, Israel
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Royal Brompton & Harefield NHS Foundation TrustGenzyme, a Sanofi CompanyUnknownPompe's Disease
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AmgenImmunex CorporationTerminatedJuvenile Rheumatoid Arthritis
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease | Glycogenesis 2 Acid Maltase DeficiencyUnited States, Canada, Australia
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingDiarrhea | Gastroesophageal Reflux | Functional Gastrointestinal Disorders | Constipation - Functional | Colic, Infantile | Dyschezia | Vomiting; CyclicalItaly
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University of British ColumbiaUniversity of Toronto; University of Calgary; Children's Hospital of Eastern... and other collaboratorsRecruitingAntimicrobial Resistance | Multi-Drug Resistant Organisms | Late-Onset Sepsis, NeonatalCanada
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Orthogyn Medical Center, BulgariaCompletedLate-onset Fetal Growth Restriction
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Jena University HospitalCenter of Fetal Surgery, University Hospital Halle Saale; Section for Neonatology...Recruiting
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Jordi Perez LopezHospital Vall d'HebronUnknown
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San Raffaele UniversityFondazione IRCCS Istituto Nazionale dei Tumori di Milano, Milan, Italy; Ospedale... and other collaboratorsRecruitingColorectal Cancer | Diet Habit | Risk Reduction | Early Onset Colorectal CancerUnited States, Finland, Germany, Italy, Norway, Spain
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Bruce A. BuckinghamCompletedType 1 Diabetes Mellitus | Autoimmune Diabetes | Juvenile-Onset Diabetes | Diabetes, Mellitus, Type 1United States
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Assistance Publique Hopitaux De MarseilleNot yet recruitingTricho Hepato Enteric SyndromeFrance
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University of Alabama at BirminghamMichael J. Fox Foundation for Parkinson's ResearchCompletedParkinson Disease | Dystonia-Parkinsonism, Adult-OnsetUnited States
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Guangzhou University of Traditional Chinese MedicineState Key Laboratory of Dampness Syndrome of Chinese Medicine, the Second...RecruitingCancer | Chronic Disease | Aging | Alzheimer Disease, Early Onset | Metabolic Disease | Dementia AlzheimersChina
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Aziende Chimiche Riunite Angelini Francesco S.p.APremier Research Group plcCompletedDelayed-Onset Muscle Soreness (DOMS)Spain
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Institute of Child HealthUniversity College, London; Great Ormond Street Hospital for Children NHS Foundation...RecruitingAlternating Hemiplegia of Childhood | ATP1A3-related Disease | Rapid Onset Dystonia Parkinsonism | CAPOSUnited Kingdom
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Rennes University HospitalRecruitingParkinson Disease | Alzheimer Disease, Early OnsetFrance
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Erasmus Medical CenterTerminatedGeneralized Anxiety Disorder | Social Anxiety Disorder | Specific Phobia | Anxiety Disorder | Anxiety Disorder of Childhood | Separation Anxiety Disorder of Childhood, Early OnsetNetherlands
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe DiseaseUnited States
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Brugmann University HospitalUniversité Libre de BruxellesUnknownSepsis | Still's Disease, Adult-Onset | Macrophagic Activation SyndromeBelgium
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Alice K. GongTerminatedInfantile Hemangioma | Very Low Birth Weight InfantsUnited States
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University Hospital TuebingenTerminatedHemangioma of Preterm Infants
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Pompe DiseaseUnited States
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Capital Medical UniversityRecruitingHad a Computed Tomography Scan of the Chest Within 24 Hours After Stroke OnsetChina
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Baskent UniversityCompletedVascular Stiffness | Hypertrophy, Left Ventricular | Diabetes Mellitus Nos New OnsetTurkey
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RenJi HospitalNot yet recruitingWhether Belimumab Could Reduce 2-year Risk of New-onset Lupus Nephritis
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Eisai Inc.AvailableLennox Gastaut Syndrome | Primary Generalized Tonic-Clonic or Partial Onset SeizuresBelgium, Chile, Estonia, Hungary, Latvia, Lithuania, Poland, Spain
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Jordan Collaborating Cardiology GroupCardiovascular Academy GroupTerminatedTriggers of Acute Myocardial Infarction | Time of Onset of Acute Myocardial Infarction | Long-term Prognosis After Acute Myocardial InfarctionJordan
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Sheba Medical CenterUnknownInfantile Canavan Disease | Deficiency Disease, AspartoacylaseIsrael
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Medical College of WisconsinMedical University of South CarolinaCompletedDiabetes Mellitus | Type 2 Diabetes Mellitus | Adult-Onset Diabetes Mellitus | Non-Insulin-Dependent Diabetes Mellitus | Noninsulin Dependent Diabetes Mellitus, Type IIUnited States
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University Hospital Center of MartiniqueRecruiting
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University of California, IrvineCompletedMuscle Weakness | Pompe DiseaseUnited States
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Sheffield Teaching Hospitals NHS Foundation TrustRecruitingColorectal Cancer | Atrial Fibrillation New OnsetUnited Kingdom
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Fundacio d'Investigacio en Atencio Primaria Jordi...Institut Català de la SalutRecruitingStroke | Atrial Fibrillation | Dementia | Atrial Fibrillation New OnsetSpain
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University of CincinnatiChildren's Hospital Medical Center, CincinnatiTerminatedAdrenoleukodystrophy | Zellweger Syndrome | Infantile Refsum's Disease | Bifunctional Enzyme Deficiency
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GAP Innovations, PBCCompletedAlzheimer Disease | Mild Cognitive Impairment | Alzheimer Disease, Early Onset | Memory Disorders | Memory Impairment | Memory LossUnited States
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SanofiCompletedPompe Disease | Mucopolysaccharidosis Type I (MPS I)Italy
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Johnson & Johnson Pharmaceutical Research & Development...CompletedObesity | Diabetes Mellitus, Type 2 | Diabetes Mellitus, Adult-Onset
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Cairo UniversityCompletedAcupuncture | PCO | Primary Hypothyroidism | Irregular MenstruationEgypt
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Harokopio UniversityNational and Kapodistrian University of Athens; University of PeloponneseUnknownInflammation | Oxidative Stress | Postprandial Hyperglycemia | Diabetes Mellitus, Adult-Onset | Platelet Dysfunction | LipidemiaGreece
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The University of Texas Medical Branch, GalvestonCompletedPreterm Infant | Umbilical Cord | Early-Onset Neonatal SepsisUnited States
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Assistance Publique - Hôpitaux de ParisEuropean Leukodystrophy AssociationWithdrawnDeficiency Disease | Canavan Disease | Infantile | Aspartoacylase | Leukodystrophy, Spongiform