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Clinical Trials on Pyruvate Kinase Deficiency in United Kingdom
Total 4550 results
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BioCryst PharmaceuticalsCompleted
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St George's, University of LondonSPD Development Company LimitedSuspendedObesity | Polycystic Ovary Syndrome | Vitamin D Deficiency | Insulin ResistanceUnited Kingdom
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TakedaRecruitingHereditary Angioedema (HAE)United Kingdom
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | Cholesterol Ester Storage Disease(CESD)United States, United Kingdom, France, Canada, Czech Republic, Italy, Poland, Switzerland
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University of BathUniversity of NottinghamActive, not recruitingAdiposity | Metabolic Disturbance | Fasting | Energy Supply; DeficiencyUnited Kingdom
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University of LiverpoolRecruitingSurgery | Preterm | Nutritional Deficiency | Immune System and Related DisordersUnited Kingdom
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University of NottinghamNottingham University Hospitals NHS TrustRecruitingChronic Obstructive Pulmonary Disease | Alpha 1-Antitrypsin DeficiencyUnited Kingdom
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University of OxfordBritish Heart Foundation; National Institute for Health Research, United KingdomCompletedPulmonary Arterial Hypertension | Iron Deficiency | Lung HypoxiaUnited Kingdom
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Z Factor LimitedHammersmith Medicines Research; Centessa Pharmaceuticals plcTerminatedAlpha1 Anti-Trypsin DeficiencyUnited Kingdom
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Adnan SharifActive, not recruitingPhysical Activity | Hemodialysis Complication | Nutritional DeficiencyUnited Kingdom
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KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited Kingdom
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BioCryst PharmaceuticalsCompletedHereditary AngioedemaUnited Kingdom
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BioCryst PharmaceuticalsCompletedHereditary AngioedemaUnited Kingdom
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BioCryst PharmaceuticalsCompletedHereditary AngioedemaUnited Kingdom
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC Deficiency Obesity | PCSK1 Deficiency Obesity | LEPR Deficiency ObesityUnited States, Australia, Spain, United Kingdom
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Great Ormond Street Hospital for Children NHS Foundation...RecruitingSevere Combined Immunodeficiency, X-LinkedUnited Kingdom
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TakedaRecruitingHereditary Angioedema (HAE)United Kingdom
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Rhythm Pharmaceuticals, Inc.CompletedLeptin Receptor Deficiency ObesityNetherlands, Germany, United Kingdom, Canada, France, Réunion
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University of NottinghamNottingham University Hospitals NHS Trust; Action for A-TCompleted
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Newcastle UniversityBill and Melinda Gates Foundation; Institute of Nutrition of Central America... and other collaboratorsUnknownVitamin A Deficiency | Vitamin A Toxicity | Hypervitaminosis AGuatemala, United Kingdom
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase DeficiencyFrance, Poland, United Kingdom, Spain, Mexico, Turkey, Japan, Australia, Russian Federation, United States, Germany, Italy, Czechia, Argentina, Croatia
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Tameside General HospitalCompletedCOVID-19 | Vitamin D DeficiencyUnited Kingdom
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Imperial College LondonTerminatedHereditary Haemorrhagic TelangiectasiaUnited Kingdom
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Institute of Child HealthGreat Ormond Street Hospital for Children NHS Foundation TrustCompletedAtaxia Telangiectasia (AT)United Kingdom
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Origin BiosciencesCompletedMolybdenum Cofactor Deficiency, Type AUnited States, Australia, Netherlands, United Kingdom, Tunisia
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Arrowhead PharmaceuticalsActive, not recruitingAlpha 1-Antitrypsin DeficiencyAustria, Germany, United Kingdom
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Royal Surrey County Hospital NHS Foundation TrustCompletedColorectal Cancer | Sarcopenia | Surgery | Surgery--Complications | Surgical Site Infection | Nutritional Deficiency | Complication, Postoperative | Infected Wound | Phagocytic DysfunctionUnited Kingdom
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National Heart and Lung InstituteWexham Park Hospital; 4th Military HospitalUnknownHeart Diseases | Anemia, Iron-Deficiency | Chronic Heart FailurePoland, United Kingdom
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Congenital FXIII DeficiencyUnited Kingdom
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Congenital FXIII DeficiencyUnited Kingdom
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Blueprint Medicines CorporationActive, not recruitingNeoplasms | Neoplasms by Histologic Type | Lung Diseases | Neoplasms by Site | Adenocarcinoma | Carcinoma | Carcinoma, Non-Small-Cell Lung | Lung Neoplasms | Respiratory Tract Neoplasms | Thoracic Neoplasms | Carcinoma, Bronchogenic | Bronchial Neoplasms | Neoplasms, Nerve Tissue | EGF-R Positive Non-Small Cell Lung... and other conditionsUnited States, Canada, Taiwan, Korea, Republic of, Singapore, Japan, United Kingdom, France, Netherlands, Spain
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Bio Products LaboratoryCompletedPrimary Antibody DeficiencyUnited Kingdom
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University of PlymouthRecruitingAtaxia Telangiectasia | Ataxia Telangiectasia in ChildrenUnited Kingdom
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Leiden University Medical CenterZonMw: The Netherlands Organisation for Health Research and Development; Horizon...RecruitingSevere Combined Immunodeficiency Due to RAG1 DeficiencySpain, Netherlands, Italy, Poland, Australia, Turkey, United Kingdom
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Great Ormond Street Hospital for Children NHS Foundation...Cukurova University; University of Kiel; Athens General Children's Hospital "Pan...Active, not recruitingChronic Kidney Disease Mineral and Bone DisorderUnited Kingdom
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Congenital FXIII DeficiencyUnited Kingdom
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Astellas Pharma Global Development, Inc.RecruitingAcute Myeloid Leukemia (AML) | Acute Myeloid Leukemia With FMS-like Tyrosine Kinase 3 (FLT3) Mutation / Internal Tandem Duplication (ITD)United States, Canada, Germany, Italy, Spain, United Kingdom, France
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NHS TaysideUniversity of DundeeCompletedAtaxia-TelangiectasiaUnited Kingdom
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Applied Therapeutics, Inc.Active, not recruitingHereditary Neuropathy Caused by SORD DeficiencyUnited States, United Kingdom, Czechia, Italy
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Rocket Pharmaceuticals Inc.California Institute for Regenerative Medicine (CIRM)CompletedLeukocyte Adhesion Defect - Type ISpain, United States, United Kingdom
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Northumbria UniversityBayerCompletedCognitive Function and Mood | Non-anaemic Iron DeficiencyUnited Kingdom
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University of SussexBrighton and Sussex University Hospitals NHS TrustActive, not recruitingHIV InfectionsUnited Kingdom
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ViiV HealthcareCompleted
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ViiV HealthcareCompleted
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Imperial College LondonPfizerCompleted
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International AIDS Vaccine InitiativeCompletedHIV InfectionsUnited Kingdom
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Gilead SciencesCompleted
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Royal Free Hampstead NHS TrustRoche Pharma AGCompleted
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Massachusetts General HospitalAlexion PharmaceuticalsUnknownCholesterol Ester Storage Disease | Lysosomal Acid Lipase DeficiencyUnited States
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Grifols Therapeutics LLCCompletedAlpha 1-Antitrypsin DeficiencyDenmark, Sweden, United Kingdom