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Clinical Trials on Pompe Disease Infantile-Onset
Total 905 results
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Radius Pharmaceuticals, Inc.TerminatedInfantile SpasmUnited States
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Turkish Society of Pediatric Gastroenterology,...CompletedDuchenne Muscular Dystrophy | Pompe Disease (Late-onset)Turkey
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University of Colorado, DenverMallinckrodtRecruitingInfantile Spasms, Non-IntractableUnited States
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University of California, San FranciscoRecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Wolman Disease | Pompe Disease Infantile-Onset | Mucopolysaccharidosis IV A | Mucopolysaccharidosis VII | Neuronopathic Gaucher DiseaseUnited States
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Retrotope, Inc.CompletedNeuroaxonal Dystrophy, InfantileEgypt, China, Saudi Arabia, India, Tunisia
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Kullasate SakpichaisakulRecruitingWest Syndrome | Infantile SpasmThailand
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Bio-Pharm Solutions Co., Ltd.TerminatedRefractory Infantile SpasmsUnited States, Korea, Republic of
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UCB Biopharma S.P.R.L.TerminatedInfantile Spasms (IS)France
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University of California, BerkeleyMakerere UniversityCompletedDiarrhea | Dehydration | Infantile Diarrhea
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National Heart, Lung, and Blood Institute (NHLBI)CompletedParkinson Disease 6, Early-Onset | Parkinson Disease (Autosomal Recessive, Early Onset) 7, Human | Parkinson Disease Autosomal Recessive, Early Onset | Parkinson Disease, Autosomal Recessive Early-Onset, Digenic, Pink1/Dj1United States
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Central Hospital, Nancy, FranceRecruitingPompe's Disease Juvenile OnsetFrance
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Massachusetts Institute of TechnologyRecruitingAlzheimer Disease | Alzheimer Disease, Early Onset | Alzheimer Disease, Late Onset | Alzheimer's Disease | Alzheimer's Disease (Incl Subtypes) | Alzheimer'sUnited States
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Marinus PharmaceuticalsTerminated
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Jazz PharmaceuticalsCompletedInfantile SpasmsUnited States, Poland
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All India Institute of Medical Sciences, New DelhiCompleted
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Jazz PharmaceuticalsCompletedInfantile SpasmsUnited States, Poland
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Lady Hardinge Medical CollegeCompleted
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INSYS Therapeutics IncTerminatedSpasms, InfantileUnited States
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Lady Hardinge Medical CollegeWithdrawnInfantile SpasmsIndia
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Lundbeck LLCWithdrawn
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Cairo UniversityNot yet recruitingEarly Disease Onset
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Second Xiangya Hospital of Central South UniversityRecruitingAdult Onset Still DiseaseChina
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Central Hospital, Nancy, FranceCompleted
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R-Pharm International, LLCData Management 365; Federal State Budgetary Educational Institution for Higher... and other collaboratorsWithdrawnAdult-Onset Still's Disease | AOSDRussian Federation
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Charite University, Berlin, GermanyTerminatedAdult-Onset Still´s DiseaseGermany
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University of HelsinkiTurku University Hospital; Oulu University Hospital; Kuopio University Hospital; Helse Stavanger... and other collaboratorsCompletedTreatment of Refractory Adult-onset Still's Disease With Anakinra: a Randomized Study (NordicAOSD05)Adult-Onset Still's DiseaseSweden
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University of MinnesotaMayo Clinic; National Institute on Aging (NIA); University of St ThomasCompletedAlzheimer's Disease, Late OnsetUnited States
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NeuroEM Therapeutics, Inc.Invicro, Boston; Byrd Alzheimer's Institute, University of South Florida; University... and other collaboratorsCompletedAlzheimer Disease | Alzheimer Disease, Late OnsetUnited States
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Federal University of Minas GeraisCompletedAlzheimer Disease, Late Onset
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Lady Hardinge Medical CollegeCompletedInfantile Spasms | West SyndromeIndia
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University of Colorado, DenverCompleted
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The Hospital for Sick ChildrenWithdrawnInfantile SpasmsCanada
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Yonsei UniversityCompleted
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Amicus TherapeuticsRecruitingGlycogen Storage Disease Type II Infantile OnsetUnited States, Taiwan, France, Germany, Italy, United Kingdom
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University of MiamiColumbia University; National Institute on Aging (NIA); Case Western Reserve... and other collaboratorsRecruitingDementia | Mild Cognitive Impairment | Alzheimer Disease, Early Onset | Alzheimer Disease, Late Onset | Dementia of Alzheimer TypeUnited States
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Göteborg UniversityRecruitingPANS Pediatric Acute-Onset Neuropsychiatric SyndromeSweden
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Indiana UniversityNational Institute on Aging (NIA)RecruitingDementia | Alzheimer Disease, Late OnsetUnited States
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IRCCS Centro San Giovanni di Dio FatebenefratelliI.R.C.C.S. Fondazione Santa Lucia; Ministero della Salute, ItalyRecruitingAlzheimer Disease | Alzheimer Disease, Late Onset | Cognitive DeteriorationItaly
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All India Institute of Medical Sciences, New DelhiActive, not recruitingWest Syndrome | ACTH | Infantile Spasm | Ketogenic DietIndia
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Wayne State UniversityCompleted
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Ohio State UniversityCompletedAlzheimer Disease, Late OnsetUnited States
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NeuroEM Therapeutics, Inc.University of South Florida Health / Byrd Alzheimer's InstituteUnknownAlzheimer Disease | Alzheimer Disease, Late OnsetUnited States
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Universitaire Ziekenhuizen KU LeuvenUnknownAlzheimer Disease, Late OnsetBelgium
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AmzellWithdrawnSpasms, InfantileItaly, Argentina, France, United States, Spain, India, Poland, Mexico
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Bin LiUnknownAcute LHON | Onset Within Three Months | Onset Between 3 to 6 Months | Onset Between 6 to 12 Months | Onset Between 12 to 24 Months | Onset Between 24 to 60 Months | Onset Over 60 MonthsChina
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Neurocrine BiosciencesTerminatedFocal Onset Seizure | Focal Onset EpilepsySpain, Australia, Belgium, Czechia, France, Hungary, Italy
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Tamir Ben-HurHebrew University of JerusalemEnrolling by invitationAlzheimer Disease, Late OnsetIsrael
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Mindful Diagnostics and Therapeutics, LLCCompleted
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Emalex Biosciences Inc.Premier Research Group plc; University of California, RiversideCompletedChildhood-Onset Fluency Disorder (Stuttering)United States
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National Institute of Mental Health (NIMH)TerminatedPediatric Acute-onset Neuropsychiatric Syndrome (PANS)United States