- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Proteostasis Deficiencies
Total 1775 results
-
Shahid Beheshti University of Medical SciencesCompleted
-
Pr. Nicolas GIRERDRecruitingTransthyretin Cardiac AmyloidosisFrance
-
Mayo ClinicCompletedTTR Cardiac AmyloidosisUnited States
-
Poitiers University HospitalPfizerCompletedTransthyretin Cardiac AmyloidosisFrance
-
Alnylam PharmaceuticalsCompletedTTR-mediated AmyloidosisUnited States, United Kingdom
-
Washington University School of MedicineCompleted
-
Alnylam PharmaceuticalsRecruitingTransthyretin-Mediated AmyloidosisUnited Kingdom
-
Alnylam PharmaceuticalsCompletedTTR-mediated AmyloidosisPortugal, Spain, Sweden, Brazil, United States, France, Germany
-
IRCCS Policlinico S. MatteoCompleted
-
Alnylam PharmaceuticalsCompleted
-
Alnylam PharmaceuticalsCompletedTTR-mediated AmyloidosisUnited Kingdom
-
Columbia UniversityAttralus, Inc.RecruitingTransthyretin AmyloidosisUnited States
-
Yale UniversityAlnylam Pharmaceuticals IncNot yet recruitingTransthyretin AmyloidosisUnited States
-
University Hospital, CaenPfizerRecruitingAmyloidosis TransthyretinFrance
-
Ionis Pharmaceuticals, Inc.CompletedHealthy Volunteers | hATTR AmyloidosisCanada
-
University of PennsylvaniaWashington University School of MedicineCompleted
-
GlaxoSmithKlineTerminated
-
C.T. Development America, Inc.CompletedAmyloidosisSpain, United States, Italy, Belgium, Netherlands, India, Tunisia, Latvia, Turkey, France, Germany, Estonia, Lithuania, Poland, Russian Federation, Georgia, United Kingdom, Israel, Egypt, Finland, Peru, Sweden, Ukraine
-
Alnylam PharmaceuticalsCompletedA Study of the Safety, Tolerability and Pharmacokinetics of ALN-TTR02 in Japanese Healthy VolunteersTransthyretin (TTR)-Mediated AmyloidosisUnited Kingdom
-
Oregon Health and Science UniversityAttralus, Inc.RecruitingAmyloidosis | Transthyretin AmyloidosisUnited States
-
GCS Ramsay Santé pour l'Enseignement et la RechercheRecruiting
-
Wuhan Union Hospital, ChinaRecruiting
-
Attralus, Inc.CompletedAmyloidosis; SystemicUnited States
-
PfizerCompletedATTR-PNUnited States, Germany, Argentina, Brazil, France, Italy, Portugal, Sweden
-
Prothena Biosciences LimitedTerminatedAmyloidogenic Transthyretin (ATTR) AmyloidosisUnited States, Spain, Sweden, Portugal
-
Fábio FernandesPfizerUnknown
-
GE HealthcareCovance; i3 StatprobeCompletedBrain Fibrillarab LevelsUnited States
-
Mayo ClinicRecruitingHealthy Adults | Amyloidosis CardiacUnited States
-
Beneficência Portuguesa de São PauloRecruiting
-
Alnylam PharmaceuticalsCompletedTransthyretin Mediated Amyloidosis (ATTR)United Kingdom, France, Portugal, Sweden
-
PfizerCompletedTransthyretin Familial Amyloid Poluneuropathy
-
Henry Ford Health SystemRecruiting
-
Alnylam PharmaceuticalsCompletedTTR-mediated AmyloidosisPortugal, Sweden, Brazil, United States, France, Spain, Germany
-
Mayo ClinicCompletedAmyloidosisUnited States
-
University of Texas Southwestern Medical CenterRecruitingTransthyretin Cardiac AmyloidosisUnited States
-
Alnylam PharmaceuticalsTerminatedAmyloidosis | Leukocyte Chemotactic Factor 2 AmyloidosisUnited States, Malaysia, United Kingdom, Mexico, Egypt, India
-
Umeå UniversityCompleted
-
University of LeipzigRecruiting
-
Wake Forest University Health SciencesRecruitingCardiac AmyloidosisUnited States
-
Brigham and Women's HospitalRecruiting
-
Oregon Health and Science UniversityRecruiting
-
European Myeloma NetworkJanssen PharmaceuticaActive, not recruitingLight Chain (AL) Amyloidosis, Stage 3BNetherlands, Greece, France, Italy
-
University College, LondonGlaxoSmithKline; Medical Research Council; University of OxfordCompleted
-
Zhi-Hong Liu, M.D.Nanjing Medical University; Soochow UniversityCompleted
-
FDA Office of Orphan Products DevelopmentCompleted
-
Fujian Medical University Union HospitalRecruiting
-
Taipei Veterans General Hospital, TaiwanApollo Medical Optics, LtdCompleted
-
Alnylam PharmaceuticalsCompletedTTR-mediated AmyloidosisUnited States, Canada, United Kingdom
-
Assistance Publique - Hôpitaux de ParisNot yet recruitingAutoinflammatory Disease | AA Amyloidosis
-
IRCCS Policlinico S. MatteoRecruiting